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Study of Standardized Withaferin-A for the treatment of Steroid Refractory acute Graft versus Host Disease.

Phase 2
Conditions
Health Condition 1: D898- Other specified disorders involving the immune mechanism, not elsewhere classified
Registration Number
CTRI/2023/07/055361
Lead Sponsor
Tata Memorial Centre
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Yet Recruiting
Sex
Not specified
Target Recruitment
0
Inclusion Criteria

1.Patients age = 12 years with a hematological malignancy who have undergone allogeneic stem cell transplant with matched related donor (MRD), haploidentical (Haplo) donor or matched unrelated donor (MUD).

2.Evidence of myeloid engraftment (eg, absolute neutrophil count =0.5 × 109 /l for 3 consecutive days).

3.Ecog performance score of 0 or 1.

4.Patients with steroid-refractory acute graft versus host disease (GVHD), defined as any of the following:

i.Patients with progressive GVHD (ie, increase in stage in any organ system or any new organ involvement) after 3 days of primary treatment with methylprednisolone =2 mg/kg/d (or equivalent).

ii.Patients with GVHD that has not improved (ie, decrease in stage in at least 1 involved organ system) after 7 days of primary treatment with methylprednisolone =2 mg/kg/d (or equivalent).

iii.Patients who previously began corticosteroid therapy at a lower dose (=1 mg/kg/d methylprednisolone) for treatment of skin GVHD or skin GVHD accompanied by upper gut GVHD but develop new GVHD in another organ system.

iv.Patients who cannot tolerate a corticosteroid taper, that is, begin corticosteroids at 2.0 mg/kg/d, demonstrate response, but progress before a 50% decrease from the initial starting dose of corticosteroids is achieved.

Exclusion Criteria

1.Known hypersensitivity or contraindications against Withaferin A.

2.Presence of an active uncontrolled infection defined as hemodynamic instability attributable to sepsis or new symptoms, worsening physical signs, or radiographic findings attributable to infection.

3.Any medical or psychiatric illness which precludes the participant from giving informed consent.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
THE OBJECTIVE RESPONSE RATE (ORR)Timepoint: AT DAY 28 FROM THE START OF STANDARDIZED WITHAFERIN A (SWA)
Secondary Outcome Measures
NameTimeMethod
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