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A pilot phase I study of azacitidine for the first relapsed patients with infant acute lymphoblastic leukemia and MLL gene rearrangement

Phase 1
Conditions
Children with first relapsed infant MLL gene rearrangement positive acute lymphoblastic leukemia
Registration Number
JPRN-UMIN000029275
Lead Sponsor
ational Center for Child Health and Development
Brief Summary

Primary endpoint of this trial was incidence of dose limiting toxicity (DLT) of the investigational drug azacytidine. No DLT was observed in DL1 for the registered patient. However, at least three patients are required to evaluate the incidence of DLT in DL1; therefore, DLT of azacitidine could not be evaluated in this study.

Detailed Description

Not available

Recruitment & Eligibility

Status
Complete: follow-up complete
Sex
All
Target Recruitment
1
Inclusion Criteria

Not provided

Exclusion Criteria

Patients should be excluded if either of the below criteria is met: (1) Patients with uncontrollable infections. (2) Patients with congenital heart disease which require any interventions. (3) Patients with somatic chromosomal abnormalities. (4) Patients with active hemorrhage at study entry. (5) Patients with CNS symptoms at study entry. (6) Patients with other malignant diseases. (7) Patients with isolated extramedullary relapse. (8) Patients with CNS relapse. (9) Patients not eligible for the study entry decided by the primary/co-investigators of the study.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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