Safety study of NaPPS in pediatric patients with mucopolysaccharidosis type VI
Phase 1
Completed
- Conditions
- mucopolysaccharidosis type VI
- Registration Number
- JPRN-jRCT2080223060
- Lead Sponsor
- ReqMed Company, Ltd.
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- completed
- Sex
- All
- Target Recruitment
- 2
Inclusion Criteria
(1) Patients who are confirmly diagnosed with Mucopolysaccharidosis type VI and have assessable symptoms of cartilage and bone.
(2) Patients who are able to explain their own condition or to show their own intention.
(3) Patients who are able to walk for 6 minutes continuously.
Exclusion Criteria
Not provided
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method