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A Prospective Study of UCAD for Diagnosing Benign or Malignant Biliary Obstruction and Follow-up

Conditions
Pancreatic Head Carcinoma
Pancreatic Carcinoma
Gallbladder Cancer
Biliary Tract Neoplasms
Interventions
Diagnostic Test: The level of CIN
Registration Number
NCT05237193
Lead Sponsor
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
Brief Summary

Chromosomal instability (CIN) refers to ongoing chromosome segregation errors throughout consecutive cell divisions. CIN is a hallmark of human cancer, and it is associated with poor prognosis, metastasis, and therapeutic resistance. Analyzing CIN of the DNA extracted from bile tract exfoliated cells in bile samples seems a promising method for diagnosing, monitoring, and predicting the prognosis of patients with malignant biliary obstruction, including biliary tract cancer (BTC), pancreatic head carcinoma. CIN can be assessed using experimental techniques such as bulk DNA sequencing, fluorescence in situ hybridization (FISH), or conventional karyotyping. However, these techniques are either time-consuming or non-specific. The investigators here intend to study whether a new method named Ultrasensitive Chromosomal Aneuploidy Detection (UCAD), which is based on low-coverage whole-genome sequencing, can be used to analyze CIN thus helping diagnose malignant biliary obstruction and assessing follow-up.

Detailed Description

CIN results from errors in chromosome segregation during mitosis, leading to structural and numerical chromosomal abnormalities. It will generate genomic heterogeneity that acts as a substrate for natural selection. Furthermore, it is proved that tumors with aneuploidies and polyploidy resulting from whole-genome doubling are related to metastasis, treatment resistance, and decreased overall survival. It is estimated that 60%-80% of human tumors exhibit chromosomal abnormalities suggestive of CIN. CIN positively correlates with tumor stage and is enriched in relapsed as well as metastatic tumor specimens. Due to the ubiquity of CIN in cancer cells, it is a potentially non-invasive way to detect CIN in the bile tract exfoliated cells in bile samples for diagnosing and monitoring malignant biliary obstruction patients. UCAD is a new method to detect CIN in the DNA sample from patients, including extracting DNA from bile, analyzing DNA by low-coverage whole-genome sequencing, processing the data by bio-information techniques, and finally optimizing the management of malignant biliary obstruction patients. The investigators intended to conduct a prospective, single-blinded study by analyzing bile samples from malignant biliary obstruction patients and control groups without any tumor in the biliary system or other organs to compare the specificity and sensitivity of the UCAD test for diagnosing malignant biliary obstruction to other modalities, such as bile cytology. The investigators also intend to investigate the potential of UCAD in malignant biliary obstruction patient follow-up by analyzing the CIN level and following malignant biliary obstruction patients for up to 2 years to determine if there is a correlation between CIN level and patient prognosis

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
400
Inclusion Criteria
  • Patients diagnosed with malignant biliary obstruction and planned to undergo ERCP(endoscopic retrograde cholangiopancreatography), PTCS(percutaneous transhepatic cholangioscopy) or surgery.
  • Malignant biliary obstruction patients confirmed by operation or biopsy.
  • Participants without any tumor disease and willing to attend the study.
  • Male or female patients aged >= 18 years.
  • Participants signed informed consent form.
Exclusion Criteria
  • Patients diagnosed with malignant biliary obstruction and planned to undergo ERCP, PTCS or surgery.
  • Malignant biliary obstruction patients confirmed by operation or biopsy.
  • Participants without any tumor disease and willing to attend the study.
  • Male or female patients aged >= 18 years.
  • Participants signed informed consent form.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Benign biliary obstructionThe level of CINPatients being treated for other biliary diseases but without any tumor will provide a negative control to provide data for determining the sensitivity and specificity of UCAD analysis.
malignant biliary obstructionThe level of CINPre-surgery patients with malignant biliary obstruction will be the experimental group to determine the sensitivity and specificity of UCAD analysis, the result will be compared with cytology.
Primary Outcome Measures
NameTimeMethod
Sensitivity and Specificity of UCAD analysisthrough study completion, an average of 30 months

number of patients "declared positive" with the UCAD test among the patients who suffered from malignant biliary obstruction and number of patients "declared negative" with the UCAD test among the patients without cancer

Assess the value of UCAD for malignant biliary obstruction patient follow-upthrough study completion, an average of 30 months

Compare the CIN level with the patient information gathered by follow-up to determine whether there is a correlation between CIN level and patient prognosis , like PFS(progression-free survival), five-year survival rate.

Secondary Outcome Measures
NameTimeMethod
Comparison of the sensitivity and specificity of the UCAD analysis versus bile cytologythrough study completion, an average of 30 months

number of patients "declared positive" with the UCAD analysis versus patients "declared positive" with the bile cytology and number of patients "declared negative" with the UCAD analysis versus patients " declared negative " with the bile cytology

Identification of the correlation between the level of CIN and the grade of the tumor samplethrough study completion, an average of 30 months

level of CIN in the bile sample compared with the grade of the tumor confirmed by histopathologic examination, like Grade 1-4.

Identification of the correlation between the level of CIN and the stage of the tumor samplethrough study completion, an average of 30 months

level of CIN in the bile sample compared with the TNM stage of the tumor confirmed by histopathologic examination, like Stage 0-IV.

Trial Locations

Locations (1)

Xinhua Hospital

🇨🇳

Shanghai, Shanghai, China

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