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A Clinical Pharmacological Study of MT-3921 in Subjects With HTLV-1 Associated Myelopathy (HAM)

Phase 1
Completed
Conditions
HTLV-1-Associated Myelopathy (HAM)
Interventions
Biological: MT-3921
Biological: Placebo
Registration Number
NCT05240612
Lead Sponsor
Mitsubishi Tanabe Pharma Corporation
Brief Summary

The purposes of this study is to assess the safety, tolerability, and pharmacokinetics of MT-3921 in subjects with Human T-cell Leukemia Virus Type 1 (HTLV-1)-Associated Myelopathy(HAM).

Subjects meeting eligibility criteria will enter the 6-month double-blind period. Subjects will be randomized in a 2:1 ratio to receive MT-3921 or placebo in a double blind manner.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
15
Inclusion Criteria

Additional screening criteria check may apply for qualification:

  • Subjects aged 20 years or older on the day of consent
  • Subjects with a confirmed diagnosis of HAM according to the diagnostic algorithm of Practical Guideline for HAM 2019 on the day of consent
  • Subjects with an Osame's motor disability score (OMDS) of ≥4 and ≤6 at Screening and on the first day of the Treatment period (predose)
  • Subjects with no change in OMDS for at least 3 months before the day of consent
  • Subjects with a CSF concentration neopterin of ≥6 pmol/mL at Screening
  • Subjects on maintenance oral steroid therapy who have continued to receive the same dose equivalent to ≤10 mg/day of prednisolone for at least 3 months before the day of consent
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Exclusion Criteria

Additional screening criteria check may apply for qualification:

  • Subjects who have a history of anaphylaxis or clinically significant allergic reactions due to administration of antibody products
  • Subjects exhibiting or with a history of malignant tumor.
  • Subjects with adult T-cell leukemia/lymphoma (ATL) or those with positive HTLV-1 clonality test (Southern blot) at screening and suspected of having ATL
  • Subjects with spinal cord compression lesions, such as cervical spine disease, disc herniation, and ossification of the yellow ligament
  • Subjects with psychiatric disorders, epileptic seizures, or dementia.
  • Subjects with suicide attempts or suicidal ideation corresponding to item 4 or 5 on the Columbia Suicide Rating Scale (C-SSRS) at screening and/or on the first day of the Treatment period (predose)
  • Subjects exhibiting or with a history of hepatitis B virus (HBV), hepatitis C virus (HCV), or human immunodeficiency virus (HIV) infection.
  • Subjects with the novel Coronavirus disease 2019 (COVID-19)
  • Subjects with severe illness
  • Male or female subjects of childbearing potential who do not agree to use a contraceptive measure from the day of consent to 16 weeks after the last dose of the investigational medical product
  • Female subjects who are pregnant, lactating, or may be pregnant
  • Subjects who have received anti-repulsive guidance molecule (RGM) a antibody containing this investigational medical product
  • Subjects who participated in other clinical studies (including clinical trials) and received drugs (including investigational medical products) or therapy within 12 weeks before the day of consent
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Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
MT-3921MT-3921Intravenous (IV)
PlaceboPlaceboIntravenous (IV)
Primary Outcome Measures
NameTimeMethod
Percentage of subjects with adverse reactions36 weeks
Serum concentrations of MT-3921PK samples will be collected at predose, 1.5 hours, 2, 4, 8, 12, 20 (predose and 1.5 hours), 24, 36 weeks post-dose.
Percentage of subjects with adverse events36 weeks
CSF concentrations of MT-3921PK samples will be collected at 2, 4, 12, 24 weeks post-dose.
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

St. Marianna University Hospital

🇯🇵

Kawasaki-shi, Kanagawa, Japan

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