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Injection Site Tolerability, Safety, Pharmacokinetics and Pharmacodynamics Study After a Single Dose Subcutaneous Treatment of Alirocumab SAR236553 (REGN727)

Phase 1
Completed
Conditions
Hypercholesterolemia
Interventions
Registration Number
NCT01448239
Lead Sponsor
Sanofi
Brief Summary

Primary Objective:

Injection Site Tolerability

Secondary Objectives:

* To assess the safety profile of alirocumab SAR236553 (REGN727)

* To assess the pharmacokinetic-pharmacodynamic relationship of alirocumab SAR236553 (REGN727)

Detailed Description

The total duration of study for each subject is up to 15 weeks including a screening period up to 3 weeks.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
24
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
alirocumab SAR236553 (REGN727) - Dose Balirocumab SAR236553 (REGN727)A single subcutaneous injection of Dose B
alirocumab SAR236553 (REGN727) - Dose Aalirocumab SAR236553 (REGN727)A single subcutaneous injection of Dose A
Primary Outcome Measures
NameTimeMethod
Pain using present pain intensity (PPI) verbal questionnaire6 weeks
Erythema at injection site by measuring diameter and qualitative assessment6 weeks
Edema at injection site by measuring diameter and qualitative assessment6 weeks
Secondary Outcome Measures
NameTimeMethod
Number of participants with Adverse EventsUp to 12 weeks
Assessment of PK parameter - time to maximum concentration (tmax)Up to 12 weeks
Assessment of PK parameter - maximum concentration (Cmax)Up to 12 weeks
Assessment of PK parameter - area under curve (AUC)Up to 12 weeks
Assessment of PK parameter - cluster of differentiation (CD) biomarker (CD29)Up to 12 weeks
Assessment of PK parameter - terminal elimination half-life (t1/2z)Up to 12 weeks
Pharmacodynamics: Change in LDL-C from baselineUp to 12 weeks

Trial Locations

Locations (1)

Sanofi-Aventis Administrative Office

🇺🇸

Bridgewater, New Jersey, United States

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