MedPath

Neoadjuvant Pyrotinib in HR-positive and HER2-low High-risk Early Breast Cancer

Phase 3
Recruiting
Conditions
Early-stage Breast Cancer
Breast Cancer Invasive
HER2 Low Breast Carcinoma
Hormone-receptor-positive Breast Cancer
Interventions
Drug: Pyrotinib, epirubicin or doxorubicin, cyclophosphamide, paclitaxel
Registration Number
NCT06144944
Lead Sponsor
Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University
Brief Summary

This is a multi-center, open-lable, prospective, randomized phase III clinical trial to further validate the efficacy and safety of neoadjuvant pyrotinib combined with chemotherapy in HR-positive/HER2-low (IHC 2+/FISH-negative) high-risk early breast cancer

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
160
Inclusion Criteria
  • Must participate voluntarily, sign the informed consent form, and have good compliance
  • Aged ≥ 18 and ≤ 70 years old with ECOG PS score of 0-1
  • Histopathological newly diagnosed, unilateral, primary invasive breast cancer
  • Histopathological hormone receptor-positve ( estrogen receptor and/or progesterone receptor ≥ 10% stained cells) and HER2-low (immunochemistry 2+ with fluorescent in situ hybridization negative)
  • TNM stage-IIb/III, or TNM stage-IIa with high risk (N+, G3, or MammaPrint High-risk)
  • At least one evaluable target breast lesion according to Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1
  • Left ventricular ejection fraction ≥ 55%, Fridericia-corrected QT interval < 450 ms in males and < 470 ms in females
  • White blood cell count: ≥ 3.0 × 10^9/L, absolute neutrophil count: ≥ 1.5 × 10^9/L, platelet count: ≥ 100 × 10^9/L, hemoglobin: ≥ 90 g/L
  • Aspartate aminotransferase and alanine aminotransferase: ≤ 2.5 × ULN, alkaline phosphatase: ≤ 2.5 × ULN, blood total bilirubin: ≤ 1.5 × ULN, serum creatinine: ≤ 1.5 × ULN
  • Non-menopausal or non-surgically sterilized female patients identified as non-pregnant and non-lactating and consented to contraception both during the trial and within 6 months after the last administration of the test drug
Exclusion Criteria
  • Metastatic BC, bilateral BC, occult BC, inflammatory BC, or with other malignant tumors
  • Known history of hypersensitivity to the study drugs
  • Patients who need receive other anti-tumor treatments (except for OFS) during neoadjuvant therapy as judged by the investigators
  • With severe cardiac disease or discomfort that is not expected to tolerate treatment, including but not limited to: a) arrhythmia that requires medication or is clinically significant, or high-grade atrioventricular block, b) unstable angina, myocardial infarction, heart failure or clinically significant heart valve disease, c) poorly controlled hypertension or any heart disease unsuitable for participation in this trial as determined by the investigators
  • Patients who participated in a clinical trial of another drug within 4 weeks prior to randomization or underwent BC-free surgery within 4 weeks or had not fully recovered after BC-free surgery
  • Other malignancy in the past 5 years, other than cured cervical carcinoma in situ, basal or squamous cell carcinoma of skin
  • Patients who had basic gastrointestinal diseases (especially long-term history of diarrhea or/and constipation), inability to swallow, intestinal obstruction or other factors will affect drugs administration and absorption
  • Presence of accompanying diseases that may pose serious risks to the safety of the patient or may affect the patient's ability to complete the study (including but not limited to severe diabetes mellitus, active infection, thyroid disorders, etc.) as judged by the investigator
  • With a history of immunodeficiency, including acquired or congenital immunodeficiencies, or a history of organ transplantation
  • Past history of confirmed neurological or mental disorders, including epilepsy or dementia
  • Other conditions of the subject determined by the investigator to be unsuitable for the study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Neoadjuvant chemotherapyEpirubicin or doxorubicin, cyclophosphamide, paclitaxel-
Neoadjuvant pyrotinib combined with chemotherapyPyrotinib, epirubicin or doxorubicin, cyclophosphamide, paclitaxel-
Primary Outcome Measures
NameTimeMethod
Residual Cancer Burden 0/1 rate as assessed by independent central reviewWithin 4 weeks after surgery

The proportion of patients with RCB 0/I after neoadjuvant therapy according to the online Residual Cancer Burden Calculator provided by the MD Anderson Cancer Center as assessed by independent central review

Secondary Outcome Measures
NameTimeMethod
Residual Cancer Burden 0/1 rate as assessed by local pathology reviewWithin 4 weeks after surgery

The proportion of patients with RCB 0/I after neoadjuvant therapy according to the online Residual Cancer Burden Calculator provided by the MD Anderson Cancer Center as assessed by local pathology review

Pathological complete response rateWithin 4 weeks after surgery

The proportion of patients with no residual invasive tumor cells in the breast and axillary nodes, regardless of ductal carcinoma in situ

Objective response rateWithin 2 weeks of breast MR examination

The percentage of patients who achieved a complete or partial response in breast according to the RECIST, version 1.1, based on MRI, at the end of cycle 2 neoadjuvant therapy and at the end of cycle 8 neoadjuvant therapy

Health-related Quality of Life 1Within 7 days before the first treatment and the end of each cycle (each cycle is 21 days)

The score of European Organization for Research and Treatment of Cancer Quality of Life Questionnaire Core-30 (version 3)

5-year event-free survivalDuring the 5 years after random assignment

the time from random assignment until any relapse, unequivocal tumor progression, or any-cause death

Breast conservation surgery rateWithin 4 weeks after surgery

The proportion of patients who had successful breast conservation surgery after neoadjuvant therapy

Health-related Quality of Life 2Within 7 days before the first treatment and the end of each cycle (each cycle is 21 days)

The score of Breast Cancer-Specific Module (QLQ-BR23)

Safety (AEs+SAEs)from signing the informed consent form until 2 years after completion of neoadjuvant treatment

General safety will be assessed according to the National Cancer Institute Common Terminology Criteria for Adverse Events (version 5.0). Ovarian toxicity will be evaluated by menstrual status and FSH and E2

Biomarkers (Immune cell subpopulations quantities)Within 4 weeks after surgery

The association between immune cell subpopulations quantities and RCB

5-year overall survivalDuring the 5 years after random assignment

the time from random assignment until any-cause death

Trial Locations

Locations (1)

Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University

🇨🇳

Guangzhou, Guangdong, China

© Copyright 2025. All Rights Reserved by MedPath