MedPath

Study of Tilpisertib Fosmecarbil in Participants With Moderately to Severely Active Ulcerative Colitis

Phase 2
Recruiting
Conditions
Ulcerative Colitis
Interventions
Registration Number
NCT06029972
Lead Sponsor
Gilead Sciences
Brief Summary

The goal of this study is to learn if tilpisertib fosmecarbil (formerly known as GS-5290) is effective and safe in treating participants with moderate to severe ulcerative colitis. The study will compare participants in different treatment groups treated with tilpisertib fosmecarbil with participants treated with placebo.

The primary objective of this study is to demonstrate the efficacy of tilpisertib fosmecarbil, compared to placebo control, in achieving Clinical Response at Week 12.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
176
Inclusion Criteria
  • Individuals assigned male at birth, or nonpregnant, nonlactating individuals assigned female at birth, 18 to 75 years of age based on the date of the screening visit.
  • Ulcerative colitis (UC) of at least 90-day duration before randomization confirmed by endoscopy and histology at any time in the past AND a minimum disease extent of 15 cm from the anal verge. Documentation of endoscopy and histology consistent with the diagnosis of UC must be available in the source documents prior to the initiation of screening.
  • Moderately to severely active UC as determined during screening with a modified Mayo Clinic Score based on the sum of Stool Frequency, Rectal Bleeding, and Endoscopic Finding of 5 to 9 points and an endoscopic subscore of 2 to 3 (determined by central reader).
  • Previous treatment history of approved UC therapy with at least one advanced therapy mechanisms of action but failure (ie, loss of response or lack of response) of no more than 3 different advanced therapy mechanisms of action.
  • A surveillance colonoscopy for dysplasia is required prior to randomization if indicated by regional guidelines for individuals with UC.

Key

Exclusion Criteria
  • Current diagnosis of Crohn's Disease (CD) or diagnosis of indeterminate colitis due to an enteric pathogen, lymphocytic or collagenous colitis.
  • Individuals with disease limited to the rectum (ulcerative proctitis) during screening endoscopy.
  • Requirement for ongoing therapy with or prior use of any prohibited medications.
  • Active clinically significant infection, or any infection requiring hospitalization or treatment with intravenous anti-infectives within 8 weeks.

of randomization; or any infection requiring oral anti-infective therapy within 6 weeks of randomization.

  • History of opportunistic infection.
  • Current diagnosis of acute severe colitis, fulminant colitis, or toxic megacolon.

Note: Other protocol-defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Tilpisertib Fosmecarbil PlaceboTilpisertib FosmecarbilBlinded Treatment Phase: Participants will receive tilpisertib fosmecarbil placebo for up to 12 weeks. An efficacy assessment will be performed at Week 12. • Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose C for up to Week 52. Non-responder Treatment Phase: • Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose A for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved Clinical Response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve Clinical Response at Non-responder Treatment Phase Week 12 will discontinue study drug.
Tilpisertib Fosmecarbil PlaceboPlaceboBlinded Treatment Phase: Participants will receive tilpisertib fosmecarbil placebo for up to 12 weeks. An efficacy assessment will be performed at Week 12. • Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose C for up to Week 52. Non-responder Treatment Phase: • Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose A for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved Clinical Response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve Clinical Response at Non-responder Treatment Phase Week 12 will discontinue study drug.
Tilpisertib Fosmecarbil Dose CTilpisertib FosmecarbilBlinded Treatment Phase: Participants will receive tilpisertib fosmecarbil Dose C for up to 12 weeks. An efficacy assessment will be performed at Week 12. • Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose C for up to Week 52. Non-responder Treatment Phase: • Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose B for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve clinical response at Non-responder Treatment Phase Week 12 will discontinue study drug.
Tilpisertib Fosmecarbil Dose ATilpisertib FosmecarbilBlinded Treatment Phase: Participants will receive tilpisertib fosmecarbil Dose A for up to 12 weeks. An efficacy assessment will be performed at Week 12. • Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Non-responder Treatment Phase: • Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose A for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve clinical response at Non-responder Treatment Phase Week 12 will discontinue study drug.
Tilpisertib Fosmecarbil Dose BTilpisertib FosmecarbilBlinded Treatment Phase: Participants will receive tilpisertib fosmecarbil Dose B for up to 12 weeks. An efficacy assessment will be performed at Week 12. • Participants who achieve clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Non-responder Treatment Phase: • Participants who do not achieve clinical response at Week 12 will discontinue the Blinded Treatment Phase and have the option to enter into the Non-responder Treatment Phase. Participants will receive tilpisertib fosmecarbil Dose B for another 12 weeks. An efficacy assessment will be performed at Week 12 of the Non-responder Treatment Phase. Participants who achieved clinical response will receive tilpisertib fosmecarbil Dose B for up to Week 52. Participants who do not achieve clinical response at Non-responder Treatment Phase Week 12 will discontinue study drug.
Primary Outcome Measures
NameTimeMethod
Proportion of Participants Achieving Clinical Response Per Modified Mayo Clinic Score at Week 12Week 12

Clinical Response is defined as a decrease from baseline of ≥ 2 points and at least 30% in 3 components of the modified Mayo Clinic Score, Stool Frequency, Rectal Bleeding, and Endoscopic Findings, in addition to a ≥ 1 point decrease from baseline in the Rectal Bleeding subscore or Rectal Bleeding subscore of ≤ 1. The modified Mayo Clinic Score is a scoring system for assessment of UC activity and is composed of subscores from endoscopy (range: 0 to 3, where 0 = normal or inactive disease and 3 = severe disease \[spontaneous bleeding, ulceration\]), rectal bleeding (range: 0 to 3, where 0 = no blood seen and 3 = blood alone passes), and stool frequency (range: 0 to 3, where 0 = normal number of stools and 3 = at least 5 or more stools more than normal). Total score for modified Mayo Clinic Score ranges from 0 to 9 (sum of all subscores), with higher scores indicating higher disease activity.

Secondary Outcome Measures
NameTimeMethod
Percentage of Participants Experiencing Treatment-emergent Adverse Events (TEAEs)First dose date up to Week 52 (responders) or Week 64 (non-responders) plus 30 days
Proportion of Participants Achieving Clinical Remission Per Modified Mayo Clinic Score at Week 12Week 12

Clinical Remission is defined as a Stool Frequency subscore ≤ 1 and not greater than baseline, Rectal Bleeding subscore of 0, and Endoscopic Findings subscore ≤ 1 at Week 12. The modified Mayo Clinic Score is a scoring system for assessment of UC activity and is composed of subscores from endoscopy (range: 0 to 3, where 0 = normal or inactive disease and 3 = severe disease \[spontaneous bleeding, ulceration\]), rectal bleeding (range: 0 to 3, where 0 = no blood seen and 3 = blood alone passes), stool frequency (range: 0 to 3, where 0 = normal number of stools and 3 = at least 5 or more stools more than normal). Total score for modified Mayo Clinic Score ranges from 0 to 9 (sum of all subscores), with higher scores indicating higher disease activity.

Proportion of Participants Achieving Histologic Endoscopic Mucosal Improvement at Week 12Week 12

Histologic Endoscopic Mucosal Improvement is defined as an Endoscopic Findings subscore ≤ 1 and Geboes score ≤ 3.1 (indicating neutrophil infiltration in \< 5% of crypts, no crypt destruction and no erosions, ulcerations, or granulation tissue). Endoscopic subscore is a part of the modified Mayo Clinic Score which is a scoring system for assessment of UC activity. Endoscopic subscore range: 0 to 3, where 0 = normal or inactive disease, 1 = mild disease (erythema, decreased vascular pattern), 2 = moderate disease (marked erythema, lack of vascular pattern, friability, erosions), and 3 = severe disease (spontaneous bleeding, ulceration). Geboes histologic remission is assessed using the Geboes histologic scores to identify histologic changes in ulcerative colitis. Possible scores are graded as Grade 0 to Grade 5, with higher grade representing higher levels of disease activity.

Percentage of Participants Experiencing Clinically Significant Laboratory AbnormalitiesFirst dose date up to Week 52 (responders) or Week 64 (non-responders) plus 30 days
Proportion of Participants Achieving Endoscopic Response at Week 12Week 12

Endoscopic Response is defined as an Endoscopic Findings subscore ≤ 1 at Week 12. Endoscopic subscore is a part of the modified Mayo Clinic Score which is a scoring system for assessment of UC activity. Endoscopic subscore range: 0 to 3, where 0 = normal or inactive disease, 1 = mild disease (erythema, decreased vascular pattern), 2 = moderate disease (marked erythema, lack of vascular pattern, friability, erosions), and 3 = severe disease (spontaneous bleeding, ulceration). Higher scores indicate higher disease activity.

Trial Locations

Locations (123)

Istituto Clinico Humanitas

🇮🇹

Rozzano, Italy

Azienda Sanitaria Universitaria Friuli Centrale

🇮🇹

Udine, Italy

Hyogo Medical University Hospital

🇯🇵

Hyogo, Japan

Nzoz Vivamed

🇵🇱

Warszawa, Poland

Fairfield General Hospital

🇬🇧

Bury, United Kingdom

Cambridge University Hospitals NHS Foundation Trust

🇬🇧

Cambridge, United Kingdom

Barts Health NHS Trust

🇬🇧

London, United Kingdom

Norfolk and Norwich University Hospital Nhs Foundation Trust

🇬🇧

Norwich, United Kingdom

Amicis Research Center

🇺🇸

Valencia, California, United States

Arizona Digestive Health

🇺🇸

Sun City, Arizona, United States

GastroSb Weight Loss Clinic

🇺🇸

Chula Vista, California, United States

Southern California Research Centers

🇺🇸

Coronado, California, United States

VVCRD Research

🇺🇸

Garden Grove, California, United States

UC San Diego Health System

🇺🇸

La Jolla, California, United States

Gastro Care Institute

🇺🇸

Lancaster, California, United States

Om Research LLC

🇺🇸

Lancaster, California, United States

United Medical Doctors

🇺🇸

Murrieta, California, United States

University of California, Davis

🇺🇸

Sacramento, California, United States

University of California San Francisco

🇺🇸

San Francisco, California, United States

Luna Research

🇺🇸

Coral Gables, Florida, United States

University of Florida

🇺🇸

Gainesville, Florida, United States

The Medici Medical Research

🇺🇸

Hollywood, Florida, United States

Encore Medical Research, LLC

🇺🇸

Hollywood, Florida, United States

Florida Research Institute

🇺🇸

Largo, Florida, United States

Wellness Research Center

🇺🇸

Miami, Florida, United States

IMIC Inc

🇺🇸

Miami, Florida, United States

Reserka LLC

🇺🇸

Miami, Florida, United States

GI PROS Research

🇺🇸

Naples, Florida, United States

Revival Clinical Research

🇺🇸

Orlando, Florida, United States

Digestive and Liver Center of Florida, LLC

🇺🇸

Orlando, Florida, United States

Advanced Medical Research Center

🇺🇸

Port Orange, Florida, United States

Gastroenterology Associates of Florida - GI Alliance

🇺🇸

Wellington, Florida, United States

Atlanta Center For Gastroenterology P.C.

🇺🇸

Decatur, Georgia, United States

Corewell Health

🇺🇸

Grand Rapids, Michigan, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Gastroenterology Associates of North Mississippi

🇺🇸

Oxford, Mississippi, United States

Digestive Health Specialists

🇺🇸

Tupelo, Mississippi, United States

St. Charles Clinical Research

🇺🇸

Saint Louis, Missouri, United States

Ellipsis Research Group

🇺🇸

Brooklyn, New York, United States

NYU Langone Long Island Clinical Research Associates

🇺🇸

Great Neck, New York, United States

Gastroenterology & Hepatology Specialists Inc

🇺🇸

Canton, Ohio, United States

Ohio Gastroenterology & Liver Institute

🇺🇸

Cincinnati, Ohio, United States

The Ohio State University Wexner Medical Centre

🇺🇸

Columbus, Ohio, United States

Dayton Gastroenterology, LLC

🇺🇸

Dayton, Ohio, United States

Great Lakes Gastroenterology Research, LLC

🇺🇸

Mentor, Ohio, United States

Skyline Gastroenterology of West Tennessee

🇺🇸

Jackson, Tennessee, United States

Hill Country Digestive Health

🇺🇸

Boerne, Texas, United States

Gastroenterology Research of America

🇺🇸

El Paso, Texas, United States

DHAT Research Institute

🇺🇸

Garland, Texas, United States

Southwest Clinical Trials

🇺🇸

Houston, Texas, United States

Lubbock Digestive Disease Associates

🇺🇸

Lubbock, Texas, United States

GI Associates and Endoscopy Center - GI Alliance

🇺🇸

Mansfield, Texas, United States

Gastroenterology Research of San Antonio

🇺🇸

San Antonio, Texas, United States

Tyler Research Institute, LLC

🇺🇸

Tyler, Texas, United States

LinQ Research LLC

🇺🇸

Pearland, Texas, United States

Clinical Associates in Research Therapeutics of America

🇺🇸

San Antonio, Texas, United States

Queen Elizabeth Hospital

🇦🇺

Woodville, South Australia, Australia

Monash Medical Centre

🇦🇺

Clayton, Victoria, Australia

Northern Health

🇦🇺

Epping, Victoria, Australia

Gastroenterology Associates of Tidewater

🇺🇸

Chesapeake, Virginia, United States

Emeritas Group Research

🇺🇸

Lansdowne Town Center, Virginia, United States

Gastroenterology Consultants of Southwest Virginia

🇺🇸

Roanoke, Virginia, United States

Swedish Medical Center

🇺🇸

Seattle, Washington, United States

Mater Adult Hospital

🇦🇺

South Brisbane, Queensland, Australia

Princess Alexandra Hospital

🇦🇺

Woolloongabba, Queensland, Australia

Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

Footscray Hospital

🇦🇺

Footscray, Victoria, Australia

Medical University of Innsbruck

🇦🇹

Innsbruck, Austria

University of Salzburg, Universitätsklinik für Innere Medizin III

🇦🇹

Salzburg, Austria

Universitätsklinikum St. Pölten

🇦🇹

St. Pölten, Austria

Medical University Vienna, Department of Internal Medicine III, Division Gastroenterology and Hepatology

🇦🇹

Vienna, Austria

Universitaire Ziekenhuis Leuven

🇧🇪

Leuven, Belgium

London Health Sciences Centre-University Hospital

🇨🇦

London, Canada

Physician's Clinical Research, Inc. (PCRI)

🇨🇦

Toronto, Canada

Mount Sinai Hospital

🇨🇦

Toronto, Canada

TDDA Speciality Research

🇨🇦

Vaughan, Canada

Centre Hospitalier Universitaire Grenoble

🇫🇷

Grenoble Cedex 9, France

Hôpital Claude Huriez

🇫🇷

Little Cedex, France

Hopital Saint Eloi

🇫🇷

Montpellier, France

Centre Hospitalier Universitaire de Nantes

🇫🇷

Nantes, France

Institut des MICI

🇫🇷

Neuilly Sur Seine, France

CHU de Saint Etienne - Hopital Nord

🇫🇷

Saint-Etienne, France

Hopital Rangueil

🇫🇷

Toulouse, France

CHRU Nancy

🇫🇷

Vandoeuvre Les Nancy, France

Charite Universitaetsmedizin Berlin Campus CVK, Department of Hepatology and Gastroenterology

🇩🇪

Berlin, Germany

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

Universitatsklinikum Schleswig-Holstein

🇩🇪

Kiel, Germany

Eugastro Gmbh

🇩🇪

Liepzig, Germany

Universitaetsklinikum Ulm Klinik fur Innere Medizin I CED Studien Ambulanz

🇩🇪

Ulm, Germany

Tolna Megye Balassa Janos Korhaz

🇭🇺

Beri Balogh, Hungary

Szent Janos Korhaz es Eszak-budai Egyesitett Korhazak

🇭🇺

Budapest, Hungary

AZIENDA UNICA OSPEDALIERO-UNIVERSITARIA"RENATO DULBECCO" - AOU"Mater Domini"

🇮🇹

Catanzaro, Italy

IRCCS Istituto Clinico Humanitas

🇮🇹

Milano, Italy

Azienda Ospedaliera San Camillo Forlanini

🇮🇹

Roma, Italy

Fukuoka University Hospital

🇯🇵

Jonan-ku, Japan

The Jikei University Hospital

🇯🇵

Minato-ku, Japan

Kitasato University Kitasato Institute Hospital

🇯🇵

Minato-ku, Japan

Kyorin University Hospital

🇯🇵

Mitaka-shi, Japan

Nagasaki University Hospital

🇯🇵

Nagasaki, Japan

Ishida Clinic of IBD and Gastroenterology

🇯🇵

Oita-shi, Japan

Saga University Hospital

🇯🇵

Sagaken, Japan

Kitasato University Hospital

🇯🇵

Sagamihara, Japan

Sapporo Medical University Hospital

🇯🇵

Sapporo, Japan

Tokyo Medical And Dental University Hospital

🇯🇵

Toukiyouto, Japan

Yonsei University Severance Hospital

🇰🇷

Seodaemun-Gu, VIC, Korea, Republic of

Inje University

🇰🇷

Busan, Korea, Republic of

Yeungnam University Hospital

🇰🇷

Daegu, Korea, Republic of

Kyungpook National University Hospital

🇰🇷

Jung-gu, Korea, Republic of

Kyung Hee University Medical Center

🇰🇷

Seoul, Korea, Republic of

Kangbuk Samsung Hospital

🇰🇷

Seoul, Korea, Republic of

Hanyang University Hospital

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Wonju Severance Christian Hospital

🇰🇷

Wonju, Korea, Republic of

Economicus Sp. z o.o., Niepubliczny Zakład Opieki Zdrowotnej (NZOZ) ALL-MEDICUS

🇵🇱

Katowice, Poland

Gabinet Endoskopii Przewodu Pokarmowego

🇵🇱

Krakow, Poland

Kliniczny Szpital Wojewódzki Nr 2 im. Sw. Jadwigi Królowej w Rzeszowie

🇵🇱

Rzeszów, Poland

Specjalistyczna Praktyka Lekarska Leszek Bryniarski

🇵🇱

Sopot, Poland

GASTROMED Kopon, Zmudzinski i wspolnicy Sp. J. Specialized Center of Gastroenterology and Endoscopy

🇵🇱

Torun, Poland

Medical Network Sp. z o.o. WIP Warsaw IBD Point Profesor Kierkus

🇵🇱

Warszawa, Poland

Specjalistyczne Gabinety Lekarskie Body Clinic

🇵🇱

Warszawa, Poland

Centrum Medyczne Oporow

🇵🇱

Wroclaw, Poland

Intesto, Gastroenterologische Praxis Crohn-Colitis-Zentrum

🇨🇭

Bern, Switzerland

University Hospital Southampton Nhs Foundation Trust

🇬🇧

Southampton, United Kingdom

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