A Long-term Study for the Outcome of Pompe Disease

Recruiting

• Conditions: Pompe Disease

• Registration Number: NCT02399748
• Lead Sponsor: National Taiwan University Hospital

Brief Summary

Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.

Detailed Description

Not available

Study Timeline

• Study Start: 2007-04
• Study First Submitted: 2015-03-21
• Study First Submitted QC: 2015-03-25
• Study First Posted: 2015-03-26
• Status Verified: 2017-07
• Last Update Submitted: 2017-07-13
• Last Update Posted: 2017-07-18
• Primary Completion: 2026-12
• Study Completion: 2026-12

Recruitment & Eligibility

• Status: RECRUITING
• Sex: All
• Target Recruitment: 50

Inclusion Criteria

Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy

Exclusion Criteria

No

Study & Design

• Study Type: OBSERVATIONAL
• Study Design: Not specified

Primary Outcome Measures

Name	Time	Method
all cause morbidities	10 years

Trial Locations

Locations (1)

National Taiwan University Hospital; 🇨🇳 Taipei, Taiwan