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An Investigational Immuno-therapy Study Of Nivolumab In Combination With Trametinib With Or Without Ipilimumab In Participants With Previously Treated Cancer of the Colon or Rectum That Has Spread

Phase 1
Completed
Conditions
Colorectal Cancer
Colorectal Neoplasm
Colorectal Tumors
Colorectal Carcinoma
Interventions
Registration Number
NCT03377361
Lead Sponsor
Bristol-Myers Squibb
Brief Summary

The purpose of this study is to investigate treatment with nivolumab in combination with trametinib with or without ipilimumab in participants with previously treated cancer of the colon or rectum that has spread.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
325
Inclusion Criteria
  • Histologically or cytologically confirmed previously treated metastatic colorectal cancer with adenocarcinoma histology and in Stage IV per American Joint Committee on Cancer (version 4.0) at study entry
  • Microsatellite status should be performed per local standard of practice, immunohistochemistry (IHC) and/or PCR. If IHC results are equivocal, PCR is required for determining microsatellite stable (MSS) status
  • Must have measurable disease per RECIST 1.1. Participants with lesions in a previously irradiated field as the sole site of measurable disease will be permitted to enroll provided the lesion(s) have demonstrated clear progression and can be measured accurately
  • Eastern Cooperative Oncology Group (ECOG) Performance Status of 0-1 at screening and on cycle 1 day 1 (C1D1)
Exclusion Criteria
  • BRAF V600 mutant colorectal cancer
  • Active brain metastases or leptomeningeal metastases
  • Active, known or suspected autoimmune disease
  • Participants with a condition requiring systemic treatment with either corticosteroids (> 10 mg daily prednisone equivalents) or other immunosuppressive medications within 14 days of study treatment administration
  • History of interstitial lung disease or pneumonitis
  • Prior treatment with immune checkpoint inhibitors and mitogen-activated protein kinase enzymes (MEK) inhibitors
  • History of allergy or hypersensitivity to study drug components

Other protocol defined inclusion/exclusion criteria apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Part 1 Cohort 1 3rd Line (3L): nivolumab + trametinibNivolumab-
Part 1A Cohort 2 2nd Line (2L): nivolumab + ipilimumab + trametinibNivolumab-
Part 1A Cohort 2 2nd Line (2L): nivolumab + ipilimumab + trametinibIpilimumab-
Part 1 Cohort 1 3rd Line (3L): nivolumab + trametinibTrametinib-
Part 1A Cohort 2 2nd Line (2L): nivolumab + ipilimumab + trametinibTrametinib-
Part 1A Cohort 3 (2L): nivolumab + ipilimumab + trametinibTrametinib-
Part 2 Cohort 4 (3L): nivolumab + ipilimumab + trametinibTrametinib-
Part 2 Cohort 5 (3L): RegorafenibRegorafenib-
Part 1B Cohort 6 (2L): nivolumab + ipilimumab + trametinibTrametinib-
Part 2 Cohort 4 (3L): nivolumab + ipilimumab + trametinibNivolumab-
Part 2 Cohort 4 (3L): nivolumab + ipilimumab + trametinibIpilimumab-
Part 1B Cohort 6 (2L): nivolumab + ipilimumab + trametinibNivolumab-
Part 1B Cohort 6 (2L): nivolumab + ipilimumab + trametinibIpilimumab-
Part 1A Cohort 3 (2L): nivolumab + ipilimumab + trametinibNivolumab-
Part 1A Cohort 3 (2L): nivolumab + ipilimumab + trametinibIpilimumab-
Primary Outcome Measures
NameTimeMethod
Incidence of DeathsUp to 100 months
Incidence of Serious Adverse Events (SAEs)Approximately 100 months
Incidence of Adverse Events (AEs)Approximately 100 months
Incidence of clinically significant changes in clinical laboratory results: Hematology testsUp to 77 months
Incidence of clinically significant changes in clinical laboratory results: Urinalysis testsUp to 77 months
Objective response rate (ORR) by investigator (Part 1B and Part 2)Approximately 24 months
Incidence of dose limiting toxicity (DLTs)Up to 23 months
Incidence of clinically significant changes in clinical laboratory results: Clinical Chemistry testsUp to 77 months
Secondary Outcome Measures
NameTimeMethod
Disease control rate (DCR)Approximately 24 months
Time to response (TTR)Approximately 24 months
Incidence of Adverse Events (AEs)Approximately 100 months
Incidence of Serious Adverse Events (SAEs)Approximately 100 months
Objective response rate (ORR) (Part 1A and Part 1)Approximately 24 months
Incidence of clinically significant changes in clinical laboratory results: Hematology testsUp to 77 months
Duration of response (DOR)Approximately 24 months
Progression-free survival (PFS) by investigator per response evaluation criteria in solid tumors (RECIST) v1.1Approximately 24 months
Best overall response (BOR)Up to 24 months
Overall survival (OS)Approximately 40 months
Incidence of DeathsUp to 100 months
Incidence of clinically significant changes in clinical laboratory results: Clinical Chemistry testsUp to 77 months
Incidence of clinically significant changes in clinical laboratory results: Urinalysis testsUp to 77 months

Trial Locations

Locations (47)

Local Institution - 0111

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Miami, Florida, United States

Local Institution - 0118

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Santiago, Región Metropolitana De Santiago, Chile

Local Institution - 0002

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Madison, Wisconsin, United States

Local Institution - 0003

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Philadelphia, Pennsylvania, United States

Local Institution - 0107

🇺🇸

Gainesville, Florida, United States

Local Institution - 0001

🇺🇸

San Francisco, California, United States

Local Institution - 0027

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Los Angeles, California, United States

Local Institution - 0022

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Birmingham, Alabama, United States

Local Institution - 0067

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Los Angeles, California, United States

Local Institution - 0028

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Baltimore, Maryland, United States

Local Institution - 0116

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Hattiesburg, Mississippi, United States

Local Institution - 0103

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Saint Louis, Missouri, United States

Local Institution - 0104

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New York, New York, United States

Local Institution - 0029

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Charlotte, North Carolina, United States

Local Institution - 0100

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Lancaster, Pennsylvania, United States

Thomas Jefferson University - Clinical Research Institute

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Philadelphia, Pennsylvania, United States

Local Institution - 0101

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Temple, Texas, United States

Local Institution - 0120

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Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

Local Institution - 0123

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Ciudad Autónoma de Buenos Aires, Distrito Federal, Argentina

Local Institution - 0044

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Blacktown, New South Wales, Australia

Local Institution - 0055

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Clayton, Victoria, Australia

Local Institution - 0043

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Southport, Queensland, Australia

Local Institution - 0068

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Elizabeth Vale, South Australia, Australia

Local Institution - 0069

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Heidelberg, Victoria, Australia

Local Institution - 0113

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Edmonton, Alberta, Canada

Local Institution

🇧🇪

Woluwe-Saint-Lambert, Belgium

Local Institution - 0070

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Toronto, Ontario, Canada

Local Institution - 0077

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Montréal, Quebec, Canada

Local Institution - 0076

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Ottawa, Canada

Local Institution - 0117

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Santiago, Metropolitana, Chile

Local Institution - 0073

🇨🇿

Hradec Kralove, Czechia

Local Institution - 0071

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Brno, Czechia

Local Institution - 0004

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Hannover, Germany

Local Institution - 0072

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Olomouc, Olomoucký Kraj, Czechia

Local Institution - 0095

🇮🇹

Catania, Italy

Local Institution - 0093

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Milan, Italy

Local Institution - 0080

🇪🇸

Pamplona, Navarra, Spain

Local Institution - 0079

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Badalona, Barcelona [Barcelona], Spain

Local Institution - 0092

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Padova, Italy

Local Institution - 0094

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Rozzano, Italy

Local Institution - 0052

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Barcelona, Spain

Local Institution - 0051

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Madrid, Spain

Local Institution - 0115

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Madrid, Spain

Local Institution - 0096

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Sevilla, Spain

Local Institution - 0114

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Madrid, Spain

Local Institution - 0122

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Buenos Aires, Distrito Federal, Argentina

Local Institution - 0119

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Buenos Aires, Argentina

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