MedPath

A Research Study to Treat Patients With Advanced Hepatocellular Carcinoma

Phase 2
Completed
Conditions
Carcinoma, Hepatocellular
Interventions
Registration Number
NCT00108953
Lead Sponsor
Bayer
Brief Summary

The purpose of this study is to evaluate the safety and efficacy of doxorubicin plus sorafenib versus doxorubicin plus placebo in patients with advanced hepatocellular carcinoma (HCC).

Detailed Description

In addition to the key secondary outcome parameters the following parameters will be assessed in an exploratory manner: relative time to progression (TTP), time to symptomatic progression (TTSP), response rate (RR) and overall survival between the 2 study populations.

The possible and potential predictive assays of clinical benefit through an assessment of the correlation between the defined baseline characteristics and key clinical endpoints.

The safety and tolerability will be assessed in the adverse event section. Doxorubicin pharmacokinetics in HCC patients treated with sorafenib versus placebo will be compared and the pharmacokinetic data will be correlated with doxorubicin-related adverse events (i.e., cardiotoxicity).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
96
Inclusion Criteria
  • Patients who have a life expectancy of at least 12 weeks

  • Patients with advanced HCC (unresectable, and/or metastatic) which has been histologically or cytologically documented

  • Patients must have at least one tumor lesion that meets both of the following criteria:

    • can be accurately measured in at least one dimension according to Response Evaluation Criteria in Solid Tumors (RECIST)
    • has not been previously treated with local therapy
  • Patients who have received local therapy except chemoembolization, such as surgery, radiation therapy, hepatic arterial embolization, radiofrequency ablation, percutaneous ethanol injection or cryoablation are eligible, provided that they either have a target lesion which has not been subjected to local therapy and/or the target lesion(s) within the field of the local therapy has shown an increase of 25% in the size. Local therapy must be completed at least 4 weeks prior to the baseline scan

  • Patients who have an Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2

Exclusion Criteria
  • Previous or concurrent cancer that is distinct in primary site or histology from HCC, EXCEPT cervical carcinoma in situ, treated basal cell carcinoma, and superficial bladder tumors (Ta, Tis & T1). Any cancer curatively treated > 3 years prior to entry is permitted
  • History of cardiac disease
  • Serious myocardial dysfunction
  • Active, clinically serious infections
  • Known history of Human Immunodeficiency Virus (HIV) infection
  • Known Central Nervous System (CNS) tumors including metastatic brain disease
  • Patients with clinically significant gastrointestinal bleeding within 30 days prior to study entry

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Sorafenib + DoxorubicinSorafenib (Nexavar, BAY43-9006) plus Doxorubicin"Sorafenib + Doxorubicin" -- combination therapy: Sorafenib (Nexavar, BAY43-9006) 200 mg tablets by mouth (orally) twice daily + doxorubicin 60 mg/m2 intravenous infusion every 21 days for 6 cycles (18 weeks)
Placebo + DoxorubicinDoxorubicin/Placebo"Placebo + Doxorubicin" -- monotherapy: Sorafenib (Nexavar, BAY43-9006) matching placebo tablets by mouth (orally) twice daily + doxorubicin 60 mg/m2 intravenous infusion every 21 days for 6 cycles (18 weeks)
Primary Outcome Measures
NameTimeMethod
Time to Progression (TTP)from date of randomization of the first patient until 3 years later

TTP was defined as the time from randomization to radiological disease progression by independent assessment.

Secondary Outcome Measures
NameTimeMethod
Percentage of Participants in Each Category of Best Tumor Responseachieved during treatment or within 30 days after termination of active therapy

Percentage of participants with complete or partial response (CR or PR) confirmed according to Response Evaluation Criteria in Solid Tumors (RECIST) and achieved during treatment or 30 days after end of treatment. CR: disappearance of all clinical and radiological tumor lesions. PR: at least 30% decrease in sum of the longest diameters of tumor lesions. Stable disease (SD): neither sufficient shrinkage to qualify for PR nor sufficient increase for progressive disease.

Time to Symptomatic Progression (TTSP)from date of randomization of the first patient until 3 years later

Time from date of randomization to date of first documented symptomatic progression defined by Functional Assessment of Cancer Therapy Hepatobiliary Symptom Index-8 (FHSI-8) assessment

Duration of Responsefrom date of randomization of the first patient until 3 years later

Time from date of first objective response (complete response \[CR\] or partial response \[PR\]) to date progression is first documented (as defined per independent central radiological assessment) or death, whichever occurs first

Time to Response (TTR)from date of randomization until 3 years later at end of study

Time from date of randomization to date of first objective response (complete response \[CR\] or partial response \[PR\]) is documented and confirmed according to RECIST criteria

Percentage of Participants for Whom Disease Control Was Achievedfrom date of randomization to end of treatment plus 30 days

Participants with disease control: those who have as best response complete response (CR), partial response (PR) or stable disease (SD: neither sufficient shrinkage to qualify for PR nor sufficient increase for progressive disease) according to Response Evaluation Criteria in Solid Tumors (RECIST)

Overall Survivalfrom date of randomization of the first patient until 3 years later

The time from date of randomization to date of death

Progression Free Survival (PFS)from date of randomization of the first patient until 3 years later

Time from the date of randomization to the date of the first documented radiological progression (as defined per independent central radiological assessment) or death, whichever occurs first

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