MedPath

A randomized double blind placebo controlled ascending dose study to evaluate the effect of APL180 on endothelial function in patients with familial hypercholesterolemia

Phase 2
Conditions
atherosclerosis
familial hypercholesterolemia
10003216
Registration Number
NL-OMON32563
Lead Sponsor
ovartis
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Pending
Sex
Not specified
Target Recruitment
20
Inclusion Criteria

Familial hypercholesterolemia
age 18-50 yrs
informed consent
BMI 18-30 kg/m2

Exclusion Criteria

smoking
previous cardiovascular event
diabetes
acute inflammatory disease
anti-inflammatory medication
ECG abnormalities

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>change in endothelial function, assessed as acetylcholine-induced vasodilation<br /><br>in the forearm</p><br>
Secondary Outcome Measures
NameTimeMethod
<p>1. side effects<br /><br>2. APL180 concentration<br /><br>3. in vitro HDL quality</p><br>
© Copyright 2025. All Rights Reserved by MedPath