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Phase 1 Study of OP-3136 in Advanced or Metastatic Solid Tumors

Phase 1
Recruiting
Conditions
Advanced or Metastatic ER+ HER2- Breast Cancer (mBC)
Advanced or Metastatic Non-Small Cell Lung Cancer (NSCLC)
Advanced or Metastatic Castration-Resistant Prostate Cancer (mCRPC)
Metastatic Breast Cancer
Fulvestrant
Palazestrant
Interventions
Registration Number
NCT06784193
Lead Sponsor
Olema Pharmaceuticals, Inc.
Brief Summary

This is a first-in-human, open-label, multicenter phase 1 study to evaluate safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD), and preliminary efficacy of OP-3136, a lysine acetyltransferases 6A and 6B (KAT6A/B) inhibitor, as monotherapy and in combination with other anticancer agents in participants with advanced solid tumors.

This study consists of 2 parts: a dose escalation part (Part 1) and dose expansion part (Part 2).

Detailed Description

Part 1A (Dose Escalation for OP-3136 Monotherapy): This part of the study will evaluate the safety, tolerability, and PK in a range of doses of OP-3136, a lysine acetyltransferases 6A and 6B (KAT6A/B) inhibitor, administered orally once daily to participants with ER+ HER2- advanced or metastatic breast cancer (mBC), advanced or metastatic castration resistant prostate cancer (mCRPC), or advanced or metastatic non-small cell lung cancer (mNSCLC), and determine the maximum tolerated dose (MTD) and the recommended dose/regimen for expansion (RDE).

Part 1B (Dose Escalation for OP-3136 in Combination with Fulvestrant): This part of the study will evaluate the safety and PK of OP-3136 administered in combination with fulvestrant in participants with ER+ HER2- mBC, and determine MTD and RDE for this combination.

Part 1C (Dose Escalation for OP-3136 in Combination with Palazestrant): This part of the study will evaluate the safety and PK of OP-3136 administered in combination with palazestrant in participants with ER+ HER2- mBC, and determine MTD and RDE for this combination.

Part 2A (Dose Expansion for OP-3136 Monotherapy): This part will evaluate two expansion cohorts at the monotherapy RDE from part 1 in participants with ER+ HER2- mBC and participants with mCRPC.

Part 2B (Dose Expansion for OP-3136 in Combination with Fulvestrant OR Palazestrant): This part will evaluate the RDEs for OP-3136 in combination with fulvestrant from Part 1B OR the RDEs of OP-3136 in combination with palazestrant in an expansion cohort in participants with ER+ HER2- mBC.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
180
Inclusion Criteria
  • Participants with advanced or metastatic ER+HER2- breast cancer, mCRPC, or NSCLC (Part 1) or advanced or metastatic ER+HER2- BC or mCRPC (Part 2).
  • Part 1A (Dose escalation for OP-3136 monotherapy): Participants must have a tumor that is unresectable or metastatic and for which life prolonging measures do not exist or available therapies are intolerable or no longer effective.
  • Part 1B (Dose escalation for OP-3136 in combination with fulvestrant): Participants with advanced or metastatic ER+ HER2- breast cancer that have progressed on or after at least 1 prior line of treatment that included endocrine therapy and CDK 4/6 inhibitor in advanced or metastatic setting and must have received no more than 2 prior lines of endocrine therapy (one of which must be in combination with CDK4/6 inhibitor) and no more than 1 prior line of chemotherapy or an antibody-drug conjugate in the advanced or metastatic setting.
  • Part 1C (Dose escalation for OP-3136 in combination with palazestrant): Participants with advanced or metastatic ER+ HER2- breast cancer that have progressed on or after at least 1 prior line of treatment that included endocrine therapy and CDK 4/6 inhibitor in advanced or metastatic setting and must have received no more than 2 prior lines of endocrine therapy (one of which must be in combination with CDK4/6 inhibitor) and no more than 1 prior line of chemotherapy or an antibody-drug conjugate in the advanced or metastatic setting.
  • Part 2A (Dose Expansion in ER+ HER2- mBC for OP-3136 monotherapy): Participants must have received up to 3 prior lines of endocrine therapy (one of which must be in combination with CDK4/6 inhibitor) and up to 1 prior line of chemotherapy or an antibody-drug conjugate.
  • Part 2A (Dose Expansion in mCRPC for OP-3136 monotherapy): Participants must have received up to 4 lines of prior systemic therapy for prostate cancer. Prior therapy must include treatment with an androgen receptor pathway inhibitor(s).
  • Part 2B (Dose Expansion in ER+ HER2- mBC for OP-3136 in combination with fulvestrant OR Dose Expansion in ER+ HER2- mBC for OP-3136 in combination with palazestrant): Participants must have progressed on or after at least 1 prior line of treatment that included endocrine therapy and CDK 4/6 inhibitor in advanced or metastatic setting. Participants must have received no more than 2 prior lines of endocrine therapy in the advanced or metastatic setting and no more than 1 prior line of chemotherapy or an antibody-drug conjugate in the advanced or metastatic setting.

Key

Exclusion Criteria
  • Prior therapy with KAT6A/B inhibitor in any treatment setting.
  • Participants with advanced/metastatic, symptomatic, visceral spread, that are at risk of life-threatening complications in the short term.
  • Known active or symptomatic central nervous system (CNS) metastases, carcinomatous meningitis, leptomeningeal disease, or a spinal cord compression that require CNS-specific treatment, or participants who did not demonstrate clinical and radiologic stability during the last 2 months prior to the first dose of study treatment or require or are currently on steroid therapy for CNS metastases.
  • History of cerebral vascular disease, including transient ischemic attack, within 6 months prior to the first dose of study treatment.
  • History of or ongoing impaired cardiac function or clinically significant cardiac disease within 6 months prior to the first dose of study treatment.

Note: Additional inclusion/exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Part 1A Dose Escalation monotherapyOP-3136-
Part 1B Dose Escalation in combination with fulvestrantFulvestrant-
Part 1B Dose Escalation in combination with fulvestrantOP-3136-
Part 2A Dose Expansion monotherapy - mCRPCOP-3136-
Part 2B Dose Expansion in combination with fulvestrant OR palazestrant-mBC @ RDE 1OP-3136-
Part 2B Dose Expansion in combination with fulvestrant OR palazestrant-mBC @ RDE 1Fulvestrant-
Part 2B Dose Expansion in combination with fulvestrant OR palazestrant-mBC @ RDE 1Palazestrant-
Part 1C Dose Escalation in combination with palazestrantOP-3136-
Part 1C Dose Escalation in combination with palazestrantPalazestrant-
Part 2A Dose Expansion monotherapy - mBCOP-3136-
Part 2B Dose Expansion in combination with fulvestrant OR palazestrant-mBC @ RDE 2OP-3136-
Part 2B Dose Expansion in combination with fulvestrant OR palazestrant-mBC @ RDE 2Fulvestrant-
Part 2B Dose Expansion in combination with fulvestrant OR palazestrant-mBC @ RDE 2Palazestrant-
Primary Outcome Measures
NameTimeMethod
Number of participants with dose-limiting toxicities in the Dose Escalation ArmsUp to 28 days
Incidence of adverse events and laboratory abnormalitiesUp to 26 months
Secondary Outcome Measures
NameTimeMethod
Maximum observed concentration (Cmax)Up to 26 months
Time to maximum concentration (Tmax)Up to 26 months
Area under the curve from time zero to 24 hours (AUC0-24)Up to 26 months
Duration of Response (DOR)Up to 26 months
Clinical Benefit Rate (CBR)Up to 26 months
Overall Response Rate (ORR)Up to 26 months

Trial Locations

Locations (8)

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Florida Cancer Specialists

🇺🇸

Sarasota, Florida, United States

University Medical Center - New Orleans

🇺🇸

New Orleans, Louisiana, United States

START - Midwest

🇺🇸

Grand Rapids, Michigan, United States

SCRI Oncology Partners

🇺🇸

Nashville, Tennessee, United States

START - San Antonio

🇺🇸

San Antonio, Texas, United States

START - Mountain Region

🇺🇸

West Valley City, Utah, United States

Cancer Research South Australia

🇦🇺

Adelaide, South Australia, Australia

Dana-Farber Cancer Institute
🇺🇸Boston, Massachusetts, United States

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