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enalidomide and 5azacitidine treatment versus 5azacitidine alone in patients with the blood cancers myelodysplastic syndrome or acute myeloid leukaemia

Phase 2
Completed
Conditions
Myelodysplastic syndromes (MDS)
Low marrow blast count acute myeloid leukaemia (AML)
Blood - Haematological diseases
Cancer - Leukaemia - Acute leukaemia
Registration Number
ACTRN12610000271000
Lead Sponsor
Australasian Leukaemia and Lymphoma Group
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
All
Target Recruitment
160
Inclusion Criteria

Disease diagnosis of either MDS (by World Health Organisation criteria, those with refractory anaemia and Refractory Anaemia with Ringed Sideroblasts to also have at least one clinically significant cytopenia), nonproliferative Chronic Myelomonocytic Leukaemia (CMML) or low marrow blast count AML; Eastern Cooperative Oncology Group (ECOG) 2 or less with life expectancy at least 3 months, adequate contraception and adequate renal and hepatic function, written informed consent.

Exclusion Criteria

Prior chemotherapy for MDS or AML except low dose cytarabine or hydroxyurea, any prior demethylating agent or immunomodulatory drug (including thalidomide or lenalidomide), prior diagnosis of cancer except with low risk of recurrence, significant renal, hepatic, cardiac or respiratory disease or severe active infection.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
To demonstrate improved efficacy with the combination of lenalidomide and 5azacitidine compared to 5azacitidine alone in patients with MDS and low marrow blast count AML, with acceptable toxicity of the combination. Outcome will be assessed by measures of disease response as defined by International Working Group (IWG) criteria (2006) and determined by peripheral blood counts, transfusions, bone marrow morphology and cytogenetics.[12 months from start of treatment]
Secondary Outcome Measures
NameTimeMethod
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