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A Donanemab (LY3002813) Study in Participants With Preclinical Alzheimer's Disease (TRAILBLAZER-ALZ 3)

Phase 3
Recruiting
Conditions
Alzheimer Disease
Interventions
Drug: Placebo
Registration Number
NCT05026866
Lead Sponsor
Eli Lilly and Company
Brief Summary

The main purpose of this study is to evaluate the safety and efficacy of donanemab in participants with preclinical Alzheimer's Disease (AD). Approximately 800 additional participants will be enrolled in a 12-month addendum to assess safety of a different titration regimen.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
2996
Inclusion Criteria
  • A Telephone Interview for Cognitive Status - modified (TICS-M) score reflective of intact cognitive functioning.
  • Has a phosphorylated tau (P-tau) result consistent with the presence of amyloid and early-tau pathology.
  • Has a reliable study partner and backup study partner familiar with overall function and behavior, such as day-to-day activities and cognitive abilities.
  • Have adequate literacy, vision, and hearing for neuropsychological testing at screening.
  • Contraceptive use by men or women should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies
  • Female participants include those who are infertile due to surgical sterilization (hysterectomy, bilateral oophorectomy, or tubal ligation), congenital anomaly such as Mullerian agenesis; or post menopausal (women 55 or older not on hormone therapy and had at least 12 months of spontaneous amenorrhea; or with a diagnosis of menopause prior to starting hormone replacement therapy.
Exclusion Criteria
  • Mild cognitive impairment or dementia, or significant other neurodegenerative disease that can affect cognition.
  • Current serious or unstable illnesses including cardiovascular, hepatic, renal, gastroenterologic, respiratory, endocrinologic, neurologic, psychiatric, immunologic, or hematologic disease that could interfere with the analysis of the study or a life expectancy of approximately ≤5 years.
  • History of cancer with high risk of recurrence and preventing completion of the trial.
  • History of clinically significant multiple or severe drug allergies, or severe posttreatment hypersensitivity reactions (including but not limited to erythema multiforme major, linear immunoglobulin A dermatosis, toxic epidermal necrolysis, and/or exfoliative dermatitis).
  • Have any clinically important abnormality at screening on magnetic resonance imaging (MRI) or clinical laboratory test results that could be detrimental to the participant or study integrity.
  • Have any contraindications for MRI, including claustrophobia or the presence of contraindicated metal (ferromagnetic) implants/cardiac pacemaker.
  • Have a centrally read MRI demonstrating presence of amyloid-related imaging abnormalities (ARIA-E), >4 cerebral microhemorrhages, more than 1 area of superficial siderosis, any macrohemorrhage or severe white matter disease at screening.
  • Have had prior treatment with a passive anti-amyloid immunotherapy <5 half-lives prior to randomization.
  • Have received active immunization against amyloid beta (Aβ) in any other study.
  • Have received active immunization against Aβ in any other study.
  • Current or previous use of prescription medications used as treatment for mild cognitive impairment (MCI) or AD.

Addendum 7 Exclusion Criteria for Clinicaltrials.gov:

  • Same as the main study except contraindications for florbetapir F 18 PET are exclusionary.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboPlacebo is administered intravenously
DonanemabDonanemabDonanemab administered intravenously (IV)
Primary Outcome Measures
NameTimeMethod
Time to clinical progression as measured by Clinical Dementia Rating - Global Score (CDR-GS)Estimated Up to Week 182

Time to clinical progression as measured by CDR-GS. CDR is a clinician-rated scale that provides an overall assessment of the participant's stage on the spectrum of AD dementia.

Secondary Outcome Measures
NameTimeMethod
Change from Baseline in Face Name Association Test (FNAME)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by FNAME in participants with preclinical AD.

Change from Baseline in Cogstate Brief Battery (CBB)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by CBB in participants with preclinical AD.

Change from Baseline in Montreal Cognitive Assessment (MoCA) scoreBaseline, Up to Week 182

Change from Baseline in clinical progression as measured by MoCA score in participants with preclinical AD.

Percentage of Participants with Treatment-emergent Anti-Drug Antibody (ADAs)Baseline through Week 16

Percentage of Participants with Treatment-emergent Anti-Drug Antibody (ADAs)

Change from Baseline in Behavioral Pattern Separation-Object test (BPS-O)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by BPS-O in participants with preclinical AD.

Change from Baseline in Cognitive Function Index (CFI)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by CFI in participants with preclinical AD.

Change from Baseline in International Shopping List Test (ISLT)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by ISLT in participants with preclinical AD.

Change from Baseline in Continuous Paired Associate Learning (CPAL)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by CPAL in participants with preclinical AD.

Change from Baseline in International Daily Symbol Substitution Test-Medicines (iDSSTm)Baseline, Up to Week 182

Change from Baseline in clinical progression as measured by iDSSTm in participants with preclinical AD.

Change from Baseline in Category FluencyBaseline, Up to Week 182

Change from Baseline in clinical progression as measured by Category Fluency in participants with preclinical AD.

Change from Baseline in CDR-Sum of Boxes (CDR-SB)Baseline, Up Week 32

Change from Baseline in clinical progression as measured by CDR-SB in participants with preclinical AD.

Pharmacokinetics (PK): Average Serum Donanemab Concentration at Steady StateBaseline through Week 76

PK: Average Serum Donanemab Concentration at Steady State

Trial Locations

Locations (213)

Parkway Medical Center

🇺🇸

Birmingham, Alabama, United States

Alabama Psychiatry - Birmingham - Brookwood Medical Center Drive

🇺🇸

Homewood, Alabama, United States

Rehabilitation & Neurological Services

🇺🇸

Huntsville, Alabama, United States

Care Access - 801 South Power Road, Mesa

🇺🇸

Mesa, Arizona, United States

Banner Alzheimer's Institute

🇺🇸

Phoenix, Arizona, United States

Banner Alzheimer's Institute Tucson

🇺🇸

Tucson, Arizona, United States

Center for Neurosciences

🇺🇸

Tucson, Arizona, United States

Care Access - Berkeley

🇺🇸

Berkeley, California, United States

Care Access - Beverly Hills

🇺🇸

Beverly Hills, California, United States

Velocity Clinical Research, Chula Vista

🇺🇸

Chula Vista, California, United States

Valley Clinical Trials, Inc.

🇺🇸

Northridge, California, United States

Neurology Center of North Orange County

🇺🇸

Fullerton, California, United States

Care Access - Gilroy

🇺🇸

Gilroy, California, United States

Care Access Research - Huntington Beach

🇺🇸

Huntington Beach, California, United States

Irvine Clinical Research

🇺🇸

Irvine, California, United States

Option Care - Irvine

🇺🇸

Irvine, California, United States

Kaizen Brain Center

🇺🇸

La Jolla, California, United States

Velocity Clinical Research, San Diego

🇺🇸

La Mesa, California, United States

Pacific Research Network

🇺🇸

Lemon Grove, California, United States

Healthy Brain Clinic

🇺🇸

Long Beach, California, United States

Neurovations

🇺🇸

Napa, California, United States

Care Access - Newport Beach

🇺🇸

Newport Beach, California, United States

Inland Psychiatric Medical Group

🇺🇸

Redlands, California, United States

Anderson Clinical Research

🇺🇸

Redlands, California, United States

Artemis Institute for Clinical Research

🇺🇸

San Diego, California, United States

Option Care - Riverside

🇺🇸

Riverside, California, United States

Clinical Trials Research

🇺🇸

Sacramento, California, United States

Ray Dolby Brain Health Center

🇺🇸

San Francisco, California, United States

Care Access - Los Gatos

🇺🇸

San Jose, California, United States

Syrentis Clinical Research

🇺🇸

Santa Ana, California, United States

Care Access - Santa Clarita

🇺🇸

Santa Clarita, California, United States

Option Care - Los Angeles South

🇺🇸

Santa Fe Springs, California, United States

Providence Medical Foundation

🇺🇸

Santa Rosa, California, United States

Mazur, Statner, Dutta, Nathan, PC

🇺🇸

Thousand Oaks, California, United States

Tilda Research

🇺🇸

Tustin, California, United States

Velocity Clinical Research, Panorama City

🇺🇸

Van Nuys, California, United States

Infectious Disease Doctors Medical Group, APC

🇺🇸

Walnut Creek, California, United States

Care Access - Aurora

🇺🇸

Aurora, Colorado, United States

Mountain Neurological Research Center

🇺🇸

Basalt, Colorado, United States

Denver Neurological Research

🇺🇸

Denver, Colorado, United States

Invicro

🇺🇸

New Haven, Connecticut, United States

JEM Research Institute

🇺🇸

Atlantis, Florida, United States

VIN-Julie Schwartzbard

🇺🇸

Aventura, Florida, United States

Neurology Offices of South Florida

🇺🇸

Boca Raton, Florida, United States

Excel Medical Clinical Trials

🇺🇸

Boca Raton, Florida, United States

SFM Clinical Research

🇺🇸

Boca Raton, Florida, United States

Bradenton Research Center, Inc.

🇺🇸

Bradenton, Florida, United States

Clinical Research of West Florida, Inc. (Clearwater)

🇺🇸

Clearwater, Florida, United States

Care Access - Daytona Beach

🇺🇸

Daytona Beach, Florida, United States

Care Access - Delray Beach

🇺🇸

Delray Beach, Florida, United States

Finlay Medical Research

🇺🇸

Miami, Florida, United States

Indago Research & Health Center, Inc

🇺🇸

Hialeah, Florida, United States

Infinity Clinical Research, LLC

🇺🇸

Hollywood, Florida, United States

Jacksonville Center for Clinical Research

🇺🇸

Jacksonville, Florida, United States

Care Access - Guava Street

🇺🇸

Lady Lake, Florida, United States

Accel Research Sites - St. Pete-Largo Clinical Research Unit

🇺🇸

Largo, Florida, United States

ClinCloud - Maitland

🇺🇸

Maitland, Florida, United States

K2 Medical Research

🇺🇸

Maitland, Florida, United States

ClinCloud - Viera

🇺🇸

Melbourne, Florida, United States

Merritt Island Medical Research, LLC

🇺🇸

Merritt Island, Florida, United States

San Marcus Research Clinic, Inc.

🇺🇸

Miami Lakes, Florida, United States

South Florida Research Phase I-IV

🇺🇸

Miami Springs, Florida, United States

Optimus U Corporation

🇺🇸

Miami, Florida, United States

VIN-Andrew Lerman

🇺🇸

Miami, Florida, United States

Brainstorm Research Group

🇺🇸

Miami, Florida, United States

IMIC, Inc.

🇺🇸

Miami, Florida, United States

VIN-Victor Faradji

🇺🇸

Miami, Florida, United States

Adult Medicine of Lake County

🇺🇸

Mount Dora, Florida, United States

Suncoast Clinical Research, Inc.

🇺🇸

New Port Richey, Florida, United States

Renstar Medical Research

🇺🇸

Ocala, Florida, United States

Charter Research - Winter Park

🇺🇸

Orlando, Florida, United States

Headlands Research Orlando

🇺🇸

Orlando, Florida, United States

Pines Care Research Center, LLC

🇺🇸

Pembroke Pines, Florida, United States

VIN- Margarita Almeida El-Ramey

🇺🇸

Pembroke Pines, Florida, United States

Emerald Coast Neurology - Airport Boulevard

🇺🇸

Pensacola, Florida, United States

Progressive Medical Research

🇺🇸

Port Orange, Florida, United States

Care Access - Sun City Center - Cypress Village Boulevard

🇺🇸

Sun City Center, Florida, United States

Care Access - Tamarac

🇺🇸

Tamarac, Florida, United States

Clinical Research of West Florida

🇺🇸

Tampa, Florida, United States

K2 Medical Research - Tampa

🇺🇸

Tampa, Florida, United States

Stedman Clinical Trials

🇺🇸

Tampa, Florida, United States

Vicis Clinical Research

🇺🇸

Tampa, Florida, United States

Coram CVS/Specialty Infusion Services - Tampa

🇺🇸

Tampa, Florida, United States

Charter Research - Lady Lake

🇺🇸

The Villages, Florida, United States

Palm Beach Research Center

🇺🇸

West Palm Beach, Florida, United States

Conquest Research

🇺🇸

Winter Park, Florida, United States

Masters of Clinical Research

🇺🇸

Augusta, Georgia, United States

iResearch Atlanta

🇺🇸

Decatur, Georgia, United States

Center for Advanced Research & Education

🇺🇸

Gainesville, Georgia, United States

Meridian Clinical Research, LLC

🇺🇸

Savannah, Georgia, United States

SKY Clinical Research Network Group-Blake

🇺🇸

Union City, Georgia, United States

North Georgia Clinical Research

🇺🇸

Woodstock, Georgia, United States

Northwest Clinical Trials

🇺🇸

Boise, Idaho, United States

IMA Clinical Research - Chicago

🇺🇸

Chicago, Illinois, United States

Neurological Associates Albany

🇺🇸

Albany, New York, United States

University of Chicago Medical Center

🇺🇸

Chicago, Illinois, United States

Great Lakes Clinical Trials - Andersonville

🇺🇸

Chicago, Illinois, United States

Uptown Research Institute

🇺🇸

Chicago, Illinois, United States

AMITA Health - Alexian Brothers Neurosciences Institute Clinical Research

🇺🇸

Elk Grove Village, Illinois, United States

Care Access - Fairview Heights

🇺🇸

Fairview Heights, Illinois, United States

Great Lakes Clinical Trials - Gurnee

🇺🇸

Gurnee, Illinois, United States

Accellacare - DuPage

🇺🇸

Lombard, Illinois, United States

Coram CVS/Specialty Infusion Services - Fort Wayne

🇺🇸

Fort Wayne, Indiana, United States

Care Access - South Indianapolis

🇺🇸

Indianapolis, Indiana, United States

Josephson Wallack Munshower Neurology, PC

🇺🇸

Indianapolis, Indiana, United States

Covenant Medical Center

🇺🇸

Waterloo, Iowa, United States

College Park Specialty Center

🇺🇸

Overland Park, Kansas, United States

Norton Brownsboro Hospital

🇺🇸

Louisville, Kentucky, United States

Optum Infusion - Baton Rouge

🇺🇸

Baton Rouge, Louisiana, United States

Care Access - Lake Charles

🇺🇸

Lake Charles, Louisiana, United States

MD Medical Research

🇺🇸

Oxon Hill, Maryland, United States

ActivMed Practices and Research

🇺🇸

Methuen, Massachusetts, United States

Boston Center for Memory

🇺🇸

Newton, Massachusetts, United States

Care Access - Quincy

🇺🇸

Quincy, Massachusetts, United States

MedVadis Research Corporation

🇺🇸

Waltham, Massachusetts, United States

Revival Research Institute

🇺🇸

Southfield, Michigan, United States

Minneapolis Clinic of Neurology - Burnsville Office

🇺🇸

Burnsville, Minnesota, United States

Coram CVS/Specialty Infusion Services - Mendota Heights

🇺🇸

Mendota Heights, Minnesota, United States

SKY Clinical Research Network Group - Hall

🇺🇸

Fayette, Mississippi, United States

SKY Clinical Research Network Group-Quinn

🇺🇸

Ridgeland, Mississippi, United States

Citizens Memorial Hospital District

🇺🇸

Bolivar, Missouri, United States

Clinical Research Professionals

🇺🇸

Chesterfield, Missouri, United States

IMA Clinical Research - St. Louis

🇺🇸

Saint Louis, Missouri, United States

Coram CVS/Specialty Infusion Services - Henderson

🇺🇸

Henderson, Nevada, United States

Option Care - Las Vegas

🇺🇸

Las Vegas, Nevada, United States

Las Vegas Medical Research

🇺🇸

Las Vegas, Nevada, United States

IMA Clinical Research Hoboken

🇺🇸

Hoboken, New Jersey, United States

The Cognitive and Research Center of New Jersey

🇺🇸

Springfield, New Jersey, United States

IMA Clinical Research Warren

🇺🇸

Warren, New Jersey, United States

Albuquerque Neuroscience Inc.

🇺🇸

Albuquerque, New Mexico, United States

IMA Clinical Research Albany

🇺🇸

Albany, New York, United States

Prime Global Research

🇺🇸

Bronx, New York, United States

Velocity Clinical Research, Syracuse

🇺🇸

East Syracuse, New York, United States

IMA Clinical Research Westchester

🇺🇸

Hartsdale, New York, United States

IMA Clinical Research

🇺🇸

New York, New York, United States

South Shore Neurologic Associates

🇺🇸

Patchogue, New York, United States

Richmond Behavioral Associates

🇺🇸

Staten Island, New York, United States

Asheville Neurology Specialists

🇺🇸

Asheville, North Carolina, United States

Care Access - Charlotte

🇺🇸

Charlotte, North Carolina, United States

Care Access - Fayetteville

🇺🇸

Fayetteville, North Carolina, United States

Care Access - Greensboro

🇺🇸

Greensboro, North Carolina, United States

Medication Management

🇺🇸

Greensboro, North Carolina, United States

Care Access - Kinston

🇺🇸

Kinston, North Carolina, United States

Monroe Biomedical Research

🇺🇸

Monroe, North Carolina, United States

Carteret Medical Group

🇺🇸

Morehead City, North Carolina, United States

Care Access - Raleigh

🇺🇸

Raleigh, North Carolina, United States

Accellacare - Winston-Salem

🇺🇸

Winston-Salem, North Carolina, United States

NeuroScience Research Center

🇺🇸

Canton, Ohio, United States

Hometown Urgent Care and Research - Cincinnati

🇺🇸

Dayton, Ohio, United States

Neurology Diagnostics, Inc.

🇺🇸

Dayton, Ohio, United States

Care Access - Lima

🇺🇸

Lima, Ohio, United States

North Star Medical Research

🇺🇸

Middleburg Heights, Ohio, United States

Care Access - Youngstown

🇺🇸

Poland, Ohio, United States

Central States Research

🇺🇸

Tulsa, Oklahoma, United States

Optum Infusion - Bend

🇺🇸

Bend, Oregon, United States

Velocity Clinical Research, Medford

🇺🇸

Medford, Oregon, United States

Center for Cognitive Health

🇺🇸

Portland, Oregon, United States

The Clinical Trial Center, LLC

🇺🇸

Jenkintown, Pennsylvania, United States

Care Access - Pottsville

🇺🇸

Pottsville, Pennsylvania, United States

Care Access Research - Warwick

🇺🇸

Warwick, Rhode Island, United States

Care Access - Anderson

🇺🇸

Anderson, South Carolina, United States

Velocity Clinical Research, Anderson

🇺🇸

Anderson, South Carolina, United States

VitaLink Research - Columbia

🇺🇸

Columbia, South Carolina, United States

Velocity Clinical Research, Gaffney

🇺🇸

Gaffney, South Carolina, United States

VitaLink Research - Greenville

🇺🇸

Greenville, South Carolina, United States

Care Access - Mauldin

🇺🇸

Mauldin, South Carolina, United States

VitaLink Research - Spartanburg

🇺🇸

Spartanburg, South Carolina, United States

VitaLink Research - Union

🇺🇸

Union, South Carolina, United States

Health Concepts

🇺🇸

Rapid City, South Dakota, United States

Neurology Clinic

🇺🇸

Cordova, Tennessee, United States

Clinical Neuroscience Solutions, Inc. dba CNS Healthcare

🇺🇸

Memphis, Tennessee, United States

Texas Diabetes & Endocrinology, P.A.

🇺🇸

Austin, Texas, United States

Senior Adults Specialty Research

🇺🇸

Austin, Texas, United States

Gadolin Research

🇺🇸

Beaumont, Texas, United States

Headlands Research - Brownsville

🇺🇸

Brownsville, Texas, United States

Conroe Willis Medical Research

🇺🇸

Conroe, Texas, United States

Advanced Neuro Research Center - ANRC

🇺🇸

El Paso, Texas, United States

Care Access - Georgetown

🇺🇸

Georgetown, Texas, United States

Optum Infusion - Houston

🇺🇸

Houston, Texas, United States

The University of Texas Health Science Center at Houston

🇺🇸

Houston, Texas, United States

Next Level Urgent Care

🇺🇸

Houston, Texas, United States

Family Practice Center

🇺🇸

McAllen, Texas, United States

El Faro Health and Therapeutics

🇺🇸

Rio Grande City, Texas, United States

Benchmark Research - Knickerbocker

🇺🇸

San Angelo, Texas, United States

Diagnostics Research Group

🇺🇸

San Antonio, Texas, United States

Consano Clinical Research, LLC

🇺🇸

Shavano Park, Texas, United States

Texas Valley Clinical Research

🇺🇸

Weslaco, Texas, United States

The Memory Clinic

🇺🇸

Bennington, Vermont, United States

Care Access - Arlington

🇺🇸

Arlington, Virginia, United States

Option Care - Chantilly

🇺🇸

Chantilly, Virginia, United States

Dominion Medical Associates, Inc.

🇺🇸

Richmond, Virginia, United States

Northwest Clinical Research Center

🇺🇸

Bellevue, Washington, United States

Universal Research Group

🇺🇸

Tacoma, Washington, United States

Optum Infusion - Woodinville

🇺🇸

Woodinville, Washington, United States

Exemplar Research

🇺🇸

Morgantown, West Virginia, United States

National Center for Geriatrics and Gerontology

🇯🇵

Obu, Aichi, Japan

Oita University Hospital

🇯🇵

Yufu, Oita, Japan

Medical Corporation Heishinkai OCROM Clinic

🇯🇵

Suita-shi, Osaka, Japan

The University of Tokyo Hospital

🇯🇵

Bunkyo-ku, Tokyo, Japan

Tokyo-Eki Center-building Clinic

🇯🇵

Chuo-ku, Tokyo, Japan

Fukuwa Clinic

🇯🇵

Chuo-ku, Tokyo, Japan

P-One Clinic

🇯🇵

Hachioji, Tokyo, Japan

Tokyo Metropolitan Geriatric Hospital

🇯🇵

Itabashi, Tokyo, Japan

Heishinkai Medical Group ToCROM Clinic

🇯🇵

Shinjuku-ku, Tokyo, Japan

Samoncho Clinic

🇯🇵

Shinjuku, Tokyo, Japan

Instituto De Neurologia Dra. Ivonne Fraga

🇵🇷

San Juan, Puerto Rico

Mindful Medical Research

🇵🇷

San Juan, Puerto Rico

University of Puerto Rico - Medical Sciences Campus_Do not use - Duplicate facility

🇵🇷

San Juan, Puerto Rico

AMC Nishiumeda Clinic

🇯🇵

Osaka, Japan

Tokyo Asbo Clinic

🇯🇵

Tokyo, Japan

SCB Research Center

🇵🇷

Bayamon, Puerto Rico

Dr. Samuel Sanchez PSC

🇵🇷

Caguas, Puerto Rico

INSPIRA Clinical Research

🇵🇷

San Juan, Puerto Rico

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