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A Study to Assess the Efficacy and Safety of ASKP1240 in de Novo Kidney Transplant Recipients

Registration Number
NCT01780844
Lead Sponsor
Astellas Pharma Global Development, Inc.
Brief Summary

The purpose of this study is to evaluate the efficacy and safety of ASKP1240, an anti-CD40 monoclonal antibody, for the prophylaxis of organ rejection after kidney transplantation. This study will compare the efficacy of basiliximab induction, ASKP1240, mycophenolate mofetil (MMF), and steroids \[calcineurin inhibitor (CNI) avoidance\] to the standard of care immunosuppressive regimen (basiliximab induction + tacrolimus + MMF + steroids). In addition, the study will compare the efficacy of basiliximab induction, ASKP1240, tacrolimus and steroids \[CNI minimization-MMF avoidance\] to the standard of care immunosuppressive regimen (basiliximab induction + tacrolimus + MMF + steroids).

Detailed Description

Subjects will be followed for 6 months. Upon completion of the first 6 months of the study, subjects may participate in the Long Term Extension period of the study. Subjects will remain on their original treatment arm up to three years post-transplant (and / or Sponsor discontinues development or the subject no longer wishes to participate in the study).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
149
Inclusion Criteria
  • Subject is a recipient of a de novo kidney from a living or deceased donor
Exclusion Criteria
  • Subject has induction therapy, other than study-assigned basiliximab, planned as part of initial immunosuppressive regimen
  • Subject has previously received or is receiving an organ transplant other than a kidney
  • Subject will receive a solitary kidney from a deceased donor < 5 years of age
  • Subject will receive a kidney with an anticipated cold ischemia time (CIT) of > 30 hours
  • Subject will receive a kidney that meets both Extended Criteria Donor (ECD) and Donation after Cardiac Death (DCD) criteria. Note: a kidney that meets either ECD or DCD criteria is eligible for inclusion
  • Subject will receive an ABO incompatible donor kidney
  • Subject has a current calculated panel reactive antibody (cPRA) level >50%

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Standard of CareMycophenolate Mofetil (MMF)Basiliximab induction + Tacrolimus + MMF + Corticosteroids
CNI avoidanceASKP1240Basiliximab induction + ASKP1240 + MMF + Corticosteroids
CNI avoidanceMycophenolate Mofetil (MMF)Basiliximab induction + ASKP1240 + MMF + Corticosteroids
CNI minimization-MMF avoidanceASKP1240Basiliximab induction + ASKP1240 + Tacrolimus + Corticosteroids
Standard of CareTacrolimusBasiliximab induction + Tacrolimus + MMF + Corticosteroids
Standard of CareBasiliximabBasiliximab induction + Tacrolimus + MMF + Corticosteroids
Standard of CarePrednisoneBasiliximab induction + Tacrolimus + MMF + Corticosteroids
Standard of CareMethylprednisoneBasiliximab induction + Tacrolimus + MMF + Corticosteroids
CNI avoidanceMethylprednisoneBasiliximab induction + ASKP1240 + MMF + Corticosteroids
CNI avoidanceBasiliximabBasiliximab induction + ASKP1240 + MMF + Corticosteroids
CNI avoidancePrednisoneBasiliximab induction + ASKP1240 + MMF + Corticosteroids
CNI minimization-MMF avoidanceTacrolimusBasiliximab induction + ASKP1240 + Tacrolimus + Corticosteroids
CNI minimization-MMF avoidanceBasiliximabBasiliximab induction + ASKP1240 + Tacrolimus + Corticosteroids
CNI minimization-MMF avoidanceMethylprednisoneBasiliximab induction + ASKP1240 + Tacrolimus + Corticosteroids
CNI minimization-MMF avoidancePrednisoneBasiliximab induction + ASKP1240 + Tacrolimus + Corticosteroids
Primary Outcome Measures
NameTimeMethod
Biopsy-proven acute (T or B cell) rejection (BPAR) (Banff 2007 Grade ≥ 1) by local review6 months
Secondary Outcome Measures
NameTimeMethod
Glomerular Filtration Rate (GFR)6 months

GFR is based on Modification of Diet in Renal Disease (4 variable-MDRD) criteria

Patient Survival6 months

Subject survival is defined as any subject who does not die during the study.

Graft Survival6 months

Graft survival is defined as any subject who does not experience graft loss during the study. Graft loss is defined as subject death, retransplantation, transplant nephrectomy, or the permanent return to dialysis (greater than 30 days).

Trial Locations

Locations (42)

Site US10038

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Pittsburgh, Pennsylvania, United States

Site US10007

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Atlanta, Georgia, United States

Site US10018

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Chicago, Illinois, United States

Site US10029

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Houston, Texas, United States

Site US10044

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Houston, Texas, United States

Site US10021

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Palo Alto, California, United States

Site US10032

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Cleveland, Ohio, United States

Site US10027

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Harrisburg, Pennsylvania, United States

Site US10026

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Greenville, North Carolina, United States

Site US10001

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Dallas, Texas, United States

Site US10006

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Birmingham, Alabama, United States

Site US10004

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San Francisco, California, United States

Site US10003

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San Francisco, California, United States

Site US10013

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Aurora, Colorado, United States

Site US10033

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Salt Lake City, Utah, United States

Site US10030

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San Diego, California, United States

Site US10041

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Augusta, Georgia, United States

Site US10037

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Chicago, Illinois, United States

Site US10010

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Chicago, Illinois, United States

Site US10014

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Baltimore, Maryland, United States

Site US10042

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Charlotte, North Carolina, United States

Site US10025

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Saint Louis, Missouri, United States

Site US10019

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Bronx, New York, United States

Site US10022

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Livingston, New Jersey, United States

Site US10031

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Buffalo, New York, United States

Site US10023

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New York, New York, United States

Site US10034

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New York, New York, United States

Site US10016

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Durham, North Carolina, United States

Site US10040

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Cleveland, Ohio, United States

Site US10035

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Nashville, Tennessee, United States

Site US10028

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Memphis, Tennessee, United States

Site US10002

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Fort Worth, Texas, United States

Site US10020

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Charlottesville, Virginia, United States

Site US10024

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Phoenix, Arizona, United States

Site US10009

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Cincinnati, Ohio, United States

Site US10005

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Madison, Wisconsin, United States

Site US10008

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Los Angeles, California, United States

Site US10045

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New Orleans, Louisiana, United States

Site US10017

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Ann Arbor, Michigan, United States

Site US10036

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Chapel Hill, North Carolina, United States

Site US10012

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Charleston, South Carolina, United States

Site US10015

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Lexington, Kentucky, United States

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