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Isavuconazole (BAL8557) in the Treatment of Candidemia and Other Invasive Candida Infections

Phase 3
Completed
Conditions
Mycoses
Candidiasis, Invasive
Candidemia
Interventions
Registration Number
NCT00413218
Lead Sponsor
Astellas Pharma Inc
Brief Summary

The purpose of the study is to compare the safety and efficacy of isavuconazole versus caspofungin followed by voriconazole in the treatment of candidemia and other invasive Candida infections.

Detailed Description

Candida infections, representing approximately 80% of all major systemic fungal infections, are the fourth most common cause of nosocomial bloodstream infections, with a mortality rate of 40%. Isavuconazole is not yet approved for the treatment of fungal infections. This study investigates the efficacy and safety of intravenous and oral isavuconazole. Patients are randomized to isavuconazole and the reference regimen. Patients with a positive blood- or deep tissue culture of candida fungi can be included.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
450
Inclusion Criteria
  • Patients with candidemia or with an invasive Candida infection
  • Presence of fever, hypothermia or other appropriate local sign of infection
  • Female patients must be non-lactating and at no risk of pregnancy
Exclusion Criteria
  • Patients with a sole diagnosis of mucocutaneous candidiasis, i.e. oropharyngeal, esophageal or genital candidiasis; or candidal lower urinary tract infection or Candida isolated solely from respiratory tract specimens
  • Patients with candidemia who failed a previous antifungal therapy for the same infection
  • Patients previously enrolled in a phase III study with isavuconazole
  • Patients with a body weight <40kg

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Isavuconazole (ISA)IsavuconazoleParticipants received 3 intravenous (IV) loading doses of 200 mg of isavuconazole on days 1 and 2, followed by an IV maintenance dose of 200 mg once daily from day 3 to day 56. On day 11 at the discretion of the investigator, non-neutropenic patients could switch from IV to oral therapy. Oral therapy consisted of 200 mg isavuconazole twice daily.
Caspofungin (CAS)/VoriconazoleCaspofunginParticipants received 1 intravenous (IV) loading dose of 70 mg CAS on day 1, followed by an IV maintenance dose of 50 mg CAS from day 2 to day 56. On day 11 at the discretion of the investigator, non-neutropenic patients could switch from IV CAS to oral voriconazole comprising of a loading dose of 400 mg twice daily (BID) on the first day of oral therapy followed by standard dosing of 200 mg BID thereafter.
Caspofungin (CAS)/VoriconazoleVoriconazoleParticipants received 1 intravenous (IV) loading dose of 70 mg CAS on day 1, followed by an IV maintenance dose of 50 mg CAS from day 2 to day 56. On day 11 at the discretion of the investigator, non-neutropenic patients could switch from IV CAS to oral voriconazole comprising of a loading dose of 400 mg twice daily (BID) on the first day of oral therapy followed by standard dosing of 200 mg BID thereafter.
Primary Outcome Measures
NameTimeMethod
Percentage of Participants With Overall Response of Success at the End of Intravenous Therapy (EOIV) as Determined by the Data Review Committee (DRC) Based on the Assessments of Clinical and Mycological Responses as Well as Alternative Systemic AFT UseEnd of Intravenous Treatment (EOIV) (Days 11-56)

A Data Review Committee (DRC) was established from independent experts in the field of fungal infections to determine diagnosis and outcomes independently of the investigators and sponsor. Success was defined as clinical response (complete or partial) and mycological response (eradication or presumed eradication) without the use of alternative systemic antifungal therapy (AFT) within 48 hours after the last dose of IV study medication.

Secondary Outcome Measures
NameTimeMethod
Percentage of Participants With Overall Response of Success at EOT and Follow Up Visit 2 (FU2) as Determined by the DRC Based on the Assessments of Clinical and Mycological Responses as Well as Alternative Systemic AFT Use at EOT and FU2EOT (Day 56) and FU2 (6 weeks after end of treatment)

A data review committee (DRC) was established from independent experts in the field of fungal infections to determine diagnosis and outcomes independently of the investigators and sponsor. Success was defined as clinical response (complete or partial) and mycological response (eradication or presumed eradication), without the use of alternative systemic antifungal therapy AFT within 48 hours after the last dose of IV study medication (for EOT analysis) or for continued treatment of the primary infection, or for recurrent or emergent infection by FU2, with no recurrent or emergent infection by FU2 (for FU2 analysis).

Percentage of Participants With Clinical Response of Success at EOIV, EOT, FU1 and FU2 as Determined by the Data Review Committee (DRC)EOIV (Days 11-56), EOT (Day 56), FU1 (2 weeks after end of treatment) and FU2 (6 weeks after end of treatment)

A data review committee (DRC) was established from independent experts in the field of fungal infections to determine diagnosis and outcomes independently of the investigators and sponsor. Success was defined as clinical response (complete or partial).

Percentage of Participants With Overall Response of Success at Follow Up Visit 1 (FU1-2 Weeks After End of Treatment (EOT)) as Determined by the DRC Based on the Assessments of Clinical, Mycological Responses and Antifungal Therapy (AFT)End of Treatment (EOT) (Day 56) and FU1 (2 weeks after end of treatment)

A data review committee (DRC) was established from independent experts in the field of fungal infections to determine diagnosis and outcomes independently of the investigators and sponsor. Success was defined as clinical response (complete or partial) and mycological response (eradication or presumed eradication), without the use of alternative systemic AFT within 48 hours after the last dose of IV study medication.

Percentage of Participants With Mycological Response of Success at Day 7 and EOT as Determined by The InvestigatorDay 7 and EOT (Day 56)

Success was defined as mycological response (eradication or presumed eradication).

Percentage of Participants With Mycological Response of Success at EOIV, EOT, FU1 and FU2 as Determined by the Data Review Committee (DRC)EOIV (Days 11-56), EOT (Day 56), FU1 (2 weeks after end of treatment) and FU2 (6 weeks after end of treatment)

A data review committee (DRC) was established from independent experts in the field of fungal infections to determine diagnosis and outcomes independently of the investigators and sponsor. Success was defined as mycological response (Eradication or Presumed Eradication).

Percentage of Participants With Clinical Response of Success at Day 7 and EOT as Determined by The InvestigatorDay 7 and EOT (Day 56)

Investigators defined clinical response as success if participants exhibited complete or partial clinical response after evaluation of clinical signs and symptoms.

All-Cause Mortality (ACM) at Day 14 and Day 56Day 14 and Day 56

All-cause mortality is represented as the percentage of participants who died on or before the analysis day. Participants who were lost to follow-up (i.e., unknown survival status) before the analysis day were counted as death. All-cause mortality was examined on Day 14 and Day 56.

Time to First Confirmed Negative CultureDay 1 up to FU1 (2 weeks after EOT (Day 56))

The first confirmed negative blood culture was defined as the first negative blood culture on or after first dose followed by a second negative blood culture at least 24 hours apart without any positive blood cultures in between. A participant without a confirmed negative blood culture was censored on the participant's last visit day. This endpoint was analyzed for mITT participants with candidemia only using the Kaplan-Meier method. Only participants with at least one positive blood culture on or prior to first dose and the culture not resolved prior to first dose were included in this analysis

Trial Locations

Locations (113)

Idaho Falls Infectious Diseases PLLC

🇺🇸

Idaho Falls, Idaho, United States

Somero Research Corporation

🇺🇸

Palm Desert, California, United States

Loyola University Hospital

🇺🇸

Maywood, Illinois, United States

Springfield Clinic LLP

🇺🇸

Springfield, Illinois, United States

Jersey Shore University Medical Center

🇺🇸

Neptune, New Jersey, United States

Hospital General de Agudos Dr. Cosme Argerich

🇦🇷

La Boca, Argentina

Fremantle Hospital

🇦🇺

Fremantle, Australia

Mater Adult Hospital

🇦🇺

South Brisbane, Australia

Westmead Hospital

🇦🇺

Westmead, Australia

Princess Alexandra Hospital

🇦🇺

Woolloongabba, Australia

Hospital Universitario de Santa Maria

🇧🇷

Santa Maria, Brazil

Hospital Dr. Hernan Henriquez Aravena

🇨🇱

Temuco, Chile

Universitaetsklinik Leipzig

🇩🇪

Leipzig, Germany

Universitaetsklinikum Leipzig

🇩🇪

Luebeck, Germany

Rabin MC

🇮🇱

Petah, Israel

Ente Ospedaliero Ospedeli Galliera

🇮🇹

Genova, Italy

AUB Medical Center

🇱🇧

Beirut, Lebanon

Hospital Ampang

🇲🇾

Ampang, Malaysia

Pusat Perubatan Universiti Kebangsaan Malaysia

🇲🇾

Kuala Lumpur, Malaysia

Auckland City Hospital

🇳🇿

Auckland, New Zealand

Philippine General Hospital

🇵🇭

Manila, Philippines

Singapore General Hospital - Parent

🇸🇬

Singapore, Singapore

Hospital del Mar

🇪🇸

Barcelona, Spain

Siriraj Hospital

🇹🇭

Bangkoknoi, Thailand

Maharat Nakhon Ratchasima Hospital

🇹🇭

Muang, Thailand

Srinagarind Hospital

🇹🇭

Muang, Thailand

Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

University of Maryland School of Medicine

🇺🇸

Baltimore, Maryland, United States

UMASS Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

Mercury Street Medical Group

🇺🇸

Butte, Montana, United States

Instituto Medico Especializado Alexander Fleming

🇦🇷

Ciudad Autonoma, Argentina

Hospital Britanico de Buenos Aires

🇦🇷

Capital Federal, Argentina

Hospital General de Agudos Dr. Carlos G. Durand

🇦🇷

Capital Federal, Argentina

Hospital Italiano de Buenos Aires

🇦🇷

Ciudad Autonoma, Argentina

Institut Jules Bordet

🇧🇪

Brussels, Belgium

Universitair Ziekenhuis Brussel

🇧🇪

Brussels, Belgium

ULB Hôpital Erasme

🇧🇪

Bruxelles, Belgium

Universitair Ziekenhuis Gent

🇧🇪

Gent, Belgium

Universitaire Ziekenhuizen Leuven

🇧🇪

Leuven, Belgium

Irmandade da Santa Casa de Misericordia de Porto Alegre

🇧🇷

Porto Alegre, Brazil

Hospital Felicio Rocho

🇧🇷

Belo Horizonte, Brazil

Hospital das Clinicas da Universidade Federal de Minas Gerai

🇧🇷

Belo Horizonte, Brazil

Santa Casa de Misericordia de Belo Horizonte

🇧🇷

Belo Horizonte, Brazil

Hospital das Clinicas da UFPR

🇧🇷

Curitiba, Brazil

Hospital Nossa Senhora das Gracas

🇧🇷

Curitiba, Brazil

Hospital Sao Lucas - PUCRS

🇧🇷

Porto Alegre, Brazil

Hospital Universitario Clementino Fraga Filho

🇧🇷

Rio de Janeiro, Brazil

Hôpital Maisonneuve - Rosemont

🇨🇦

Montreal, Quebec, Canada

Hospital del Salvador

🇨🇱

Santiago, Chile

Hamilton Health Sciences - Henderson Site

🇨🇦

Hamilton, Ontario, Canada

Universidade Federal de Sao Paulo - UNIFESP

🇧🇷

São Paulo, Brazil

University of Alberta Hospital

🇨🇦

Edmonton, Alberta, Canada

Hôpital de Brabois Adultes

🇫🇷

Vandoeuvre les Nancy, France

Queen's University

🇨🇦

Kingston, Ontario, Canada

University Health Network - Toronto General Hospital

🇨🇦

Toronto, Ontario, Canada

Hospital Dr. Sotero del Rio

🇨🇱

Puente Alto Santiago, Chile

West China Hospital of Sichuan University

🇨🇳

Chengdu, China

Hôpital Hautepierre

🇫🇷

Strasbourg, France

The Ottawa Hospital - General Campus

🇨🇦

Ottawa, Ontario, Canada

Huashan Hospital Fudan University

🇨🇳

Shanghai, China

Debreceni Egyetem Orvos- es Egeszsegtudomanyi Centrum

🇭🇺

Debrecen, Hungary

Charite Campus Mitte

🇩🇪

Berlin, Germany

Universitaetsklinikum Freiburg

🇩🇪

Freiburg, Germany

Klinikum St. Georg

🇩🇪

Leipzig, Germany

Universitaet Koeln

🇩🇪

Koeln, Germany

Universitaetsklinikum Wuerzburg

🇩🇪

Wuerzburg, Germany

Petz Aladar Megyei Oktato Korhaz

🇭🇺

Györ, Hungary

Kasturba Medical College and Hospital

🇮🇳

Mangalore, Karna, India

Kasturba Medical College K. M. C. Hospital

🇮🇳

Manipal, Karna, India

Amrita Institute Of Medical Science

🇮🇳

Cochin, Kerala, India

Deenanath Mangeshkar Hospital and Research Centre

🇮🇳

Pune, Mahara, India

Apollo Hospitals Educational & Research Foundation

🇮🇳

Chennai, India

Nizam's Institute of Medical Sciences

🇮🇳

Hyderabad, India

Rambam Health Care Campus

🇮🇱

Haifa, Israel

Chaim Sheba Medical Center

🇮🇱

Ramat Gan, Israel

AMRI Hospital

🇮🇳

Kolkata, India

Christian Medical College & Hospital

🇮🇳

Vellore Tamilnadu, India

Ha Emek Medical Center

🇮🇱

Afula, Israel

Hadassah Universtiy Hospital - Ein Kerem

🇮🇱

Jerusalem, Israel

Instituto Nacional de Ciencias Medicas y Nutricion Salvador

🇲🇽

Mexico, Mexico

Wolfson Medical Center

🇮🇱

Holon, Israel

Sapir Medical Center, Meir Hospital

🇮🇱

Kfar-Saba, Israel

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Ma

🇮🇹

Bologna, Italy

Sourasky MC Ichilov Hospital Tel Aviv

🇮🇱

Tel Aviv, Israel

Azienda Ospedaliera Spedali Civili di Brescia

🇮🇹

Brescia, Italy

Azienda Ospedaliero Universitaria San Martino

🇮🇹

Genova, Italy

Azienda Ospedaliera di Verona-Ospedale Civile Maggiore

🇮🇹

Verona, Italy

Rafik Hariri Uni Hospital

🇱🇧

Beirut, Lebanon

Hospital Civil de Guadalajara Dr Juan I Menchaca

🇲🇽

Guadalajara, Mexico

De La Salle Health Sciences Institute- DLSUMC

🇵🇭

Cavite City, Philippines

State Institution "Hematology Research Center" RAMS

🇷🇺

Moscow, Russian Federation

Hospital Civil de Guadalajara Fray Antonio Alcalde

🇲🇽

Guadalajara, Mexico

Hospital Universitario Dr Jose Eleuterio Gonzalez

🇲🇽

Monterrey, Mexico

S.I. Russian Oncological Research Center n.a. N.N. Blokhin

🇷🇺

Moscow, Russian Federation

Waikato Urology Research Ltd

🇳🇿

Hamilton, New Zealand

Hôpitaux Universitaires de Genève - HUG

🇨🇭

Geneva, Switzerland

Universitaetsspital Zuerich

🇨🇭

Zurich, Switzerland

National Neuroscience Institute

🇸🇬

Singapore, Singapore

Unitas Hospital

🇿🇦

Lyttelton Centurion, South Africa

Ramathibodi Hospital

🇹🇭

Ratchathewi, Thailand

Songklanagarind Hospital

🇹🇭

Hat Yai, Thailand

Maharaj Nakorn Chiang Mai Hospital

🇹🇭

Muang, Thailand

Temple University Health Sciences

🇺🇸

Philadelphia, Pennsylvania, United States

Regional Infection Diseases Infusion Center Inc.

🇺🇸

Lima, Ohio, United States

Metro Centre for Respiratory Diseases

🇮🇳

Noida, Delhi, India

Max Super Speciality Hospital

🇮🇳

New Delhi, Delhi, India

New York Presbyterian Hospital

🇺🇸

New York, New York, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

University of California Davis Health System

🇺🇸

Sacramento, California, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

University of California at San Francisco

🇺🇸

San Francisco, California, United States

Infectious Disease of Indiana

🇺🇸

Indianapolis, Indiana, United States

Wake Forest University Health Sciences

🇺🇸

Winston-Salem, North Carolina, United States

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