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Randomized, Double-Blind, Placebo Controlled Study of the Short Term Clinical Effects of Tolvaptan in Patients Hospitalized for Worsening Heart Failure With Challenging Volume Management

Phase 3
Completed
Conditions
Heart Failure
Interventions
Drug: placebo or sugar pill
Registration Number
NCT01584557
Lead Sponsor
Cardiovascular Clinical Science Foundation
Brief Summary

The purpose of this study is to evaluate the short term efficacy and safety of tolvaptan in subjects hospitalized for worsening heart failure who have volume overload and one of the following: renal insufficiency, or hyponatremia or inadequate response to diuretic therapy. The primary variable for assessing efficacy will be self-assessed 7-point dyspnea score at 8 and 16 hours.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
250
Inclusion Criteria
  1. Subjects hospitalized for worsening heart failure and randomized within 36 hours of initial presentation.

  2. Males and females 18 years of age or older.

  3. NYHA Class III or IV on admission to the hospital.

  4. Able to understand content of and willing to provide written informed consent

  5. Dyspnea, measured by the 5-point current dyspnea scale (moderately short of breath or worse), within 2 hours of randomization and dosing.

    The following must be met within 12 hours of randomization.

  6. The subject must have signs of extracellular volume expansion, defined as two or more of the following five: Signs of RHF ( jugular venous distention, pitting edema (≥1+), ascites) and/or Signs of LHF (pulmonary congestion on chest x-ray, pulmonary rales)

  7. Have at least one of the following:

    • eGFR < 60ml/min/1.73m2, OR
    • serum sodium ≤ 134 mEq/L, OR
    • urine output ≤ 125 ml/hr over anytime frame of at least 2 hours, following administration of IV furosemide of at least 40mg. See table below.

Time Period (hr) Cumulative UO (mL) 2 <250 3 <375 4 <500 5 <625 6 <750 7 <875 8 <1000

Exclusion Criteria
  1. Positive urine pregnancy test for women of child bearing potential.
  2. Inability to provide written informed consent.
  3. Cardiac surgery within 60 days prior to study randomization.
  4. Acute Coronary Syndrome (ACS) or percutaneous coronary intervention within 30 days prior to study randomization.
  5. Planned revascularization procedures, cardiac mechanical support implantation, cardiac transplantation, or other cardiac surgery within 30 days following study randomization.
  6. Planned electrophysiologic (EP) device implantation within 7 days following study randomization.
  7. Subjects who are on cardiac mechanical support.
  8. Co-morbid condition with an expected survival less than six months.
  9. History of a cerebrovascular accident within the last 30 days.
  10. Hemodynamically significant uncorrected primary cardiac valvular disease.
  11. Hypertrophic cardiomyopathy (obstructive or non-obstructive).
  12. Uncorrected thyroid disease, active myocarditis or known amyloid cardiomyopathy.
  13. History of primary significant liver disease or acute hepatic failure, as defined by the investigator.
  14. Chronic uncontrolled diabetes mellitus as determined by the investigator.
  15. Supine systolic arterial blood pressure < 90 mmHg.
  16. Serum creatinine > 3.5 mg/dL or undergoing dialysis.
  17. Hemoglobin < 9 g/dL
  18. History of hypersensitivity and/or idiosyncratic reaction to benzazepine derivatives (such as benazepril).
  19. Inability to take oral medications.
  20. Participation in another clinical drug or device trial where the last dose of drug was within the past 30 days or an investigational medical device is currently implanted.
  21. Previous exposure to tolvaptan within 7 days prior to randomization.
  22. Subjects with refractory, end-stage, heart failure defined as subjects who are appropriate candidates for specialized treatment strategies, such as ventricular assist devices, continuous positive IV inotropic therapy, or hospice care.
  23. Ultrafiltration within 7 days prior to randomization or planned.
  24. Active gout
  25. Serum sodium >144 mEq/L

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
sugar pillplacebo or sugar pillplacebo, sugar pill
Tolvaptan, SamscaTolvaptan or SamscaTolvaptan, Samsca, uncoated tablet, 30 mg, once per day, up to 7 days.
Primary Outcome Measures
NameTimeMethod
To evaluate the short term efficacy and safety of tolvaptan in subjects hospitalized for worsening heart failure who have volume overload and one of the following: renal insufficiency, or hyponatremia or inadequate response to diuretic therapy.8 and 16 hours

The primary variable for assessing efficacy will be self-assessed 7-point dyspnea score at 8 and 16 hours.

Secondary Outcome Measures
NameTimeMethod
Change from baseline in cognitive function at 48 hours or discharge, whichever comes firstat 48 hours or dischage, whichever comes first

Change from baseline in cognitive function at 48 hours or discharge, whichever comes first

Change from baseline in body weight measured daily while hospitalized up to 7 days.up to 7 days

Change from baseline in body weight measured daily while hospitalized up to 7 days.

Diuretic dose measured daily while hospitalized up to 7 days.up to 7 days.

Diuretic dose measured daily while hospitalized up to 7 days.

Re-hospitalization for worsening heart failure or death at 30 days30 days.

Re-hospitalization for worsening heart failure or death at 30 days

Change from baseline in estimated glomerular filtration rate (eGFR) at discharge or day 7, whichever comes first.at discharge or day 7, whichever comes first.

Change from baseline in estimated glomerular filtration rate (eGFR) at discharge or day 7, whichever comes first.

Days alive and out of the hospital over 30 days30 days.

Days alive and out of the hospital over 30 days

Trial Locations

Locations (37)

The Valley Hospital

🇺🇸

Ridgewood, New Jersey, United States

Drexel University College of Medicine

🇺🇸

Philadelphia, Pennsylvania, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Greater Los Angeles VA Medical Center

🇺🇸

Los Angeles, California, United States

The Heart Center Research

🇺🇸

Huntsville, Alabama, United States

MIMA Century Research Associates

🇺🇸

Melbourne, Florida, United States

University of Florida Health Science Ctr. Jacksonville

🇺🇸

Jacksonville, Florida, United States

University Cardiology Associates, LLC

🇺🇸

Augusta, Georgia, United States

Emory University

🇺🇸

Atlanta, Georgia, United States

Advocate Christ Medical Center

🇺🇸

Oak Lawn, Illinois, United States

Mercer University School of Medicine

🇺🇸

Macon, Georgia, United States

Advocate Medical Group - Oakbrook

🇺🇸

Naperville, Illinois, United States

Louisiana Heart Center and Research

🇺🇸

Slidell, Louisiana, United States

CardioSpecialists Group

🇺🇸

Munster, Indiana, United States

Lahey Hospital and Medical Center

🇺🇸

Burlington, Massachusetts, United States

University of Maryland

🇺🇸

Baltimore, Maryland, United States

Crittenton Hospital Medical Center

🇺🇸

Rochester, Michigan, United States

Tufts Medical Center

🇺🇸

Boston, Massachusetts, United States

Bryan Heart Institute

🇺🇸

Lincoln, Nebraska, United States

Caromont Heart/Gaston Memorial Hospital

🇺🇸

Gastonia, North Carolina, United States

Duke Cardiology of Lumberton Research/Southeastern Regional Medical Cente

🇺🇸

Lumberton, North Carolina, United States

Akron General Medical Center

🇺🇸

Akron, Ohio, United States

The Sisters of Mercy of Hamilton, Ohio dba Mercy Hospital Fairfield

🇺🇸

Fairfield, Ohio, United States

Oklahoma Heart Hospital

🇺🇸

Oklahoma City, Oklahoma, United States

The Miriam Hosptial

🇺🇸

Providence, Rhode Island, United States

The Heart Hospital Baylor Plano - Research Insititute

🇺🇸

Plano, Texas, United States

Memorial Hospital of RI

🇺🇸

Pawtucket, Rhode Island, United States

University of Texas Health Science Center

🇺🇸

Houston, Texas, United States

CV Group Central Lynchburg/Stroobants Heart Center

🇺🇸

Lynchburg, Virginia, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

Jackson Memorial Hospital

🇺🇸

Miami, Florida, United States

Minneapolis Heart Institute

🇺🇸

Minneapolis, Minnesota, United States

St. Vincent Medical Group

🇺🇸

Indianapolis, Indiana, United States

Dayton Heart Center

🇺🇸

Dayton, Ohio, United States

Ochsner Medical Center

🇺🇸

New Orleans, Louisiana, United States

Advanced Cardiovascular Specialists

🇺🇸

Shreveport, Louisiana, United States

University of Cincinnati

🇺🇸

Cincinnatti, Ohio, United States

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