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I-SPY TRIAL: Neoadjuvant and Personalized Adaptive Novel Agents to Treat Breast Cancer

Phase 2
Recruiting
Conditions
HER2-negative Breast Cancer
Hormone Receptor Positive Tumor
Angiosarcoma
TNBC - Triple-Negative Breast Cancer
Breast Neoplasms
Breast Tumors
HER2-positive Breast Cancer
Hormone Receptor Negative Tumor
Breast Cancer
Early-stage Breast Cancer
Interventions
Registration Number
NCT01042379
Lead Sponsor
QuantumLeap Healthcare Collaborative
Brief Summary

The purpose of this study is to further advance the ability to practice personalized medicine by learning which new drug agents are most effective with which types of breast cancer tumors and by learning more about which early indicators of response (tumor analysis prior to surgery via magnetic resonance imaging (MRI) images along with tissue and blood samples) are predictors of treatment success.

Detailed Description

I-SPY2 will assess the efficacy of novel drugs in sequence with standard chemotherapy. The goal is identify treatment strategies for subsets on the basis of molecular characteristics (biomarker signatures) of their disease with high estimated pCR rate. As described for previous adaptive trials, novel regimens with sufficiently high activities alone and contribute to treatment strategies that show a high Bayesian predictive probability of being more effective than the dynamic control will graduate from the trial with their corresponding biomarker signature(s). Treatment strategies will be dropped if they show a low probability of improved efficacy with any biomarker signature. New drugs will enter as those that have undergone testing complete their evaluation.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
5000
Inclusion Criteria
  • Histologically confirmed invasive cancer of the breast
  • Clinically or radiologically measureable disease in the breast after diagnostic biopsy, defined as longest diameter greater than or equal to 25 mm (2.5cm)
  • No prior cytotoxic regimens are allowed for this malignancy. Patients may not have had prior chemotherapy or prior radiation therapy to the ipsilateral breast for this malignancy. Prior bis-phosphonate therapy is allowed
  • Age ≥18 years
  • ECOG performance status 0-1
  • Willing to undergo core biopsy of the primary breast lesion to assess baseline biomarkers
  • Non-pregnant and non-lactating
  • No ferromagnetic prostheses. Patients who have metallic surgical implants that are not compatible with an MRI machine are not eligible.
  • Ability to understand and willingness to sign a written informed consent (I-SPY TRIAL Screening Consent)
  • Eligible tumors must meet one of the following criteria: Stage II or III, or T4, any N, M0, including clinical or pathologic inflammatory cancer or Regional Stage IV, where supraclavicular lymph nodes are the only sites metastasis
  • Any tumor ER/PgR status, any HER-2/neu status as measured by local hospital pathology laboratory and meets any tumor assay profile described in protocol section 4.1.2F
  • Normal organ and marrow function: Leukocytes ≥ 3000/μL, Absolute neutrophil count ≥ 1500/μL, Platelets ≥ 100,000/μL, Total bilirubin within normal institutional limits, unless patient has Gilbert's disease, for which bilirubin must be ≤ 2.0 x ULN, AST(SGOT)/ALT (SGPT) ≤ 1.5 x institutional ULN, creatinine < 1.5 x institutional ULN
  • No uncontrolled or severe cardiac disease. Baseline ejection fraction (by nuclear imaging or echocardiography) must by ≥ 50%
  • No clinical or imaging evidence of distant metastases by PA and Lateral CXR, Radionuclide Bone scan, and LFTs including total bilirubin, ALT, AST, and alkaline phosphatase
  • Tumor assay profile must include on of the following: MammaPrint High, any ER status, any HER2 status, or MammaPrint Low, ER negative (<5%), any HER2 status, or MammaPrint Low, ER positive, HER2/neu positive by any one of the three methods used (IHC, FISH, TargetPrint™)
  • Ability to understand and willingness to sign a written informed consent document (I-SPY 2 TRIAL Consent #2)
Exclusion Criteria
  • Use of any other investigational agents within 30 days of starting study treatment
  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to the study agent or accompanying supportive medications.
  • Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, or psychiatric illness/social situations that would limit compliance with study requirements

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
CemiplimabCemiplimabNovel Investigational Agent. Arm is closed.
Cemiplimab plus REGN3767Cemiplimab plus REGN3767Novel Investigational Agent. Arm is closed.
Sarilumab + Cemiplimab + Paclitaxel in Block B followed by SOC Block CSarilumab + Cemiplimab + PaclitaxelNovel investigational Agent
TucatinibTucatinib plus trastuzumab and pertuzumabArm is closed.
Endocrine Optimization Pilot: ARV-471 + LetrozoleARV-471 + LetrozoleNovel investigational Agent
Endocrine Optimization Pilot: ARV-471 + AbemaciclibARV-471 + AbemaciclibNovel investigational Agent
Endocrine Optimization Pilot: (Z)-Endoxifen + AbemaciclibEndoxifen + AbemaciclibNovel investigational Agent
Standard TherapyStandard TherapyPaclitaxel, Herceptin followed by Doxorubicin and Cyclophosphamide treatment depending on HR/HER-2 status.
AMG 386 with or without TrastuzumabAMG 386 with or without TrastuzumabArm is closed.
AMG 386 with or without TrastuzumabAMG 386 and TrastuzumabArm is closed.
AMG 479 plus MetforminAMG 479 (Ganitumab) plus MetforminArm is closed.
MK-2206 with or without TrastuzumabMK-2206 with or without TrastuzumabArm is closed.
T-DM1 and PertuzumabT-DM1 and PertuzumabArm is closed.
Pertuzumab and TrastuzumabPertuzumab and TrastuzumabNovel Control Investigational Agent. Arm is closed.
GanetespibGanetespibArm is closed.
ABT-888ABT-888Arm is closed.
NeratinibNeratinibArm is closed.
PLX3397PLX3397Arm is closed.
Pembrolizumab 4 cyclePembrolizumab - 4 cycleArm is closed.
Talazoparib plus IrinotecanTalazoparib plus IrinotecanArm is closed.
Patritumab with or without TrastuzumabPatritumab and TrastuzumabArm is closed.
Pembrolizumab 8 cyclePembrolizumab - 8 cycleArm is closed.
Durvalumab plus OlaparibDurvalumab plus OlaparibArm is closed.
SD-101 + PembrolizumabSD-101 + PembrolizumabArm is closed.
Trilaciclib with or without trastuzumab + pertuzumabTrilaciclib with or without trastuzumab + pertuzumabNovel Investigational Agent. Arm is closed.
SYD985 ([vic-]trastuzumab duocarmazine)SYD985 ([vic-]trastuzumab duocarmazine)Novel Investigational Agent. Arm is closed.
Oral Paclitaxel + Encequidar + Dostarlimab (TSR-042) + Carboplatin with or without trastuzumabOral Paclitaxel + Encequidar + Dostarlimab (TSR-042) + Carboplatin with or without trastuzumabNovel Investigational Agent. Arm is closed.
DAN222 + Niraparib in Block A and followed by SOC in Block BDan222 + NiraparibNovel investigational Agent
Oral Paclitaxel + Encequidar + Dostarlimab (TSR-042) with or without trastuzumabOral Paclitaxel + Encequidar + Dostarlimab (TSR-042) with or without trastuzumabNovel Investigational Agent. Arm is closed.
Endocrine Optimization Pilot: Amcenestrant MonotherapyAmcenestrantNovel Investigational Agent. Arm is closed.
Endocrine Optimization Pilot: Amcenestrant + AbemaciclibAmcenestrant + AbemaciclibNovel Investigational Agent. Arm is closed.
Endocrine Optimization Pilot: Amcenestrant + LetrozoleAmcenestrant + LetrozoleNovel Investigational Agent. Arm is closed.
ARX788 in Block A and followed by SOC in Block BARX788Novel investigational Agent followed by SOC
ARX788 + Cemiplimab in Block A and followed by SOC in Block BARX788 + CemiplimabNovel investigational Agent followed by SOC. Arm is closed.
VSV-IFNβ-NIS (VOYAGER V1™; VV1) + Cemiplimab in Block A and followed by SOC in block BVV1 + CemiplimabNovel investigational Agent followed by SOC
Datopotamab Deruxtecan in Block A and followed by SOC in block BDatopotamab deruxtecanNovel investigational Agent followed by SOC
Datopotamab Deruxtecan + Durvalumab in Block A and followed by SOC in block BDatopotamab deruxtecan + DurvalumabNovel investigational Agent followed by SOC
Endocrine Optimization Pilot: LasofoxifeneLasofoxifeneNovel investigational Agent
Endocrine Optimization Pilot: (Z)-EndoxifenZ-endoxifenNovel investigational Agent
Endocrine Optimization Pilot: ARV-471ARV-471Novel investigational Agent
Rilvegostomig + TDXd in Block A and followed by SOC in Block BRilvegostomig + TDXdNovel investigational Agent
SGN-LIV1ASGN-LIV1AArm is closed.
Zanidatamab in Block A and followed by SOC in block BZanidatamabNovel investigational Agent followed by SOC
Primary Outcome Measures
NameTimeMethod
Determine whether adding experimental agents to standard neoadjuvant medications increases the probability of pathologic complete response (pCR) over standard neoadjuvant chemotherapy for each biomarker signature established at trial entry.Post surgery based on upto 36-week treatment
Secondary Outcome Measures
NameTimeMethod
Establishing predictive and prognostic indices based on qualification and exploratory markers to predict pCR and residual cancer burden (RCB).Blood and Tissue Collection: Baseline, Post-Randomization, Pre-AC, Pre- and Post-Surgery
To determine three- and five-year relapse-free survival (RFS) and OS among the treatment arms.Three- and Five-Year Post-surgery Follow-up
MRI VolumeFour time points during the on-study phase: Baseline, Post-randomization, Pre-AC treatment and Pre-Surgery
To determine incidence of adverse events (AEs), serious adverse events (SAEs), and laboratory abnormalities of each investigational agent tested.Post-Randomization, Pre-AC, Pre-Surgery, Post-Surgery upto One Year during follow-up

Trial Locations

Locations (36)

Rutgers Cancer Institute of New Jersey

🇺🇸

New Brunswick, New Jersey, United States

University of Texas, Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

University of Kansas

🇺🇸

Westwood, Kansas, United States

Herbert-Herman Cancer Center, Sparrow Hospital

🇺🇸

Lansing, Michigan, United States

Winship Cancer Institute of Emory University

🇺🇸

Atlanta, Georgia, United States

University of Chicago

🇺🇸

Chicago, Illinois, United States

University Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Sanford Clinical Research

🇺🇸

Sioux Falls, South Dakota, United States

University of Texas, M.D. Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Swedish Cancer Institute

🇺🇸

Seattle, Washington, United States

University of Washington

🇺🇸

Seattle, Washington, United States

University of California San Francisco (UCSF)

🇺🇸

San Francisco, California, United States

Vanderbilt University Medical Center

🇺🇸

Nashville, Tennessee, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Oregon Health & Science Institute (OHSU)

🇺🇸

Portland, Oregon, United States

University of Rochester Wilmot Cancer Institute

🇺🇸

Rochester, New York, United States

University of Colorado

🇺🇸

Aurora, Colorado, United States

University of Southern California

🇺🇸

Los Angeles, California, United States

City of Hope

🇺🇸

Duarte, California, United States

University of Arizona

🇺🇸

Tucson, Arizona, United States

Mayo Clinic - Scottsdale

🇺🇸

Scottsdale, Arizona, United States

University of California San Diego

🇺🇸

La Jolla, California, United States

HOAG Memorial Hospital Presbyterian

🇺🇸

Newport Beach, California, United States

Georgetown University Medical Center

🇺🇸

Washington, District of Columbia, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Loyola University

🇺🇸

Maywood, Illinois, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Wake Forest Baptist Comprehensive Cancer Center

🇺🇸

Winston-Salem, North Carolina, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Laura and Isaac Perlmutter Cancer Center / NYU Langone Health

🇺🇸

New York, New York, United States

University of Pennsylvania (U Penn)

🇺🇸

Philadelphia, Pennsylvania, United States

Inova Health System

🇺🇸

Falls Church, Virginia, United States

University of Minnesota

🇺🇸

Minneapolis, Minnesota, United States

Yale Cancer Center

🇺🇸

New Haven, Connecticut, United States

Montefiore Medical Center

🇺🇸

Bronx, New York, United States

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