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A Trial to Evaluate the Efficacy, Durability, and Safety of KSI-301 Compared to Aflibercept in Participants With Diabetic Macular Edema (DME)

Phase 3
Terminated
Conditions
Diabetic Macular Edema
Interventions
Other: Sham Procedure
Registration Number
NCT04611152
Lead Sponsor
Kodiak Sciences Inc
Brief Summary

This Phase 3 study will evaluate the efficacy, durability, and safety of KSI-301 compared to aflibercept in participants with treatment-naïve DME.

Detailed Description

This is a Phase 3, prospective, randomized, double-masked, two-arm, multi-center non-inferiority study evaluating the efficacy and safety of repeated intravitreal dosing of KSI-301 5 mg in participants with treatment-naïve DME.

The primary endpoint will be assessed at Year 1; additional secondary endpoints for efficacy will be assessed at Years 1 and 2.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
460
Inclusion Criteria
  1. Signed informed consent prior to participation in the study.
  2. Treatment-naïve diabetic macular edema, with vision loss and center involvement (if present) diagnosed within 9 months of screening.
  3. BCVA ETDRS letter score between 78 and 25 (-20/25 to 20/320 Snellen equivalent), inclusive, in the Study Eye.
  4. CST of ≥ 320 microns on SD-OCT (Heidelberg Spectralis or equivalent on other OCT instruments) as determined by the Reading Center.
  5. Decrease in vision determined by the Investigator to be primarily the result of DME.
  6. Type 1 or Type 2 diabetes mellitus and a HbA1c of ≤12%.
  7. Other protocol-specified inclusion criteria may apply.
Exclusion Criteria
  1. Macular edema in the Study Eye considered to be secondary to a cause other than DME.
  2. Active iris or angle neovascularization or neovascular glaucoma in the Study Eye.
  3. High-risk proliferative diabetic retinopathy characteristics in the Study Eye.
  4. History of Pan-retinal Photocoagulation (PRP) laser in the Study Eye within 3 months of screening.
  5. Tractional retinal detachment in the Study Eye.
  6. Active retinal disease other than the condition under investigation in the Study Eye.
  7. Any history or evidence of a concurrent ocular condition present, that in the opinion of the Investigator could require either medical or surgical intervention or affect macular edema or alter visual acuity during the study (e.g., vitreomacular traction, epiretinal membrane).
  8. Active or suspected ocular or periocular infection or inflammation in either eye at Day 1.
  9. Any prior use of an approved or investigational treatment for DME in the Study Eye (e.g., anti-VEGF, intraocular or periocular steroids, macular laser photocoagulation).
  10. Women who are pregnant or lactating or intending to become pregnant during the study.
  11. Uncontrolled blood pressure defined as a systolic value ≥ 180 mmHg or diastolic value ≥100 mmHg while at rest.
  12. Recent history (within the 6 months prior to screening) of myocardial infarction, stroke, transient ischemic attack, acute congestive heart failure or any acute coronary event.
  13. History of a medical condition that, in the judgment of the Investigator, would preclude scheduled study visits, completion of the study, or a safe administration of investigational product.
  14. Other protocol-specified exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
KSI-301 (Arm A)KSI-301Intravitreal injection of KSI-301 (5 mg) once every 4 weeks for 3 monthly doses followed by an individualized dosing regimen (every 8 to 24 weeks) via intravitreal injection from Week 16 to Week 100.
KSI-301 (Arm A)Sham ProcedureIntravitreal injection of KSI-301 (5 mg) once every 4 weeks for 3 monthly doses followed by an individualized dosing regimen (every 8 to 24 weeks) via intravitreal injection from Week 16 to Week 100.
Aflibercept (Arm B)AfliberceptIntravitreal injection of aflibercept (2 mg) once every 4 weeks for 5 monthly doses followed by aflibercept (2 mg) once every 8 weeks via intravitreal injection from Week 24 to 100.
Aflibercept (Arm B)Sham ProcedureIntravitreal injection of aflibercept (2 mg) once every 4 weeks for 5 monthly doses followed by aflibercept (2 mg) once every 8 weeks via intravitreal injection from Week 24 to 100.
Primary Outcome Measures
NameTimeMethod
Mean Change in BCVADay 1 to Week 64

Mean change in best-corrected visual acuity (BCVA) from baseline to the average of Weeks 60 and 64 (using Early Treatment Diabetic Retinopathy Study (ETDRS) Letters). Best Corrected Visual Acuity (BCVA) was measured on the Early Treatment Diabetic Retinopathy Study (ETDRS) chart at a starting distance of 4 meters. The BCVA letter score ranges from 0 to 100 (best score), and a gain in BCVA letter score from baseline indicates an improvement in visual acuity.

Secondary Outcome Measures
NameTimeMethod
Percentage of Patients With a ≥ 2-step Worsening on the ETDRS DRSS in Study KS301P104Day 1 to Week 52

Percentage of patients with a ≥ 2-step worsening on the Early Treatment Diabetic Retinopathy Study (ETDRS) Diabetic Retinopathy Severity Scale (DRSS) from baseline at Week 52 using last observation carried forward (LOCF) in Study KS301P104. The Diabetic Retinopathy Disease Severity Scale (DRSS) may be used to describe overall retinopathy severity as well as the change in severity over time. Severity range from level 10 (DR absent) to level 85 (advanced proliferative DR: posterior fundus obscured, or center of macula detached).

Percentage of Patients in the KSI-301 Arm on a Q8W, Q12W, Q16W, Q20W, or Q24W Treatment IntervalWeek 56

Percentage of patients in the KSI-301 arm on a Q8W, Q12W, Q16W, Q20W, or Q24W treatment interval at the primary endpoint. Analyses include KSI-301 patients who completed a treatment interval from Week 56 onwards.

Mean Change in OCT CSTDay 1 to Week 64

Mean change in Optical Coherence Tomography (OCT) central subfield retinal thickness (CST) from baseline to the average of Weeks 60 and 64

Percentage of Patients With a ≥ 2-step Worsening on the ETDRS DRSS in Studies KS301P104 and KS301P105 CombinedDay 1 to Week 52

Percentage of patients with a ≥ 2-step worsening on the Early Treatment Diabetic Retinopathy Study (ETDRS) Diabetic Retinopathy Severity Scale (DRSS) from baseline at Week 52 using last observation carried forward (LOCF) in Studies KS301P104 and KS301P105 combined. The Diabetic Retinopathy Disease Severity Scale (DRSS) may be used to describe overall retinopathy severity as well as the change in severity over time. Severity range from level 10 (DR absent) to level 85 (advanced proliferative DR: posterior fundus obscured, or center of macula detached).

Mean Number of Intravitreal InjectionsDay 1 to Week 60

Mean number of intravitreal injections from Day 1 to Week 60

Trial Locations

Locations (75)

Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

🇺🇸

Torrance, California, United States

MidAtlantic Retina

🇺🇸

Philadelphia, Pennsylvania, United States

Ophthalmic Consultants of Boston

🇺🇸

Boston, Massachusetts, United States

Retina Consultants of Texas

🇺🇸

Houston, Texas, United States

Retina Consultants of San Antonio

🇺🇸

San Antonio, Texas, United States

Tennessee Retina PC

🇺🇸

Nashville, Tennessee, United States

Florida Retina Consultants

🇺🇸

Lakeland, Florida, United States

California Retina Consultants

🇺🇸

Santa Maria, California, United States

UCSD Jacobs Retina Center

🇺🇸

La Jolla, California, United States

Fakultna nemocnica Trencin

🇸🇰

Trencín, Slovakia

Hospital dos de Maig

🇪🇸

Barcelona, Spain

Center for Retina & Macular Disease

🇺🇸

Winter Haven, Florida, United States

Spokane Eye

🇺🇸

Spokane, Washington, United States

Fondazione PTV Policlinico Tor Vergata

🇮🇹

Roma, Italy

Emanuelli Research & Development Center LLC

🇵🇷

Arecibo, Puerto Rico

Dietrich Bonhoeffer Klinikum Neubrandenburg

🇩🇪

Neubrandenburg, Mecklenburg-Vorpommern, Germany

Pauls Stradins Clinical University Hospital

🇱🇻

Riga, Latvia

Fakultna nemocnica s poliklinikou Zilina

🇸🇰

Žilina, Slovakia

Ganglion Medical Center

🇭🇺

Pécs, Hungary

Black Hills Regional Eye Institute

🇺🇸

Rapid City, South Dakota, United States

Fakultna nemocnica s poliklinikou F. D. Roosevelta

🇸🇰

Banská Bystrica, Slovakia

Uvea Klinika, S.R.O.

🇸🇰

Martin, Slovakia

Jahn Ferenc Dél-Pesti Kórház és Rendelointézet

🇭🇺

Budapest, Hungary

St. Elisabeth Krankenhaus

🇩🇪

Köln, Nordrhein-Westfalen, Germany

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Spain

Signes Ozolinas Doctor Praxis In Ophthalmology

🇱🇻

Jelgava, Latvia

Riga Eastern Clinical University Hospital Clinic Bikernieki

🇱🇻

Riga, Latvia

Latvian American Eye Center

🇱🇻

Riga, Latvia

Univerzitna nemocnica Bratislava

🇸🇰

Bratislava, Slovakia

Universitätsklinikum Freiburg

🇩🇪

Freiburg, Baden-Württemberg, Germany

Hospital Clinico Universitario Lozano Blesa

🇪🇸

Zaragoza, Spain

Universitätsklinikum Regensburg

🇩🇪

Regensburg, Bayern, Germany

St Franziskus Hospital

🇩🇪

Münster, Nordrhein-Westfalen, Germany

Nemocnica s poliklinikou Trebisov a.s. Ocne oddelenie - jednonova zdravotna starostlivost

🇸🇰

Trebišov, Slovakia

Hospital Universitari General de Catalunya - Grupo Quironsalud

🇪🇸

Barcelona, Spain

Retina Northwest

🇺🇸

Portland, Oregon, United States

Hospital Universitario Puerta de Hierro - Majadahonda

🇪🇸

Madrid, Spain

Hospital Universitari i Politecnic La Fe de Valencia

🇪🇸

Valencia, Spain

Hospital Universitario Rio Hortega

🇪🇸

Valladolid, Spain

Hospital Universitario Miguel Servet

🇪🇸

Zaragoza, Spain

Retina Consultants of Southern California

🇺🇸

Redlands, California, United States

Conneticut Eye Consultants

🇺🇸

Danbury, Connecticut, United States

Colorado Retina Associates PC

🇺🇸

Lakewood, Colorado, United States

Retina Group of Florida

🇺🇸

Boca Raton, Florida, United States

Blue Ocean Clinical Research

🇺🇸

Clearwater, Florida, United States

Florida Eye Associates

🇺🇸

Melbourne, Florida, United States

Retina Specialty Institute

🇺🇸

Pensacola, Florida, United States

Springfield Clinic LLP

🇺🇸

Springfield, Illinois, United States

Wolfe Eye Clinic

🇺🇸

West Des Moines, Iowa, United States

Cumberland Valley Retina Consultants PC

🇺🇸

Hagerstown, Maryland, United States

Retina Associates PA

🇺🇸

Lenexa, Kansas, United States

Vitreo Retinal Consultants and Surgeons

🇺🇸

Wichita, Kansas, United States

The Retina Center of New Jersey

🇺🇸

Bloomfield, New Jersey, United States

Foundation for Vision Research

🇺🇸

Grand Rapids, Michigan, United States

NJ Retina

🇺🇸

Teaneck, New Jersey, United States

Charlotte Eye Ear Nose & Throat Associates, P.A.

🇺🇸

Charlotte, North Carolina, United States

Cascade Medical Research Institute

🇺🇸

Springfield, Oregon, United States

Retina Research of Beaufort

🇺🇸

Beaufort, South Carolina, United States

Pametto Retina Center

🇺🇸

Florence, South Carolina, United States

Charleston Neuroscience Institute

🇺🇸

Ladson, South Carolina, United States

Palmetto Retina Center

🇺🇸

West Columbia, South Carolina, United States

Charles Retina Institute

🇺🇸

Germantown, Tennessee, United States

Texas Retina Associates

🇺🇸

Arlington, Texas, United States

Southwest Retina Specialists

🇺🇸

Amarillo, Texas, United States

Star Retina

🇺🇸

Burleson, Texas, United States

Strategic Clinical Research Group, LLC

🇺🇸

Willow Park, Texas, United States

Florida Retina Institute

🇺🇸

Orlando, Florida, United States

Retina Associates of Florida

🇺🇸

Tampa, Florida, United States

Retina Vitreous Associates of Florida

🇺🇸

Tampa, Florida, United States

Charleston Neuroscience Institute - West Ashley

🇺🇸

Charleston, South Carolina, United States

Vitreo Retinal Associates

🇺🇸

Gainesville, Florida, United States

Retina Associates of Kentucky

🇺🇸

Lexington, Kentucky, United States

Austin Retina Associates

🇺🇸

Austin, Texas, United States

Piedmont Eye Center

🇺🇸

Lynchburg, Virginia, United States

Retina Center Northwest

🇺🇸

Silverdale, Washington, United States

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