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Optimal care for Duchenne and Becker muscular dystrophy: Learning, behavior and careful care

Conditions
DMD&BMD
Duchenne and Becker muscular dystrophy
Dystrophinopathy
10028302
10009841
Registration Number
NL-OMON46818
Lead Sponsor
eids Universitair Medisch Centrum
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Pending
Sex
Not specified
Target Recruitment
131
Inclusion Criteria

- Progressive muscle weakness
- Confirmed diagnosis of dystrophinopathy: defined mutation in the dystrophin gene and / or either reduced or lack of dystrophin levels in a muscle biopsy
- Age > 4 years
- Dutch as mother tongue

Exclusion Criteria

- No informed consent

Study & Design

Study Type
Observational non invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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