MedPath

sability Study of Mobile App for Long-Term Follow-Up in Gene Therapy

Not Applicable
Recruiting
Conditions
Patients treated with onasemnogene abeparvovec
Registration Number
JPRN-UMIN000046480
Lead Sponsor
ational Center for Child Health and Development
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
10
Inclusion Criteria

Not provided

Exclusion Criteria

None

Study & Design

Study Type
Observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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