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Immunomodulatory Effect of Vitamin D in Allogenic Post-transplant

Phase 1
Completed
Conditions
Hematopoietic Stem Cell Transplantation
Interventions
Drug: 1000IU/day of Vitamine D
Drug: 5000IU/day of Vitamine D
Registration Number
NCT02600988
Lead Sponsor
Fundación Pública Andaluza para la gestión de la Investigación en Sevilla
Brief Summary

The purpose of this study is to determine whether vitamin D is effective in the prevention of graft-versus-host-disease after completion of allogeneic transplant.

Detailed Description

The allogeneic transplant of haematopoietic cell is the only treatment option for many malignant blood diseases. Unfortunately, the progression free survival and the quality of life of transplanted patients is limited due to the development of graft-versus-host-disease (GVHD).

The development of new prophylaxis strategies of GVHD based in the use of immunomodulator agents (allowing the generation of an immunotolerance state and avoiding the use of immunosuppression) is essential.

The GVHD is due to the cytotoxic effect of the donor lymphocytes T against healthy organs and tissues of the receptor. Calcineurin inhibitor combined with methotrexate or antibodies anti-lymphocytes T are used as standard prophylaxis. This type of antibodies has demonstrated efficacy to reduce GVHD, but have not increased survival due to increasing the risk of relapses and serious post-transplant infections.

Due to its interactions with VDR (vitamin D receptor) present in immune system cells, vitamin D is able to inhibit the activation of dendritic cells and the proliferation and production of cytokines by lymphocytes T. Based on this effect, the peri- and post- transplant administration of vitamin D might decrease the risk of GVHD in allogeneic transplanted patients, subsequently decreasing the immunosuppressant treatment requirements and improving the prognosis of those patients.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
150
Inclusion Criteria
  • Age ≥ 18 years
  • The patient should accomplish all the criteria to proceed to an allogeneic transplant
  • The patient or their legal guardians should signed the informed consent approved by the Ethics Committees of Clinical Trials
Exclusion Criteria
  • Hypercalcemia ≥ 10.5 mg/dl
  • Renal insufficiency with creatinine level ≥ 2 x upper limit of normal (1,1 mg/dl)
  • Participation in others Clinical Trials in which the intervention may affect the result of the study.
  • Patients receiving GVHD immunoprophylaxis with thymoglobuline or GVHD prophylaxis including in vitro or in vivo lymphocytes T depletion (anti-lymphocyte T globulin, ALG)
  • Patients receiving a transplant from an haploidentical donor

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Group 2: 1000IU/day of Vitamine D1000IU/day of Vitamine DIt is composed by the following 50 patients joining the study. They will take 1000 IU of vitamin D once a day.
Group 3: 5000IU/day of Vitamine D5000IU/day of Vitamine DIt is composed by the last 50 patients joining the study. They will take 5000 IU of vitamin D once a day.
Primary Outcome Measures
NameTimeMethod
Incidence/severity of Graft-Versus-Host-DiseaseDay +150 post-transplant

Number of cases of GVHD/Seriousness graded according to National Institutes of Health Consensus Development Project on Criteria for Clinical Trials in Chronic Graft-versus-Host Disease

Secondary Outcome Measures
NameTimeMethod
Serum levels of Th1/Th2 cytokinesDay -5 pre-transplant and +1, +7, +21,+56 and +100 post-transplant

(IL-2, IL-4, IL-6, IL-10, tumor necrosis factor alfa (TNF)-α and interferon gamma (IFN-g)) are determined by flow cytometry using the BD Human Th1/Th2 Cytokine CBA

Dendritic cellsDay +21,+56 and +100 post-transplant

The following markers were used to identify different subpopulations

CD16-PB, CD45-V500, HLADR-FITC, BDCA-PE, CD11c-PerCP-Cy5.5, CD86-PE-Cy7, CD123-APC and CD14-APC-H7.

Plasmacytoid dendritic cells: HLADR+ CD123++ CD11c- CD16- CD14- BDCA1- CD45+.

Monocyte-derived dendritic cells: HLADR+ CD123+d CD11c+ CD16++ CD14-/+d BDCA- CD45+.

Myeloid BDCA1 dendritic cells : HLADR+ CD123- CD11c+ CD16- CD14- BDCA+ CD45+

Subpopulations of lymphocytesDay +21,+56 and +100 post-transplant

To be identified using the combination CD19+CD8-FITC, CD3+CD56-PE, CD4- PerCP-Cy5.5, HLADR-APC T cells: CD3+ (CD3+CD4+CD8-, CD3+CD4-CD8+, CD3+CD4+CD8+, CD3+CD4-CD8+)

B cells: CD19+ HLADR+

NK cells: CD3- CD19- CD56+

CD45RA-FITC and CCR7-PE were used to distinguish the repertory of naive/effector/memory of CD4 and CD8 cells.

-naive T cells: CD45RA+CCR7+

-effector T cells: CD45RA+CCR7-

-central memory T cells: CD45RA-CCR7+

-Peripheral memory T cells: CD45RA-CCR7-

Regulatory T cellsDay +21,+56 and +100 post-transplant

after incubation of surface antigens (CD25-FITC, CD127-PE and CD4-PerCP-Cy5.5), cells were washed in PBS and then fixed and permeabilized with FoxP3 Staining Buffer Set (eBiosciences) for FOXP3 staining.

phenotype of Treg: CD4+CD25+CD127-/+wFoxP3+

NK markersDay +21,+56 and +100 post-transplant

using the following combinations:

CD94-FITC/CD56-PE/CD3-PerCP-Cy5.5/HLADR-APC

CD11a-FITC/CD16-PE/CD3-PerCP-Cy5.5/CD56-APC

CD158a-FITC/CD161-PE/CD3-PerCP-Cy5.5/CD56-APC

CDNKB1-FITC/NKAT-PE/CD3-PerCP-Cy5.5/CD56-APC

We identify NK cells with weak expression of CD56 (CD56 called " weak) and those expressing more intensely this marker CD56 "bright ". In addition the expression of different KIR receptor as CD158a , CD161 , and NKAT2 NKB1 were reported.

Activation of T cellsDay +21,+56 and +100 post-transplant

Activation assays are performed on 500 µl of peripheral blood added in 48-well plates. Peripheral blood is stimulated or not with PMA (20µg/2ml) and ionomycin (0.91 µg/ml).

Peak Plasma Concentration (Cmax) of Vitamin DDay -5 pre-transplant and +1, +7 and +21 post-transplant

Peak Plasma Concentration (Cmax)

Area under the plasma concentration of Vitamin DDay -5 pre-transplant and +1, +7 and +21 post-transplant

Area under the plasma concentration versus time curve (AUC)

Bone densitometry changes carried out by protocol in post-transplant periodDay +150 post-transplant

Treatment effect in the subsequent development of osteoporosis

Trial Locations

Locations (7)

Raquel Saldaña Moreno

🇪🇸

Jerez de la Frontera, Cádiz, Spain

David Valcárcel Ferreiras

🇪🇸

Barcelona, Spain

Christelle Ferrà i Coll

🇪🇸

Badalona, Barcelona, Spain

Manuel Jurado Chacón

🇪🇸

Granada, Spain

Carmen Martínez

🇪🇸

Barcelona, Spain

Mª Ángeles Cuesta

🇪🇸

Málaga, Spain

Fermín Martín Sánchez- Guijo

🇪🇸

Salamanca, Spain

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