MedPath

NG-Nitro-L-Arginine in Treating Patients With Advanced Solid Tumors

Phase 1
Terminated
Conditions
Unspecified Adult Solid Tumor, Protocol Specific
Registration Number
NCT01324115
Lead Sponsor
Cancer Research UK
Brief Summary

RATIONALE: NG-nitro-L-arginine may stop the growth of tumor cells by disrupting blood flow to the tumor.

PURPOSE: This phase I trial is studying the side effects and best dose of NG-nitro-L-arginine in treating patients with advanced solid tumors.

Detailed Description

OBJECTIVES:

Primary

* To determine if there is a differential effect of NG-nitro-L-arginine (L-NNA) on tumor and normal tissue vasculature (blood flow/volume) in patients with advanced solid tumors in order to propose a safe recommended dose range for further evaluation.

Secondary

* To determine the correlation between plasma concentration of L-NNA and toxicity and vascular effects.

* To further determine the effects of nitric oxide synthase (NOS) inhibition on tumor tissue vasculature.

* To determine the pharmacokinetics of L-NNA.

* To determine the safety profile of L-NNA.

Tertiary

* To evaluate the potential pharmacodynamic effect of NOS inhibition on angiogenesis.

* To evaluate the effect of L-NNA on circulating NOS levels.

* To evaluate the correlation between expression levels of iNOS and eNOS and vasoconstrictive effects of L-NNA in tumor tissue (where available).

OUTLINE: This is a dose-escalation study.

Patients receive a single dose of NG-nitro-L-arginine (L-NNA) IV over 10 minutes on day 1. All patients undergo up to 6 dynamic contrast-enhanced computed tomography (DCE-CT).

Patients enrolled in the expanded cohort study undergo 4 additional scans of dynamic contrast-enhanced magnetic resonance imaging (DCE-MRI) as well as DCE-CT scans.

Blood samples are collected periodically for pharmacokinetic and biomarker studies. Samples are analyzed for L-NNA levels via a reverse-phase high performance liquid chromatography, NOS inhibition via cGMP analysis, and VEGF-A and osteopontin levels. Previously collected biopsy samples are analyzed for iNOS and eNOS expression.

After completion of study treatment and one week assessments, patients are followed up once a week for 28 days and then monthly thereafter (if required).

Peer Reviewed and Funded or Endorsed by Cancer Research UK.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
6
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Dose-limiting toxicities (DLT) and/or subsequent maximum dose
Dose at which there is no additional differential effect of L-NNA on the tumor vasculature as measured by dynamic contrast-enhanced computed tomography (DCE-CT)
Pharmacokinetic (predominantly AUC-dependent specific vascular effects) dependent effects (duration and magnitude of effect on blood flow/volume) in the tumor tissue compared to renal tissue using data from volumetric assessments via DCE-CT
Secondary Outcome Measures
NameTimeMethod
Effect on tumor blood perfusion using dynamic contrast-enhanced magnetic resonance imaging (DCE-MRI) with additional blood oxygen level-dependent (BOLD) imaging and diffusion-weighted imaging (DWI) sequences
Causality of each adverse event to L-NNA and severity grade according to NCI CTCAE Version 4.02
Tertiary Outcome(s) - Measurement of L-NNA concentrations in plasma samples
Measurement of serum biomarker concentrations, osteopontin, and vascular endothelial growth factor (VEGF-A)
Measurement of NOS concentrations in circulating blood (cyclic guanine monophosphate analysis)
Measurement of iNOS and eNOS expression levels in pre-treatment tumor biopsy samples (where available)

Trial Locations

Locations (1)

Mount Vernon Cancer Centre at Mount Vernon Hospital

🇬🇧

Northwood, England, United Kingdom

© Copyright 2025. All Rights Reserved by MedPath