The multicenter continuous clinical trial of the safety and efficacy of bezafibrate for mitochondrial fatty acid beta-oxidation disorders
Phase 2
- Conditions
- mitochondrial fatty acid beta-oxidation disorders
- Registration Number
- JPRN-UMIN000016951
- Lead Sponsor
- Shimane University Hospital
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up complete
- Sex
- All
- Target Recruitment
- 10
Inclusion Criteria
Not provided
Exclusion Criteria
Patient who; (1) is considered ineligible for enrolling the study by a principal investigator or sub-investigator
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Safety endpoint Existence and its contents of adverse events and side effects
- Secondary Outcome Measures
Name Time Method Efficacy endpoint frequency of occurrence of muscle cramp attacks every week