Study of Efficacy of Sirolimus in Patients with Activated PI3Kdelta Syndrome
Not Applicable
- Conditions
- Activated PI3Kdelta Syndrome
- Registration Number
- JPRN-UMIN000023046
- Lead Sponsor
- Department of Human Genetics National Center for Child Health and Development
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up complete
- Sex
- All
- Target Recruitment
- 5
Inclusion Criteria
Not provided
Exclusion Criteria
1) Patients with severe infections 2) Patients with severe thrombocytopenia
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method