Skip to main content
Clinical Trials/DRKS00030327
DRKS00030327
Recruiting
Not Applicable

Description of the clinical picture of adults with rare genetic syndromes - 2022-2019-HUM-ADULT

Heinrich-Heine-Universität Düsseldorf0 sites100 target enrollmentSeptember 22, 2022

Overview

Phase
Not Applicable
Intervention
Not specified
Conditions
icolaides-Baraitser syndromeCoffin-Siris syndromeCostello syndromeCardiofaziocutaneous (CFC) syndrome
Sponsor
Heinrich-Heine-Universität Düsseldorf
Enrollment
100
Status
Recruiting
Last Updated
last year

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
September 22, 2022
End Date
TBD
Last Updated
last year
Study Type
Observational
Sex
All

Investigators

Eligibility Criteria

Inclusion Criteria

  • Molecularly confirmed diagnosis of one of the following four syndromes:
  • Nicolaides\-Baraitser syndrome
  • Coffin\-Siris syndrome
  • Costello syndrome
  • CFC (Cardio\-facio\-cutaneous) syndrome
  • \- Written informed consent from the participant or the legal guardian if the participant has a legal guardian.

Exclusion Criteria

  • \- Individuals with a syndromal disease without molecular genetic confirmation.
  • \- Age\<18 years
  • \- No consent for data collection in the context of this study

Outcomes

Primary Outcomes

Not specified

Similar Trials