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Dose Individualization of Chemotherapy in Patients With Gastrointestinal Cancers Lacking a Specific Liver Enzyme

Phase 2
Recruiting
Conditions
Digestive Cancer
Colorectal Cancer
Interventions
Drug: FOLFOX regimen
Drug: CAPOX regimen
Registration Number
NCT06475352
Lead Sponsor
UNICANCER
Brief Summary

The goal of this clinical trial is to establish guidelines for fluoropyrimidine dose reduction according to uracilemia in patients with DPD deficiency in the treatment of digestive cancers. The main question it aims to answer is:

- Which reduction dose of fluoropyrimidine is needed for patient with DPD deficiency?

Participants will:

* Take the treatment with the reduction of dose stated by the protocol

* Visit the clinic once every 2-3 weeks for checkups and tests for collection of adverse events

Detailed Description

Multicenter phase II trial evaluating different strategies of pre-specified fluoropyrimidine-dose adjustment according to \[U\] in DPD-deficient patients with gastrointestinal cancer.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
400
Inclusion Criteria
  1. Patients with pre-treatment screening based on [U] value according to INCa/HAS recommendations.

  2. Eastern Cooperative Oncology Group performance status (ECOG PS) ≤2

  3. Fluoropyrimidine-naïve patients with gastrointestinal cancer starting chemotherapy combining fluoropyrimidine (5-FU or capecitabine) and oxaliplatin whatever the context (adjuvant, neoadjuvant, palliative) including the following regimens (the most frequently prescribed in gastrointestinal cancers):

    • biweekly 5-FU and oxaliplatin (FOLFOX) +/- targeted therapy (TT)
    • three-weekly capecitabine and oxaliplatin (CAPOX) +/- TT
  4. Age ≥ 18 years

  5. Patients eligible for full standard fluoropyrimidine and oxaliplatin doses regardless of DPD deficiency

  6. Adequate bone marrow function (cell blood count (CBC)), estimated glomerular filtration rate (DFG) ≥ 50 ml/min, alkaline phosphatase (ALP) / aspartate aminotransferase (ASAT) / alanine aminotransferase (ALAT) ≤ 5 upper limit of normal (ULN), and bilirubin ≤ 50 micromol/L

  7. Patient must have signed and dated a written informed consent form prior to any trial specific procedures. When the patient is physically unable to give their written consent, a trusted person of their choice, independent from the investigator or the sponsor, can confirm in writing the patient's consent.

  8. Women of childbearing potential must have a negative serum or urine pregnancy test.

  9. Patients must agree to remain abstinent or use contraceptive methods with a failure rate of < 1% per year for the duration of study treatment and within 6 months after completing treatment.

  10. Patients must be affiliated to a Social Security System (or equivalent).

  11. Patient is willing and able to comply with the protocol for the duration of the trial including undergoing treatment and scheduled visits, and examinations including follow-up.

Exclusion Criteria
  1. Patients with complete DPD deficiency based on [U] ≥150 ng/mL
  2. Any prior treatment including a fluoropyrimidine
  3. Patients with any contraindication to treatment with fluoropyrimidine or oxaliplatin regardless of DPD deficiency
  4. Patients not eligible for full standard dose fluoropyrimidine and oxaliplatin for clinical reasons including older age and/or comorbidity regardless of a DPD deficiency
  5. Patients unwilling or unable to comply with trial obligations for geographic, social, or physical reasons, or who are unable to understand the purpose and procedures of the trial
  6. Recent or concomitant treatment with brivudine
  7. Pregnant or breastfeeding woman.
  8. Participation in another therapeutic trial within 30 days prior to inclusion.
  9. Persons deprived of their liberty or under protective custody or guardianship.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Uracilemia [20-50[ - 25%FOLFOX regimenPatients with uracilemia between \[20-50\[ ng/mL will be randomized to receive a 25% fluoropyrimidine dose reduction
Uracilemia [50-100[FOLFOX regimenPatients with uracilemia between \[50-100\[ ng/mL will receive a 50% fluoropyrimidine dose reduction
Uracilemia [20-50[ - 25%CAPOX regimenPatients with uracilemia between \[20-50\[ ng/mL will be randomized to receive a 25% fluoropyrimidine dose reduction
Uracilemia [100-150[FOLFOX regimenPatients with uracilemia between \[100-150\[ ng/mL will receive a 75% fluoropyrimidine dose reduction
Uracilemia <16FOLFOX regimenPatient with uracilemia \<16 ng/mL will receive a full standard fluoropyrimidine dose
Uracilemia [16-20[FOLFOX regimenPatients with uracilemia between \[16-20\[ ng/mL will receive a full standard fluoropyrimidine dose -dose
Uracilemia [20-50[ - 50%CAPOX regimenPatients with uracilemia between \[20-50\[ ng/mL will be randomized to receive a 50% fluoropyrimidine dose reduction
Uracilemia [50-100[CAPOX regimenPatients with uracilemia between \[50-100\[ ng/mL will receive a 50% fluoropyrimidine dose reduction
Uracilemia <16CAPOX regimenPatient with uracilemia \<16 ng/mL will receive a full standard fluoropyrimidine dose
Uracilemia [16-20[CAPOX regimenPatients with uracilemia between \[16-20\[ ng/mL will receive a full standard fluoropyrimidine dose -dose
Uracilemia [20-50[ - 50%FOLFOX regimenPatients with uracilemia between \[20-50\[ ng/mL will be randomized to receive a 50% fluoropyrimidine dose reduction
Uracilemia [100-150[CAPOX regimenPatients with uracilemia between \[100-150\[ ng/mL will receive a 75% fluoropyrimidine dose reduction
Primary Outcome Measures
NameTimeMethod
Proportion of fluoropyrimidine-induced grade ≥ 3 haematological and gastrointestinal toxicity after 2 cyclesThroughout the two first cycles of treatment, up to 42 days

The National Cancer Institute-Common Terminology Criteria for Adverse Events version 5 (NCI-CTCAE v5) is widely accepted in the community of oncology research as the leading rating scale for adverse events. This scale, divided into 5 grades (1 = "mild", 2 = "moderate", 3 = "severe", 4 = "life-threatening", and 5 = "death") determined by the investigator, will make it possible to assess the severity of the disorders.

Secondary Outcome Measures
NameTimeMethod
Percentage of fluoropyrimidine dose modificationThroughout the four first cycles of treatment, up to 3 months

Percentage of patients for whom fluoropyrimidine dose is increased or decreased

Recommended fluoropyrimidine doseThroughout the four first cycles of treatment, up to 3 months

The rate of fluoropyrimidine induced grade ≥ 3 haematological and gastrointestinal toxicity in each uracilemia-based group of DPD-deficient patients (according to uracilemia level) compared to the rate observed in non DPD-deficient patients (control arm)

Description of fluoropyrimidine doseThroughout the four first cycles of treatment, up to 3 months

The cumulative dose (mg/m²) of chemotherapy delivered to patients will be recorded along with reasons of dose-modifications or treatment discontinuation for limiting toxicity

Fluoropyrimidine toxicity during the studyThroughout the four first cycles of treatment, up to 3 months

The National Cancer Institute-Common Terminology Criteria for Adverse Events version 5 (NCI-CTCAE v5) is widely accepted in the community of oncology research as the leading rating scale for adverse events. This scale, divided into 5 grades (1 = "mild", 2 = "moderate", 3 = "severe", 4 = "life-threatening", and 5 = "death") determined by the investigator, will make it possible to assess the severity of the disorders.

Disease-free survival (DFS) - Stage III Colon Cancer3 years

Disease-free survival is defined as the delay between date of inclusion and tumor relapse (local, regional, or distant) or death from any cause, whichever occurs first.

Overall survival (OS) - Stage III Colon CancerFrom randomization to death from any cause, up to 3 years.

The overall survival is the length of time from randomization that patients enrolled in the study are still alive.

Progression-free survival (PFS) - Stage IV Colon CancerFrom randomization to disease progression or death, up to 1 year.

The progression-free survival is the length of time during and after the treatment of a disease that a patient lives with the disease but it does not get worse.

Trial Locations

Locations (34)

CHU Amiens

🇫🇷

Amiens, France

Institut du Cancer Avignon Provence

🇫🇷

Avignon, France

CH Aunay Bayeux

🇫🇷

Bayeux, France

CH Cote Basque

🇫🇷

Bayonne, France

CHU Besançon

🇫🇷

Besançon, France

Centre François Baclesse

🇫🇷

Caen, France

Polyclinique du Parc - Centre d'Oncologie Maurice Tubiana

🇫🇷

Caen, France

Hopital Privé Drome-Ardeche

🇫🇷

Guilherand-Granges, France

CHU Clermont Ferrand

🇫🇷

Clermont-Ferrand, France

Hopital Beaujon

🇫🇷

Clichy, France

Hopital Henri Mondor

🇫🇷

Créteil, France

CHU Dijon

🇫🇷

Dijon, France

GH Mutualiste de Grenoble

🇫🇷

Grenoble, France

CHU Dupuytren

🇫🇷

Limoges, France

Hopital Privé Jean Mermoz

🇫🇷

Lyon, France

Centre Léon Bérard

🇫🇷

Lyon, France

Grand Hopital de l'Est Francilien

🇫🇷

Meaux, France

Hopital Nord Franche Comté - Site du Mittan

🇫🇷

Montbéliard, France

Centre Antoine Lacassagne

🇫🇷

Nice, France

CHU d'Orléans

🇫🇷

Orléans, France

Institut Curie

🇫🇷

Paris, France

Hopital Saint Louis

🇫🇷

Paris, France

Hopital Saint Antoine

🇫🇷

Paris, France

GH Diaconesses Croix St Simon

🇫🇷

Paris, France

CHU Bordeaux

🇫🇷

Pessac, France

Hospices Civiles de Lyon

🇫🇷

Pierre-Bénite, France

CHU Poitiers

🇫🇷

Poitiers, France

Hopital Robert Debré

🇫🇷

Reims, France

Institut Jean Godinot

🇫🇷

Reims, France

CH de Saint Malo

🇫🇷

Saint-Malo, France

Institut du Cancer de Strasbourg

🇫🇷

Strasbourg, France

CHU de Toulouse

🇫🇷

Toulouse, France

Hopital Bretonneau

🇫🇷

Tours, France

Gustave Roussy Cancer Campus

🇫🇷

Villejuif, France

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