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Toxin Treatment for Amyotrophic Lateral Sclerosis (ALS) Related Sialorrhea

Phase 2
Completed
Conditions
Sialorrhea
Amyotrophic Lateral Sclerosis
Interventions
Drug: Placebo injection
Registration Number
NCT01551940
Lead Sponsor
Hospices Civils de Lyon
Brief Summary

Evaluation of the decrease of the secretion of saliva in patients with amyotrophic lateral sclerosis by a local ultrasound-guided bilateral injection of botulinum toxin type A in parotids and submandibular glands. The investigators want to demonstrate 1 month after the injection, by a multicenter French randomized double blind study, an improvement of at least 25 % of the functional embarrassment due to saliva, estimated with a visual analogue scale, a decrease of the quantity of saliva and a decrease of the embarrassment for the main caregiver.

Detailed Description

The patient will benefit from an ultrasound guided injection of botulinum toxin A (Botox®) or placebo (NaCl 0.9 %) and will be followed up in consultation at 4, 12, 16 (if reinjection) and 24 weeks. He will be contacted by telephone in 2 and in 8 weeks (percentage of decrease of functional embarrassment, percentage of decrease of salivary secretion rate). He can be able to benefit in the open label phase of a botulinum toxin type A injection at the 12-week follow up if he estimates that first injection was not effective or if the efficiency of the first injection began to become blurred. After the 6 months of the study, the patient will benefit again from the usual follow-up as advised by the French consensus conference in November, 2005.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
18
Inclusion Criteria
  • Age > 18 years
  • Obtaining of a written consent after information
  • Diagnosis of probable or certain ALS according to the El Escorial criteria of the World Federation and Neurology Committee on Neuromuscular Diseases
  • Patient having a follow-up in an ALS center
  • Sialorrhea with VAS functional embarrassment > or equal at 50/100.
  • Patient beneficiary of Social Security regime
Exclusion Criteria
  • Evolving disease associated with predictable survival < 1 month
  • Patient having previously received an injection of botulinum toxin in the salivary glands
  • Patient taking the other medical treatments for sialorrhea in the 7 days before the inclusion in the study (scopoderm, trihexyph'nidyle, atropine, ipatropium, amitriptyline, clomipramine, oxybutinine, diphenhydramine, beta-blockers)
  • Patient having benefited from radiotherapy or from surgery on the salivary glands
  • Behavioral problems, dementia or other psychiatric problems
  • Myasthenia
  • Known Pregnancy or absence of contraception recognized as effective, breast feeding

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
BotoxBotox injectionBotox injection : 100 UI of botulinum toxin type A (Botox®) diluted in 2.2 ml of NaCl 0.9 %
PlaceboPlacebo injectionPlacebo injection : NaCl 0.9 %
Primary Outcome Measures
NameTimeMethod
Improvement of the functional embarrassment provoked by sialorrhea1 month after the injection

Demonstrate after the injection of botulinum toxin type A an improvement of at least 25 % of the functional embarrassment provoked by sialorrhea in the ALS patient, evaluated with a horizontal visual analogue scale (VAS).

Secondary Outcome Measures
NameTimeMethod
Decrease of the salivary secretion rate and a decrease of the embarrassment for the main caregiver1 month after the injection

Demonstrate, one month after the injection of botulinum toxin type A, a decrease of the salivary secretion rate and a decrease of the embarrassment for the main caregiver by a horizontal visual analogue scale.

Improvement of the value of the hypersalivation item in ALSFRS-R scale1 month after the injection

Demonstrate, one month after the injection of botulinum toxin type A, an improvement of the value of the hypersalivation item in ALSFRS-R scale.

Modification of the speech evaluation1 month after the injection

Demonstrate, one month after the injection of botulinum toxin typeA, a modification of the speech evaluation (evaluation realized by speech evaluator)

Description of patient cohort after the first injection6 months after the injection

Describe cohort after the first injection: evolution of scores for every patient among Day0 and Month1, delay of appearance of the efficiency, the duration of effect of the treatment, the side effects, the modification of the consistency of the saliva and the possible necessity for re-injecting the patient at 3 months of follow-up.

Decrease of the score of severity and frequency of the drooling rating scale1 month after the injection

Demonstrate, one month after the injection of botulinum toxin type A, a decrease of the score of severity and frequency of the drooling rating scale

Decrease of the cotton roll weight1 month after the injection

Demonstrate, one month after the injection of botulinum toxin type A, a decrease of the cotton roll weight.

Cotton rolls weight: production and quantity of saliva are verified by placing dental cotton rolls during 3 minutes in the mouth of the patient and by comparing the weight of rolls dry and soaked with saliva.

Decrease of the number of paper handkerchiefs used1 month after the injection

Demonstrate, one month after the injection of botulinum toxin type A, a decrease of the number of paper handkerchiefs used. We ask the patient to count the number of handkerchiefs used a day.

Improvement of the quality of life1 month after the injection

Demonstrate, one month after the injection of botulinum toxin type A, an improvement of the quality of life. Scale to estimate quality of life (ALSAQ-40), usually used with the patients affected by ALS

Trial Locations

Locations (13)

Service de Neurologie, Hôpital Gabriel Montpied, CHU de Clermont-Ferrand

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Clermont-Ferrand cedex 1, France

Fédération des Maladies du Système Nerveux, Groupement Hospitalier Pitié Salpêtrière, AP-HP

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Paris cedex 13, France

Centre de Référence maladies Neuromusculaires, Service de Médecine Physique et Réadaptation, Hôpital de l'Archet 1, CHU de Nice

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Nice cedex 3, France

Service de Neurologie, CHU de Saint-Etienne

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Saint-Etienne cedex 2, France

Département de Neurologie, Hôpital de Hautepierre, CHRU de Strasbourg

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Strasbourg, France

Département de Neurologie, Hôpital de l'Hôtel-Dieu, CHU d'Angers

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Angers cedex 9, France

Service de Neurologie, Hôpital de la Timone, CHU de Marseille

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Marseille cedex 5, France

Service de Neurologie, Hôpital Central, CHU de Nancy

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Nancy, France

Centre SLA, Groupement Hospitalier Est, Hôpital Neurologique Pierre Wertheimer, Hospices Civils de Lyon

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Bron, France

Service de Neurologie, Hôpital Dupuytren, CHU de Limoges

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Limoges, France

Service d'Explorations Fonctionelles Neuro-Musculaires, Hôpital Rangueil, CHU de Toulouse

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Toulouse, France

Service de Neurologie Vastel, Hôpital Côte de Nacre, CHU de Caen

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Caen cedex 9, France

Centre SLA, Service de Neurologie A et pathologies du mouvement, Hôpital Roger Salengro, CHU de Lille

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Lille, France

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