Observational Prolonged Trial in Myotonic Dystrophy type 1 to Improve Qol Standards, a Taget Identification Collaboration.
- Conditions
- Myotonic Dystrofy type 1 and Dystrofia Myotonica (DM1)10029317
- Registration Number
- NL-OMON38289
- Lead Sponsor
- niversitair Medisch Centrum Sint Radboud
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Pending
- Sex
- Not specified
- Target Recruitment
- 72
Inclusion Criteria
Patients DM1, genetically proven
Older than 18 years
CIS fatigue score >35
Exclusion Criteria
Severe depression at screening
Neurologische of orthopedische co-morbiditeit
Unable to complete study questionnaires
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method <p>2.2 OUTCOMES<br /><br>See Appendix 1 for the trial outcome measurement schedule.<br /><br><br /><br>2.2.1 Primary Outcome<br /><br>The primary outcome measure will be the DM1-Activ measured at the end of the<br /><br>10-month intervention period. DM1-Activ is a specific outcome measure of<br /><br>activity and participation for patients with DM1 [Hermans 2010]. </p><br>
- Secondary Outcome Measures
Name Time Method