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Study of Quizartinib in Combination With Standard Therapies in Chinese Participants With Newly Diagnosed Acute Myeloid Leukemia (AML)

Phase 1
Completed
Conditions
Acute Myeloid Leukemia (AML)
Interventions
Registration Number
NCT03723681
Lead Sponsor
Daiichi Sankyo Co., Ltd.
Brief Summary

20 mg or 40 mg of quizartinib will be given to Chinese patients who were just diagnosed with AML. The study drug will be given to them along with standard therapies. The purpose is to find out the highest dose they can stand.

Detailed Description

This is a Phase 1, multicenter, open-label study to evaluate the safety and pharmacokinetics (PK) of quizartinib in combination with standard induction therapy and consolidation therapy in Chinese patients with newly diagnosed AML.

The quizartinib doses will be Level 1: 20 mg and Level 2: 40 mg. No increase in the quizartinib dose will be made in the same subject.

Dose-limiting toxicity associated with quizartinib occurring at each level will be assessed, and the maximum tolerated dose (MTD) will be decided using a 3 + 3 design.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
7
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Quizartinib 20 mgQuizartinibParticipants receive 20 mg quizartinib in combination with standard induction therapy and consolidation therapy once daily in the fasted state in the morning (at least 1 hour before or two hours after a meal)
Quizartinib 40 mgQuizartinibParticipants receive 40 mg quizartinib in combination with standard induction therapy and consolidation therapy once daily in the fasted state in the morning (at least 1 hour before or two hours after a meal)
Primary Outcome Measures
NameTimeMethod
Maximum Concentration (Cmax)within 56 days

Categories: quizartinib, active metabolite

Number of Participants with Dose-Limiting ToxicitiesAt the end of induction phase at approximately 56 days
Number of Participants with Adverse Events During the Trialwithin approximately 19 months
Time to Cmax (Tmax)within 56 days

Categories: quizartinib, active metabolite

Area under the Plasma Concentration-Time Curve (AUC)within 56 days

Categories: quizartinib, active metabolite

Secondary Outcome Measures
NameTimeMethod
Number of Participants with Responsewithin approximately 19 months

Categories: Complete remission (CR), CR with incomplete platelet or hematological recovery (CRi), partial remission (PR), no response (NR)

Response Rateswithin approximately 19 months

Categories: response rate (CRc + PR), composite CR (CRc: CR + CRi) rate

Trial Locations

Locations (1)

Institute of Hematology and Blood Diseases Hospital Chinese Academy of Medical Sciences

🇨🇳

Tianjin, China

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