MedPath

Aprepitant Versus Hydroxyzine in Persistent Aquagenic Pruritus for Patients With Myeloproliferative Neoplasms

Phase 3
Conditions
Myeloproliferative Disorder
Aquagenic Pruritus
Interventions
Registration Number
NCT03808805
Lead Sponsor
University Hospital, Brest
Brief Summary

Phase 3, randomized prospective study, double blind-double placebo, testing oral therapies APREPITANT versus HYDROXYZINE in patients followed for myeloproliferative neoplasms and suffering of persistent aquagenic pruritus.

Detailed Description

Identification of patients with myeloproliferative neoplasms and aquagenic pruritus. Evaluation of the intensity of the aquagenic pruritus. Patients with value \>5/10 on the VAS (Visual Analogue Scale ) are proposed to participate to the protocole. Randomization between the two treatments. Duration of the treatment : 14 days. Regular evaluation of efficacity of the drugs (questionnaires). Evaluations will stop 2 months after the last intake. Blood samples will be collected before and after the intakes to study cytokine and neuropeptide levels.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
80
Inclusion Criteria
  • Major patients with myeloproliferative neoplasms (polycythemia vera, essential thrombocythaemia or myelofibrosis)
  • and treated with hydroxyurea, pipobroman, anagrelide, α2a pegylated interferon, ruxolitinib or bled for more than 6 months
  • and suffering of persistent aquagenic pruritus
  • and with a pruritus intensity on Analogic Visual Scale >5/10
  • patients who gave their written consent for participation in the study
Exclusion Criteria
  • patients with a physical or psychological disability to sign the consent form
  • patients with myeloproliferative neoplasms and suffering of aquagenic pruritus but only treated by aspirin
  • patients already included in another therapeutic protocol
  • patients with diffuse dermatological disease where pruritus may be present (psoriasis, atopic dermatitis, prurigo
  • patients already on anti-anxiety and / or anti-depressant treatment
  • patients with absolute contraindications to the use of Aprepitant or Hydroxyzine
  • hypersensitivity to Aprepitant and / or Hydroxyzine or to any of their excipients
  • lactose intolerance
  • pregnant or lactating women

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
studied groupPlacebo of HydroxyzineAprepitant 80 mg daily - 14 days Plus placebo of Hydroxyzine - 14 days
comparative groupHydroxyzine 25mgHydroxyzine 25 mg/d - 14 days Plus placebo of Aprepitant - 14 days
comparative groupPlacebo of AprepitantHydroxyzine 25 mg/d - 14 days Plus placebo of Aprepitant - 14 days
studied groupAprepitant 80 mgAprepitant 80 mg daily - 14 days Plus placebo of Hydroxyzine - 14 days
Primary Outcome Measures
NameTimeMethod
Reduction of pruritus intensity below (or equal) 3/10 on the VAS (Visual Analogue Scale )at 15 days

number of patients with a pruritus intensity below (or equal) 3/10 on the VAS (Visual Analogue Scale wich measure the intensity of symptoms of pruritus, 0 is minimum and 10 is maximum intensity of symptoms)

Secondary Outcome Measures
NameTimeMethod
Time observed to decreased the VAS to 3/1001 to 60 days

number of days to obtain an intensity of pruritus at 3/10 on the VAS (Visual Analogue Scale )

Reduction of pruritus intensity below (or equal) 3/10 on the VAS (Visual Analogue Scale )at 60 days

number of patients with a pruritus intensity below (or equal) 3/10 on the VAS (Visual Analogue Scale wich measure the intensity of symptoms of pruritus, 0 is minimum and 10 is maximum intensity of symptoms)

Cessation of pruritusat 60 days

number of patients with a pruritus intensity at 0/10 on the VAS (Visual Analogue Scale wich measure the intensity of symptoms of pruritus, 0 is minimum and 10 is maximum intensity of symptoms))

Duration of treatment effectiveness1 to 60 days

number of days the VAS (Visual Analogue Scale ) is below (or equal) 3/10

Quality of life through the use of validated questionnaire : the PASYMPLE questionnaireat 60 days

Evaluation of quality of life by completion of the PASYMPLE (evaluation of pruritus with 7 questions about occurence, timing, intensity and localisation of pruritus) questionnaire

Quality of life through the use of validated questionnaires : the MPN-SAF (Myeloproliferative Neoplasm Symptom Assessment Form) questionnaireat 30 days

Evaluation of quality of life by completion of the MPN-SAF (Myeloproliferative Neoplasm Symptom Assessment Form calculated as the mean score for 10 items. Questions focus on fatigue, concentration, early satiety, inactivity, night sweats, itching, bone pain, abdominal discomfort, weight loss, and fevers) questionnaire

Adverse event occurring during the association therapeuticat 15 days

type of adverse event occuring during the treatment period

Complete blood count (normal or abnormal)1 to 60 days

number of patients with hematologic remission : hematocrit \<45% with leukocytes \<10 giga/l and platelets \<400 giga/l

Number of prematurely discontinued anti-pruritic treatmentat 15 days

Total number of prematurely discontinued treatments for all subjects

Quality of life through the use of validated questionnaire : the MPN-SAF (Myeloproliferative Neoplasm Symptom Assessment Form) questionnaireat 60 days

Evaluation of quality of life by completion of the MPN-SAF (Myeloproliferative Neoplasm Symptom Assessment Form calculated as the mean score for 10 items. Questions focus on fatigue, concentration, early satiety, inactivity, night sweats, itching, bone pain, abdominal discomfort, weight loss, and fevers) questionnaire

Quantification of the change of plasma concentrations of cytokines and neuropeptidesat 60 days

Plasma concentrations of cytokines (ng/L) and neuropeptides (ng/mL)

Trial Locations

Locations (11)

CHU d'Angers

🇫🇷

Angers, France

Centre Hospitalier des Pays de Morlaix

🇫🇷

Morlaix, France

Hôpital Yves Le Foll

🇫🇷

Saint-Brieuc, France

Hôpital Pontchaillou

🇫🇷

Rennes, France

Centre Léon Bérard

🇫🇷

Lyon, France

CHU de Caen

🇫🇷

Caen, France

Centre Hospitalier de Douarnenez

🇫🇷

Douarnenez, France

CHU Grenoble Alpes

🇫🇷

Grenoble, France

CHU de Nantes

🇫🇷

Nantes, France

Centre Hospitalier de Cornouaille

🇫🇷

Quimper, France

CHRU de Brest - Hôpital Morvan

🇫🇷

Brest, Brest Cedex, France

© Copyright 2025. All Rights Reserved by MedPath