The natural history study of ambulatory patients with Duchenne muscular dystrophy
Not Applicable
- Conditions
- Duchenne muscular dystrophy
- Registration Number
- JPRN-UMIN000030562
- Lead Sponsor
- ational Center of Neurology and Psychiatry (NCNP)
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up continuing
- Sex
- Male
- Target Recruitment
- 33
Inclusion Criteria
Not provided
Exclusion Criteria
1) Patients with clinically apparent symptoms of cardiac failure and/or respiratory failure as determined by the investigators 2) Patients continuously using a ventilator (use of non-invasive positive-pressure ventilation [NPPV] during sleep is allowed) 3) Patients with behavior abnormalities including intellectual disability, autistic tendency, and attention deficit hyperactivity disorder that, in the opinion of the investigators, could prevent to conduct the assessment of motor function 4) Other patients as determined by the investigators to be ineligible to participate in this study 5) Patients participating in another clinical trial at baseline
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Motor function test
- Secondary Outcome Measures
Name Time Method Activities of daily living (ADL) Patient reported outcome (PRO) Acceleration meter/activity meter Subject demographics