MedPath

Efficacy and Safety of 24 Weeks of Oral Treatment With BIIL 284 BS in Adult and Pediatric Patients

Phase 2
Terminated
Conditions
Cystic Fibrosis
Registration Number
NCT00060801
Lead Sponsor
Boehringer Ingelheim
Brief Summary

The purpose of this study is to determine the effect of 24 weeks of treatment with BIIL 284 BS compared with placebo on pulmonary function and incidence of pulmonary exacerbation in adult and pediatric cystic fibrosis patients.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
420
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Change from baseline in post-bronchodilator forced expiratory volume in one second (FEV1) (percent predicted)28 weeks
Proportion of patients with at least one pulmonary exacerbation during the treatment period as per definition of Fuchs et al28 weeks
Secondary Outcome Measures
NameTimeMethod
Time to first pulmonary exacerbation28 weeks
Proportion of patients with at least one pulmonary exacerbation during the treatment period as described in Rosenfeld et al.28 weeks
Change from baseline in post-bronchodilator forced vital capacity (FVC) percent predicted28 weeks
Change from baseline in post-bronchodilator mean forced expiratory flow during the middle half of the FVC (FEF25-75% ) percent predicted28 weeks
Change from baseline in post-bronchodilator inspiratory capacity (IC)28 weeks
Change from baseline in pre-bronchodilator FEV1% predictedweek 12, 24 and 28
Change from baseline in pre-bronchodilator FVC % predictedweek 12, 24 and 28
Change from baseline in pre-bronchodilator FEF25-75% % predictedweek 12, 24 and 28
Change from baseline in pre-bronchodilator MEF50% % predictedweek 12, 24 and 28
Change from baseline in pre-bronchodilator MEF25%% predictedweek 12, 24 and 28
Number of pulmonary exacerbations during the treatment period28 weeks
Proportion of patients with at least 1 hospitalisation for a pulmonary exacerbation during the treatment period28 weeks
Time to first hospitalisation for a pulmonary exacerbation28 weeks
Number of hospitalisations for a pulmonary exacerbation28 weeks
Number of days in hospital for a pulmonary exacerbation28 weeks
Proportion of patients with at least one pulmonary exacerbation requiring i.v. antibiotics during the treatment period28 weeks
Time to first course of i.v. antibiotics for a pulmonary exacerbation28 weeks
Number of pulmonary exacerbations requiring i.v. antibiotics during the treatment period28 weeks
Number of days of i.v. antibiotic use for pulmonary exacerbations during the treatment period28 weeks
Change from baseline in weight28 weeks
Change from baseline in height (in pediatrics)28 weeks
Change from baseline in weight for age percentiles28 weeks
Change from baseline in weight for age percentiles (in pediatrics)28 weeks
Change from baseline in weight expressed as % ideal body weight (IBW)28 weeks
Change from baseline in body mass index28 weeks
Change from baseline in BMI for age percentiles28 weeks
Change from baseline in blood levels of cytokines, chemokines and other inflammatory mediators28 weeks
Change in patient's health status as reported by patient28 weeks
Change in patient's health status as reported by physician28 weeks
Change from baseline in post-bronchodilator maximal expiratory flow when 50% of FVC remains in lung (MEF50% )percent predicted28 weeks
Change from baseline in post-bronchodilator maximal expiratory flow when 25% of FVC remains in lung (MEF25%) percent predicted28 weeks
Change from baseline in post-bronchodilator slow vital capacity (SVC)28 weeks

Trial Locations

Locations (35)

St. Christopher's Hospital for Children

🇺🇸

Philadelphia, Pennsylvania, United States

Washington University-St. Louis Children's Hospital

🇺🇸

St. Louis, Missouri, United States

Children's Hospital Medical Center of Akron

🇺🇸

Akron, Ohio, United States

Children's Hospital of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

University of Arizona

🇺🇸

Tucson, Arizona, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

University of Kentucky

🇺🇸

Lexington, Kentucky, United States

Tulane University

🇺🇸

New Orleans, Louisiana, United States

Children's Memorial Hospital

🇺🇸

Chicago, Illinois, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Children's Hospital of Los Angeles

🇺🇸

Los Angeles, California, United States

Stanford University Medical Center

🇺🇸

Palo Alto, California, United States

The Nemours Children's Clinic

🇺🇸

Orlando, Florida, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Pediatric Pulmonary Associates, PA

🇺🇸

St. Petersburg, Florida, United States

Albany Medical College

🇺🇸

Albany, New York, United States

Children's Memorial Center of Dallas

🇺🇸

Dallas, Texas, United States

University of North Carolina

🇺🇸

Chapel Hill, North Carolina, United States

MCP Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Columbus Children's Hospital

🇺🇸

Columbus, Ohio, United States

University of Wisconsin Hospitals & Clinics

🇺🇸

Madison, Wisconsin, United States

Children's Hospital & Health Center

🇺🇸

San Diego, California, United States

Riley Hospital

🇺🇸

Indianapolis, Indiana, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Children's Hospital

🇺🇸

Boston, Massachusetts, United States

University of Minnesota

🇺🇸

Minneapolis, Minnesota, United States

Texas Children's Hospital

🇺🇸

Houston, Texas, United States

Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

University of California at San Francisco

🇺🇸

San Francisco, California, United States

University of Nebraska

🇺🇸

Omaha, Nebraska, United States

University of Colorado

🇺🇸

Denver, Colorado, United States

University of Michigan Health System

🇺🇸

Ann Arbor, Michigan, United States

Vanderbilt Children's Hospital

🇺🇸

Nashville, Tennessee, United States

Rainbow Babies & Children's Hospital

🇺🇸

Cleveland, Ohio, United States

© Copyright 2025. All Rights Reserved by MedPath