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A Study Evaluating Megestrol Acetate Modulation in Hormone Receptor Positive Advanced Breast Cancer

Registration Number
NCT03024580
Lead Sponsor
Instituto Nacional de Cancer, Brazil
Brief Summary

This pilot trial evaluates in vivo megestrol acetate (MA) modulation of steroidal receptors in advanced breast cancer.

Detailed Description

Progesterone receptor (PR) expression has been considered a biomarker of oestrogen receptor-α (ERα) activity. This longstanding relationship has been recently challenged and instead of being merely an ERα-induced gene target, PR may be a critical determinant of ERα activity. The functional significance of this steroid receptor crosstalk is regulation of a gene expression program associated with low tumorigenicity; hence, better disease outcome. Genomic alterations in the PR genomic locus seem to be a relatively common mechanism for reduction of PR expression, which may consequently lead to altered ERα chromatin binding and target gene expression patterns that increase breast tumorigenicity and confers a poor clinical outcome. This ERα-PR crosstalk may be directly influenced by many variables, including the relative receptor levels and the hormonal milieu.

ER-positive advanced breast cancer is a heterogeneous group of diseases with considerable variability in outcome to a range of treatments. Prior response predicts the likelihood of subsequent benefit from another endocrine agent and this should be taken into account in the treatment decision process when assessing whether to prescribe a subsequent endocrine therapy. Despite the enormous progress made regarding the elucidation of breast cancer subgroups and their molecular drivers, most information comes from primary tumors. MA lacks cross-resistance and is active after acquired resistance to potent AI. This pilot trial evaluates in vivo MA modulation of steroidal receptors in advanced breast cancer.

Recruitment & Eligibility

Status
UNKNOWN
Sex
Female
Target Recruitment
20
Inclusion Criteria
  • Metastatic breast cancer with ER and/or PR positive (primary tumor)
  • Metastatic site amenable to biopsy
Exclusion Criteria
  • Platelet count below 100,000 / mm3
  • Renal or hepatic impairment
  • Coagulation disorder

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Megestrol acetateMegestrol Acetate 160Mg TabletMegestrol acetate 160 mg PO daily until disease progression or unacceptable toxicity Tumor biopsy and blood collection before treatment initiation and at the time of disease progression.
AnastrozoleAnastrozole 1Mg TabletAnastrozole 1 mg PO daily until disease progression or unacceptable toxicity Tumor biopsy and blood collection before treatment initiation and at the time of disease progression.
LetrozoleLetrozole 2.5Mg TabletLetrozole 2.5 mg PO daily until disease progression or unacceptable toxicity Tumor biopsy and blood collection before treatment initiation and at the time of disease progression.
ExemestaneExemestane 25 MGExemestane 25 mg PO daily until disease progression or unacceptable toxicity Tumor biopsy and blood collection before treatment initiation and at the time of disease progression.
FulvestrantFulvestrant 50Mg Solution for InjectionFulvestrant 500 mg intramuscularly (IM) d1, d14, d28 and q28 days until disease progression or unacceptable toxicity Tumor biopsy and blood collection before treatment initiation and at the time of disease progression.
TamoxifenTamoxifen 20Mg TabletTamoxifen 20 mg PO daily until disease progression or unacceptable toxicity Tumor biopsy and blood collection before treatment initiation and at the time of disease progression.
Primary Outcome Measures
NameTimeMethod
Progression free survivalFrom date of randomization until disease progression or death due to any cause, assessed up to 18 months

From date of randomization until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 18 months

Secondary Outcome Measures
NameTimeMethod
Overall survivalFrom date of randomization until death, assessed up to 18 months

From date of randomization until the date of death from any cause, assessed up to 18 months

Clinical benefitPartial response and stable disease for more than 24 weeks, assessed up to 18 months

Partial response and stable disease for more than 24 weeks, as per RECIST criteria, from date of randomization until the date of first documented progression or date of death, whichever came first, assessed up to 18 months

Trial Locations

Locations (1)

Hospital do Cancer III

🇧🇷

Rio de Janeiro, Brazil

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