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A Study to Evaluate the Efficacy and Safety of Simtuzumab Combined With Gemcitabine for Metastatic Pancreatic Adenocarcinoma

Phase 2
Completed
Conditions
Pancreatic Cancer
Interventions
Drug: Placebo to match simtuzumab
Registration Number
NCT01472198
Lead Sponsor
Gilead Sciences
Brief Summary

This study will compare the efficacy of simtuzumab (GS-6624) versus placebo in combination with gemcitabine in adults with pancreatic cancer. The treatment phase of this study will be comprised of 2 sequential parts: an open label treatment phase and a double-blinded treatment phase.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
250
Inclusion Criteria
  • Initial diagnosis of metastatic pancreatic cancer must have occurred ≤6 weeks prior to the completion of screening.

  • The presence of measurable metastatic pancreatic cancer documented by contrast enhanced CT (or MRI) scan in addition to 1 of the following:

    1. Histological diagnosis of pancreatic adenocarcinoma confirmed by pathologist OR

    2. Pathologist confirmed histological/cytological diagnosis of adenocarcinoma consistent with pancreatic origin in conjunction with either:

      1. The presence of a mass in the pancreas OR
      2. A history of resected pancreatic carcinoma
  • Measurable disease per RECIST (ver. 1.1)

  • ECOG Performance Status of 0 or 1.

  • Adequate hepatic, hematologic and renal functions.

Exclusion Criteria
  • A history or evidence of clinically significant disorder other than metastatic cancer of the pancreas.
  • A diagnosis of pancreatic islet neoplasms.
  • Subject has undergone major surgery other than diagnosis surgery within 4 weeks of randomization
  • Presence of biliary obstruction requiring external drainage
  • Brain metastases.
  • Unstable cardiovascular function within the last 6 months of screening
  • Clinically active liver disease, including active viral hepatitis (HBV or HCV) or cirrhosis
  • Known HIV infection.
  • Uncontrolled hypertension at Screening
  • History or presence of any form of cancer, other than pancreatic cancer, within the 3 years prior to enrollment
  • Prior or concurrent anti-tumor therapy (chemotherapy, antibody therapy, molecular targeted therapy, retinoid therapy, hormonal therapy) for the treatment of inoperable locally advanced or metastatic pancreatic cancer; prior radiotherapy and chemotherapy given as pre-operative neoadjuvant therapy or radio sensitizers for locally advanced pancreatic cancer are allowed.
  • Uncontrolled systemic fungal, bacterial or viral infection
  • Participation in an investigational drug or device trial with therapeutic intent within 30 days prior to study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo (randomized)Placebo to match simtuzumabParticipants will receive placebo to match simtuzumab plus gemcitabine in cycles of 28 days for up to 3 years.
Simtuzumab 700 mg (randomized)GemcitabineParticipants will receive simtuzumab 700 mg plus gemcitabine in cycles of 28 days for up to 3 years.
Simtuzumab (open-label)SimtuzumabParticipants will receive simtuzumab 700 mg plus gemcitabine in cycles of 28 days for up to 3 years.
Simtuzumab 200 mg (randomized)SimtuzumabParticipants will receive simtuzumab 200 mg plus gemcitabine in cycles of 28 days for up to 3 years.
Simtuzumab (open-label)GemcitabineParticipants will receive simtuzumab 700 mg plus gemcitabine in cycles of 28 days for up to 3 years.
Simtuzumab 700 mg (randomized)SimtuzumabParticipants will receive simtuzumab 700 mg plus gemcitabine in cycles of 28 days for up to 3 years.
Simtuzumab 200 mg (randomized)GemcitabineParticipants will receive simtuzumab 200 mg plus gemcitabine in cycles of 28 days for up to 3 years.
Placebo (randomized)GemcitabineParticipants will receive placebo to match simtuzumab plus gemcitabine in cycles of 28 days for up to 3 years.
Primary Outcome Measures
NameTimeMethod
Progression free survivalUp to 3 years

Progression free survival is measured as time from date of randomization to the earliest event time of death regardless of cause or first indication of disease progression.

Secondary Outcome Measures
NameTimeMethod
Overall survivalUp to 3 years

Overall survival is measured as time from date of randomization to death regardless of cause.

Objective responseUp to 3 years

Objective response is assessed by the Response Evaluation Criteria In Solid Tumors (RECIST) criteria version 1.1 as complete response, partial response, stable disease, or progressive disease.

Trial Locations

Locations (56)

UCLA Community Oncology Practice

🇺🇸

Los Angeles, California, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

Comprehensive Cancer Centers of Nevada

🇺🇸

Henderson, Nevada, United States

Montana Cancer Institute Foundation c/o Montana Cancer Specialists

🇺🇸

Missoula, Montana, United States

South Carolina Oncology Associates

🇺🇸

Columbia, South Carolina, United States

Regional Oncology Dispensary

🇷🇺

Ivanovo, Russian Federation

Central Hematology Oncology Medical Group, Inc.

🇺🇸

Alhambra, California, United States

Comprehensive Blood and Cancer Center

🇺🇸

Bakersfield, California, United States

California Cancer Associates for Research and Excellence (CCARE)

🇺🇸

Fresno, California, United States

Pacific Shores Medical Group

🇺🇸

Long Beach, California, United States

Stanford University Medical Center

🇺🇸

Palo Alto, California, United States

Wilshire Oncology Medical Group, Inc.

🇺🇸

Rancho Cucamonga, California, United States

Sharp Health Care

🇺🇸

San Diego, California, United States

San Jose Medical Group

🇺🇸

San Jose, California, United States

Saint Mary's Regional Cancer Center

🇺🇸

Grand Junction, Colorado, United States

Hematology Oncology Associates, PC

🇺🇸

Stamford, Connecticut, United States

Georgia Cancer Specialists, P.C.

🇺🇸

Atlanta, Georgia, United States

Anne Arundel Medical Center, Annapolis Oncology Center

🇺🇸

Annapolis, Maryland, United States

Providence Cancer Center Oncology and Hematology Care Clinic-Eastside Portland

🇺🇸

Southfield, Michigan, United States

West Michigan Cancer Center

🇺🇸

Kalamazoo, Michigan, United States

Hematology and Oncology Associates at BridgePoint

🇺🇸

Tupelo, Mississippi, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Saint Joseph Oncology, Inc.

🇺🇸

Saint Joseph, Missouri, United States

Beth Israel Comprehensive Cancer Center

🇺🇸

New York, New York, United States

Saint Luke's-Roosevelt Hospital Center

🇺🇸

New York, New York, United States

Duke University Medical Center, Comprehensive Cancer Center

🇺🇸

Durham, North Carolina, United States

PinnacleHealth

🇺🇸

Harrisburg, Pennsylvania, United States

Tennessee Cancer Specialists

🇺🇸

Knoxville, Tennessee, United States

Abington Hematology Oncology Associates, Inc.

🇺🇸

Willow Grove, Pennsylvania, United States

Tennessee Oncology, PLLC

🇺🇸

Nashville, Tennessee, United States

Coastal Bend Cancer Center

🇺🇸

Corpus Christi, Texas, United States

University of Texas Southwestern Medical Center at Dallas

🇺🇸

Dallas, Texas, United States

San Antonio Military Medical Center

🇺🇸

Fort Sam Houston, Texas, United States

Center for Cancer and Blood Disorders, PC

🇺🇸

Fort Worth, Texas, United States

Joe Arrington Cancer Research and Treatment Center

🇺🇸

Lubbock, Texas, United States

Utah Cancer Specialists

🇺🇸

Salt Lake City, Utah, United States

Virginia Cancer Institute

🇺🇸

Richmond, Virginia, United States

Virginia Cancer Specialists, PC

🇺🇸

Fairfax, Virginia, United States

Republic Clinical Oncology Dispensary of the Ministry of Healthcare of Republic of Bashkortostan

🇷🇺

Ufa, Bashkortostan, Russian Federation

Medical Radiological Research Center of Russian Academy of Medical Sciences, Obninsk

🇷🇺

Obninsk, Kaluga, Russian Federation

State Institution of Healthcare "Arkhangelsk Regional Clinical Oncology Dispensary"

🇷🇺

Arkhangelsk, Primorskiy, Russian Federation

Republican Clinical Oncologic Dispensary of Ministry of health of Republic Tatarstan

🇷🇺

Kazan, Tatarstan, Russian Federation

Kursk Regional Oncologic Dispensary

🇷🇺

Kursk, Russian Federation

Blokhin Cancer Research Center of Russia, Dept. of clinical pharmacology

🇷🇺

Moscow, Russian Federation

State Institution "Blokhin Cancer Research Centre RAMS"

🇷🇺

Moscow, Russian Federation

Non-State Institution of healthcare "Central Clinical Hospital #1 OAO RZD

🇷🇺

Moscow, Russian Federation

Non-state Healthcare Institution "N.A. Semashko Central Clinical Hospital #2 of JSC "Russian Railway

🇷🇺

Moscow, Russian Federation

State Budgetary Healthcare Institution "Nizhny Novgorod Regional Oncological Dispensary"

🇷🇺

Nizhny Novgorod, Russian Federation

Budgetary Healthcare Institution of Omsk Region "Clinical Oncologic Dispensary"

🇷🇺

Omsk, Russian Federation

Petrov Research Oncology Institute

🇷🇺

Saint Petersburg, Russian Federation

Florida Cancer Specialists

🇺🇸

Tampa, Florida, United States

Oncology Hematology Care, Inc.

🇺🇸

Blue Ash, Ohio, United States

Birmingham Hematology and Oncology Associates, LLC

🇺🇸

Birmingham, Alabama, United States

University of South Alabama Mitchell Cancer Institute

🇺🇸

Mobile, Alabama, United States

Emerywood Hematology and Oncology

🇺🇸

High Point, North Carolina, United States

Charleston Hematology Oncology Associates, PA

🇺🇸

Charleston, South Carolina, United States

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