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A Study to Evaluate the Efficacy, Durability, and Safety of KSI-301 Compared to Aflibercept in Participants With Diabetic Macular Edema (DME)

Phase 3
Terminated
Conditions
Diabetic Macular Edema
Interventions
Other: Sham Procedure
Registration Number
NCT04603937
Lead Sponsor
Kodiak Sciences Inc
Brief Summary

This Phase 3 study will evaluate the efficacy, durability, and safety of KSI-301 compared to aflibercept in participants with treatment-naïve DME.

Detailed Description

This is a Phase 3, prospective, randomized, double-masked, two-arm, multi-center non-inferiority study evaluating the efficacy and safety of repeated intravitreal dosing of KSI-301 5 mg in participants with treatment-naïve DME.

The primary endpoint will be assessed at Year 1; additional secondary endpoints for efficacy will be assessed at Years 1 and 2.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
459
Inclusion Criteria
  1. Signed informed consent prior to participation in the study.
  2. Treatment-naïve diabetic macular edema, with vision loss and center involvement (if present) diagnosed within 9 months of screening.
  3. BCVA ETDRS letter score between 78 and 25 (-20/25 to 20/320 Snellen equivalent), inclusive, in the Study Eye.
  4. CST of ≥ 320 microns on SD-OCT (Heidelberg Spectralis or equivalent on other OCT instruments) as determined by the Reading Center.
  5. Decrease in vision determined by the Investigator to be primarily the result of DME.
  6. Type 1 or Type 2 diabetes mellitus and a HbA1c of ≤12%.
  7. Other protocol-specified inclusion criteria may apply.
Exclusion Criteria
  1. Macular edema in the Study Eye considered to be secondary to a cause other than DME.
  2. Active iris or angle neovascularization or neovascular glaucoma in the Study Eye.
  3. High-risk proliferative diabetic retinopathy characteristics in the Study Eye.
  4. History of Pan-retinal Photocoagulation (PRP) laser in the Study Eye within 3 months of screening.
  5. Tractional retinal detachment in the Study Eye.
  6. Active retinal disease other than the condition under investigation in the Study Eye.
  7. Any history or evidence of a concurrent ocular condition present, that in the opinion of the Investigator could require either medical or surgical intervention or affect macular edema or alter visual acuity during the study (e.g., vitreomacular traction, epiretinal membrane).
  8. Active or suspected ocular or periocular infection or inflammation in either eye at Day 1.
  9. Any prior use of an approved or investigational treatment for DME in the Study Eye (e.g., anti-VEGF, intraocular or periocular steroids, macular laser photocoagulation).
  10. Women who are pregnant or lactating or intending to become pregnant during the study.
  11. Uncontrolled blood pressure defined as a systolic value ≥ 180 mmHg or diastolic value ≥100 mmHg while at rest.
  12. Recent history (within the 6 months prior to screening) of myocardial infarction, stroke, transient ischemic attack, acute congestive heart failure or any acute coronary event.
  13. History of a medical condition that, in the judgment of the Investigator, would preclude scheduled study visits, completion of the study, or a safe administration of investigational product.
  14. Other protocol-specified exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
KSI-301 (Arm A)KSI-301Intravitreal injection of KSI-301 (5 mg) once every 4 weeks for 3 monthly doses followed by an individualized dosing regimen (every 8 to 24 weeks) via intravitreal injection from Week 16 to Week 100.
KSI-301 (Arm A)Sham ProcedureIntravitreal injection of KSI-301 (5 mg) once every 4 weeks for 3 monthly doses followed by an individualized dosing regimen (every 8 to 24 weeks) via intravitreal injection from Week 16 to Week 100.
Aflibercept (Arm B)Sham ProcedureIntravitreal injection of aflibercept (2 mg) once every 4 weeks for 5 monthly doses followed by aflibercept (2 mg) once every 8 weeks via intravitreal injection from Week 24 to 100.
Aflibercept (Arm B)AfliberceptIntravitreal injection of aflibercept (2 mg) once every 4 weeks for 5 monthly doses followed by aflibercept (2 mg) once every 8 weeks via intravitreal injection from Week 24 to 100.
Primary Outcome Measures
NameTimeMethod
Mean Change in BCVADay 1 to Week 64

Mean change in best-corrected visual acuity (BCVA) from baseline to the average of Weeks 60 and 64 (using Early Treatment Diabetic Retinopathy Study (ETDRS) Letters). Best Corrected Visual Acuity (BCVA) was measured on the Early Treatment Diabetic Retinopathy Study (ETDRS) chart at a starting distance of 4 meters. The BCVA letter score ranges from 0 to 100 (best score), and a gain in BCVA letter score from baseline indicates an improvement in visual acuity.

Secondary Outcome Measures
NameTimeMethod
Percentage of Patients With a ≥ 2-step Worsening on the ETDRS DRSS in Studies KS301P104 and KS301P105 CombinedDay 1 to Week 52

Percentage of patients with a ≥ 2-step worsening on the Early Treatment Diabetic Retinopathy Study (ETDRS) Diabetic Retinopathy Severity Scale (DRSS) from baseline at Week 52 using last observation carried forward (LOCF) in Studies KS301P104 and KS301P105 combined. The Diabetic Retinopathy Disease Severity Scale (DRSS) may be used to describe overall retinopathy severity as well as the change in severity over time. Severity range from level 10 (DR absent) to level 85 (advanced proliferative DR: posterior fundus obscured, or center of macula detached).

Percentage of Patients With a ≥ 2-step Worsening on the ETDRS DRSS in Study KS301P105Day 1 to Week 52

Percentage of patients with a ≥ 2-step worsening on the Early Treatment Diabetic Retinopathy Study (ETDRS) Diabetic Retinopathy Severity Scale (DRSS) from baseline at Week 52 using last observation carried forward (LOCF) in Study KS301P105. The Diabetic Retinopathy Disease Severity Scale (DRSS) may be used to describe overall retinopathy severity as well as the change in severity over time. Severity range from level 10 (DR absent) to level 85 (advanced proliferative DR: posterior fundus obscured, or center of macula detached).

Percentage of Patients in the KSI-301 Arm on a Q8W, Q12W, Q16W, Q20W, or Q24W Treatment IntervalWeek 56

Percentage of patients in the KSI-301 arm on a Q8W, Q12W, Q16W, Q20W, or Q24W treatment interval at the primary endpoint. Analyses include KSI-301 patients who completed a treatment interval from Week 56 onwards.

Mean Number of Intravitreal InjectionsDay 1 to Week 60

Mean number of intravitreal injections from Day 1 to Week 60

Mean Change in OCT CSTDay 1 to Week 64

Mean change in Optical Coherence Tomography (OCT) central subfield retinal thickness (CST) baseline to the average of Weeks 60 and 64

Trial Locations

Locations (71)

Cleveland Clinic Foundation, Cole Eye Institute

🇺🇸

Cleveland, Ohio, United States

CHRU Dijon Complexe Du Bocage

🇫🇷

Dijon, Côte-d'Or, France

Retina Specialists of Idaho

🇺🇸

Boise, Idaho, United States

Georgia Retina, P.C.

🇺🇸

Marietta, Georgia, United States

Centre Hospitalier Intercommunal de Créteil

🇫🇷

Créteil, France

Ospedale San Raffaele S.r.l. - PPDS

🇮🇹

Milano, Lombardia, Italy

Hadassah University Hospital

🇮🇱

Jerusalem, Israel

Talley Eye

🇺🇸

Evansville, Indiana, United States

Retina-Vitreous Surgeons of Central NY

🇺🇸

Liverpool, New York, United States

Northern California Retina Vitreous Associates

🇺🇸

Mountain View, California, United States

Retina Consultants of Hawaii, Inc

🇺🇸

'Aiea, Hawaii, United States

Retina Vitreous Associates of Florida

🇺🇸

Saint Petersburg, Florida, United States

Asheville Eye Associates

🇺🇸

Asheville, North Carolina, United States

Southeastern Retina Associates PC

🇺🇸

Knoxville, Tennessee, United States

Ophthalmic Consultants of Long Island

🇺🇸

Oceanside, New York, United States

Associated Retinal Consultants PC

🇺🇸

Royal Oak, Michigan, United States

Fondation Rothschild

🇫🇷

Paris, France

Austin Retina Associates (Round Rock)

🇺🇸

Round Rock, Texas, United States

Retina Consultants of Houston - (Woodlands)

🇺🇸

The Woodlands, Texas, United States

Southeast Retina Center

🇺🇸

Augusta, Georgia, United States

Retina Consultants of NV

🇺🇸

Henderson, Nevada, United States

Lekarna BENU

🇨🇿

Praha, Czechia

OFTEX s.r.o.

🇨🇿

Pardubice, Czechia

Bnai Zion

🇮🇱

Haifa, Israel

Kaplan MC

🇮🇱

Rehovot, Israel

Assuta HaShalom

🇮🇱

Tel Aviv, Israel

Tel Aviv Sourasky Medical Center

🇮🇱

Tel Aviv, Israel

Rand Eye Institute

🇺🇸

Deerfield Beach, Florida, United States

Vseobecna Fakultni

🇨🇿

Praha, Czechia

AOU dell'Università degli Studi della Campania Luigi Vanvitelli

🇮🇹

Naples, Italy

Centre Paradis Monticelli

🇫🇷

Marseille, France

Rambam MC

🇮🇱

Haifa, Israel

Meir MC

🇮🇱

Kfar Saba, Israel

Rabin Medical Center

🇮🇱

Petach Tikva, Israel

Shamir Medical Center Assaf Harofeh

🇮🇱

Tzrifin, Israel

Retina Research Institute of Texas

🇺🇸

Abilene, Texas, United States

Retina Consultants of San Diego

🇺🇸

Poway, California, United States

Retina Vitreous Associates

🇺🇸

Beverly Hills, California, United States

Retina Consultants of Orange County

🇺🇸

Fullerton, California, United States

Florida Eye Microsurgical Institute

🇺🇸

Boynton Beach, Florida, United States

National Ophthalmic Research Institute

🇺🇸

Fort Myers, Florida, United States

Retina Group of New England

🇺🇸

Waterford, Connecticut, United States

Sierra Eye Associates

🇺🇸

Reno, Nevada, United States

Fort Lauderdale Eye Institute

🇺🇸

Plantation, Florida, United States

Vitreo Retinal Consultants

🇺🇸

Hauppauge, New York, United States

Southern Vitreoretinal Associates

🇺🇸

Tallahassee, Florida, United States

Maine Eye Center

🇺🇸

Portland, Maine, United States

Retina Consultants, LLC

🇺🇸

Salem, Oregon, United States

Retina Consultants of Houston-(Katy)

🇺🇸

Katy, Texas, United States

Texas Retina Associates

🇺🇸

Plano, Texas, United States

Hôpital Lariboisière - Service Pharmacie , Essais cliniques - Aude Jacob

🇫🇷

Paris, France

Emanuelli Research & Development Center LLC

🇵🇷

Arecibo, Puerto Rico

Hôpital de La Croix Rousse

🇫🇷

Lyon, Rhône, France

Szabolcs-Szatmar-Bereg Megyei Korhazak es Egyetemi Oktatokorhaz , Josa Andras Oktatókórház

🇭🇺

Nyíregyháza, Szabolcs-Szatmár-Bereg, Hungary

Optimum Profesorskie Centrum Okulistyki

🇵🇱

Gdansk, Pomorskie, Poland

Oftalmika Sp. z o.o.

🇵🇱

Bydgoszcz, Poland

Dr Nowosielska Okulistyka i Chirurgia Oka

🇵🇱

Warszawa, Poland

Fondazione Policlinico Universitario A Gemelli

🇮🇹

Roma, Lazio, Italy

Semmelweis Egyetem

🇭🇺

Budapest, Hungary

Uniwersyteckie Centrum Kliniczne Im. Prof. K. Gibinskiego Slaskiego Uniwersytetu Medycznego w Katowi

🇵🇱

Katowice, Slaskie, Poland

Specjalistyczny Szpital im. Alfreda Sokolowskiego

🇵🇱

Wałbrzych, Poland

Bajcsy-Zsilinszky Korhaz es Rendelointezet

🇭🇺

Budapest, Hungary

Budapest Retina Associates Kft

🇭🇺

Budapest, Hungary

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza Radeckiego we Wroclawiu

🇵🇱

Wrocław, Poland

Retinal Research Institute, LLC

🇺🇸

Phoenix, Arizona, United States

Retinal Consultants Medical Group Inc

🇺🇸

Sacramento, California, United States

Austin Research Center for Retina

🇺🇸

Austin, Texas, United States

Medical Center Ophthalmology Associates

🇺🇸

San Antonio, Texas, United States

Vitreoretinal Surgery PA

🇺🇸

Minneapolis, Minnesota, United States

Retina Institute of Virginia

🇺🇸

Richmond, Virginia, United States

Retina Associates of Western NY

🇺🇸

Rochester, New York, United States

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