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A Safety and Tolerability Study of Neural Stem Cells (NR1) in Subjects with Chronic Ischemic Subcortical Stroke (ISS)

Phase 1
Active, not recruiting
Conditions
Ischemic Stroke
Interventions
Biological: Neural Stem Cells
Registration Number
NCT04631406
Lead Sponsor
Gary Steinberg, MD, PhD
Brief Summary

Evaluation of the safety and tolerability of escalating doses of NR1 administered intracerebrally at a single time-point post-injury to subjects with chronic ISS with or without cortical stroke.

Detailed Description

Evaluation of the safety and tolerability of escalating doses of NR1 administered intracerebrally at a single time-point post-injury to subjects with chronic ISS with or without cortical stroke. The study will be a dose escalation using up to 4 cohorts each at a single dose level, of intracerebral administration of NR1 cells. Secondary objectives are to evaluate clinical and radiologic responses as well as utility of efficacy measurement tools.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
30
Inclusion Criteria
  • Age 18 - 75 years
  • History of ischemic subcortical stroke in the middle cerebral artery and/or lenticulostriate artery 6 to 60 months from time of stroke
  • Ability of subject to understand and provide written Informed Consent
  • Willing to take tacrolimus (Prograf) 2 days before and for 2 months after transplant
Exclusion Criteria
  • Stroke lesion less than 1 cubic centimeter or greater than 100 cubic centimeters measured by MRI
  • Index stroke is lacunar infarct less than 1 year old
  • History or presence of any major neurological disease
  • History of active cancer other than basal or squamous cell skin cancers
  • History of seizures
  • Pregnant or breast-feeding

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Neural Stem cells injected intracerebrallyNeural Stem CellsSubject cohorts will be treated with increasing doses of Neural Stem Cells injected intracerebrally using a traditional 3+3 trial design
Primary Outcome Measures
NameTimeMethod
Incidence of Treatment-Emergent Adverse Events0-12 months

Number of participants with treatment-related adverse events as assessed by CTCAE v4.0

Fugl Meyer (FM) motor score0-12 months

Change in neurologic functional outcome to evaluate efficacy post-injection as defined by change in Fugl Meyer motor score in comparison to baseline

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Stanford Health Center

🇺🇸

Stanford, California, United States

Stanford Health Center
🇺🇸Stanford, California, United States

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