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A Study of the Efficacy and Safety of Drug BAX 802 in Subjects with Congenital Hemophilia A with Factor VIII Inhibitors Undergoing Surgical or Other Invasive Procedures

Phase 1
Conditions
Hemophilia A with anti factor VIII
MedDRA version: 20.0Level: LLTClassification code 10053751Term: Hemophilia A with anti factor VIIISystem Organ Class: 100000004850
Therapeutic area: Diseases [C] - Blood and lymphatic diseases [C15]
Registration Number
EUCTR2015-005521-39-IT
Lead Sponsor
BAXALTA INNOVATIONS GMBH
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
Male
Target Recruitment
8
Inclusion Criteria

1. Subject is male and = 18 to = 65 years old at the time of screening
2. Subject has provided signed informed consent
3. Subject has severe (FVIII level < 1%) or moderately severe (FVIII level = 2%) CHA with inhibitors
to human FVIII, as tested at screening at the central laboratory
4. Subject requires elective surgery or other invasive procedures
5. Subject is not currently receiving or has recently received (< 30 days) ITI therapy
6. Subject has a Karnofsky performance score of = 60
7. Subject is human immunodeficiency virus negative (HIV-); or HIV+ with stable disease and
CD4+ count = 200 cells/mm3 at screening
8. Subject is hepatitis C virus negative (HCV-) by antibody or polymerase chain reaction (PCR) testing;
or HCV+ with chronic stable hepatitis disease
9. Subject is willing and able to comply with the requirements of the protocol.
Are the trial subjects under 18? no
Number of subjects for this age range: 1
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 14
F.1.3 Elderly (>=65 years) no
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

1. The subject requires emergency surgery
2. The subject’s weight is < 35 kg or > 120 kg
3. Clinically symptomatic liver disease (eg, = 5 X upper limit of normal alanine aminotransferase
[ALT], as confirmed by central laboratory at screening, clinical evidence of portal hypertension,
severe hypoalbuminemia or a documented prothrombin time/international normalized ratio [PT/INR]
> 1.5)
4. Clinically symptomatic renal disease (serum creatinine > 2.0 mg/dL), as confirmed by central
laboratory at screening
5. Anti-porcine inhibitor > 10 Bethesda units (BU) prior to surgery
6. Platelet count < 100,000/µL
7. Subject has another active coagulation disorder, other than hemophilia A, as per the medical history
8. Planned use of a-interferon with or without ribavarin for HCV infected patients or planned use of a
protease inhibitor for HIV-infected patients. Patients currently taking any of these medications for
= 30 days are eligible
9. Known hypersensitivity to rpFVIII, or hamster or murine proteins
10. Subject has been exposed to an IP within 30 days prior to enrollment or is scheduled to participate in
another clinical study involving an IP or investigational device during the course of this study
11. Unable to tolerate quantity of blood to be drawn for protocol procedures
12. Subject is a family member or employee of the investigator

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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