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A Study of ME-401 in Subjects With CLL/SLL, FL, and B-cell Non Hodgkin's Lymphoma

Phase 1
Terminated
Conditions
Chronic Lymphocytic Leukemia (CLL)
Small Lymphocytic Lymphoma (SLL)
Marginal Zone B Cell Lymphoma
High Grade Non-Hodgkin's Lymphoma
Mantle Cell Lymphoma (MCL)
Follicular Lymphoma (FL)
Diffuse Large B-cell Lymphoma (DLBCL)
Interventions
Registration Number
NCT02914938
Lead Sponsor
MEI Pharma, Inc.
Brief Summary

A Three-Arm Study of ME-401 in Subjects with Relapsed/Refractory CLL/SLL or FL, of ME-401 in Combination with Rituximab in Subjects with Relapsed/Refractory CLL/SLL or B-cell NHL, and of ME-401 in Combination with Zanubrutinib in Subjects with Relapsed/Refractory CLL/SLL or B-cell NHL

Detailed Description

This is a three-arm study of ME-401 alone, of ME-401 in combination with rituximab, and of ME-401 in combination with zanubrutinib in subjects with relapsed/refractory CLL/SLL or B cell NHL. The 3 arms of the study will be conducted in parallel, with subject allocation to ME-401 alone, ME-401 plus rituximab, or ME-401 plus zanubrutinib based on disease type and availability of an open enrollment slot.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
97
Inclusion Criteria

Not provided

Exclusion Criteria
  • Known histological transformation from CLL to an aggressive lymphoma
  • Uncontrolled autoimmune hemolytic anemia or immune thrombocytopenia
  • Subjects who have tested positive for hepatitis B surface antigen and/or hepatitis B core antibody
  • Positive for hepatitis C virus antibody (HCV Ab) or human immunodeficiency virus (HIV) antibody
  • Ongoing drug-induced pneumonitis
  • History of clinically significant cardiovascular abnormalities
  • History of severe bleeding disorders (ME-401 plus zanubrutinib arm only)
  • Known central nervous system (CNS) hemorrhage or stroke within 6 months prior to start of study drugs (ME-401 plus zanubrutinib arm only)

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
ME-401 AloneME-401This arm is an open-label, dose escalation study to determine the safety, efficacy and pharmacokinetics of ME-401 along with the mBED, MTD, and DLTs. There are 4 planned cohorts which may enroll up to 61 subjects.
ME-401 in Combination with RituximabME-401The second arm is an open label study to evaluate the safety, efficacy, and pharmacokinetics of ME-401 in combination with rituximab in subjects with various B-cell malignancies. There are two planned cohorts which may enroll up to 30 subjects.
ME-401 in Combination with ZanubrutinibME-401The third arm is an open label study evaluating the safety, efficacy, MTD, DLT and pharmacokinetics of ME-401 in combination with zanubrutinib in subjects with various B-cell malignancies. This arm will include 2 stages: a safety evaluation stage (cohort of 6-12 subjects) and a disease-specific expansion cohort stage (up to 74 subjects).
ME-401 in Combination with RituximabRituximabThe second arm is an open label study to evaluate the safety, efficacy, and pharmacokinetics of ME-401 in combination with rituximab in subjects with various B-cell malignancies. There are two planned cohorts which may enroll up to 30 subjects.
ME-401 in Combination with ZanubrutinibZanubrutinibThe third arm is an open label study evaluating the safety, efficacy, MTD, DLT and pharmacokinetics of ME-401 in combination with zanubrutinib in subjects with various B-cell malignancies. This arm will include 2 stages: a safety evaluation stage (cohort of 6-12 subjects) and a disease-specific expansion cohort stage (up to 74 subjects).
Primary Outcome Measures
NameTimeMethod
Minimum Biologically Effective Dose (mBED) of ME-401 alone1 year

The mBED will be defined as the dose that is safe and that achieves an objective response rate that is not less than 30%.

Maximally Tolerated Dose (MTD) of ME-401 alone1 year

The MTD will be determined as the maximum dose that is safe. DLT rate closest to .25 and not to exceed 2 DLTs in 6 subjects

Determine the MTD of ME-401 plus zanubrutinib1 year

The MTD of ME-401 is defined as the dose level with a DLT rate closest to 0.25.

Determine the DLTs of ME-401 plus zanubrutinibwithin the first 56 days

DLTs will be measured by the number of treatment related AEs that occur within the first 56 days of ME-401 plus zanubrutinib

Evaluate the safety and tolerability of ME-401 plus zanubrutinib1 year

Safety and tolerability will be measured by the number of treatment related AEs

Dose Limiting Toxicities (DLTs) of ME-401 alonewithin the first 56 days

DLTs will be measured by the number of treatment related AEs that occur within the first 56 days of ME-401 administration, is considered clinically significant by the P.I. and occurs in the presence of supportive care

Evaluate the safety and tolerability of ME-401 plus rituximab1 year

Safety and tolerability will be measured by the number of treatment related AEs

Secondary Outcome Measures
NameTimeMethod
Evaluate the PK (Cmax) of ME-401 alone2 years

Determined by Peak Plasma Concentration (Cmax)

Efficacy of ME-401 with rituximab2 years

The efficacy of ME-401 with Rituximab will be determined by the overall response (OR) of subjects calculated as the percent of subjects achieving a complete remission (CR), duration of response (DOR) or Progression Free survival (PFS) according to the International Workshop on Chronic Lymphocytic Leukemia (iwCLL)

Evaluate the PK (AUC) of ME-401 with rituximab2 years

Determined by the Area Under the Concentration time curve (AUC)

Evaluate the PK (Cmax) of ME-401 with rituximab2 years

Determined by Peak Plasma Concentration (Cmax)

Efficacy of ME-401 with zanubrutinib2 years

The efficacy of ME-401 with zanubrutinib will be assessed by the overall response (OR) of subjects calculated as the percent of subjects achieving a complete remission (CR), Duration of response (DOR) and progression free survival (PFS)

Evaluate the PK (AUC) of ME-401 in combination with zanubrutinib2 years

Determined by the Area Under the Concentration time curve (AUC)

Evaluate the PK (Cmax) of ME-401 in combination with zanubrutinib2 years

Determined by Peak Plasma Concentration (Cmax)

Safety profile of ME-401 alone1 year

Safety profile will be measured by number of participants with treatment-related adverse events as assessed by CTCAE v4.0

Efficacy of ME-401 alone as assessed by (OR)2 years

The efficacy of ME-401 alone will be assessed by the overall response (OR) of subjects which is calculated as the percent of subjects achieving complete response (CR), minimal disease negativity (MRD), duration of response (DOR) and progression free survival (PFS).

Evaluate the (AUC) PK of ME-401 alone2 years

Determined by the Area Under the Concentration time curve (AUC)

Trial Locations

Locations (18)

Swedish Cancer Institute

🇺🇸

Issaquah, Washington, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Compassionate Care

🇺🇸

Corona, California, United States

Memorial Sloan Kettering

🇺🇸

Uniondale, New York, United States

Vanderbilt

🇺🇸

Nashville, Tennessee, United States

Dana Farber

🇺🇸

Boston, Massachusetts, United States

Stony Brook

🇺🇸

Stony Brook, New York, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Sylvester Comprehensive Cancer Center (Univ of Miami School of Med)

🇺🇸

Miami, Florida, United States

MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Swedish Cancer Center

🇺🇸

Seattle, Washington, United States

University of Arizona

🇺🇸

Tucson, Arizona, United States

lstituto Oncologico della Svizzera ltaliana Ospedale Regionale Bellinzona e Valli CH

🇨🇭

Bellinzona, Switzerland

Massachusetts General Hospital Cancer Center

🇺🇸

Boston, Massachusetts, United States

NYU Langone Laura & Isaac - Perlmutter Cancer Center

🇺🇸

New York, New York, United States

University of Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Carbone Cancer Center

🇺🇸

Madison, Wisconsin, United States

Stephenson Cancer Center

🇺🇸

Oklahoma City, Oklahoma, United States

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