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Sickle Cell Outcome REsearch

Recruiting
Conditions
Sickel cell Anemia
Sickle cell Disease
10018902
10005330
Registration Number
NL-OMON55241
Lead Sponsor
Erasmus MC, Universitair Medisch Centrum Rotterdam
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Not specified
Target Recruitment
1000
Inclusion Criteria

- A diagnosis of SCD of any genotype;
- Written patient (and in case of a patient <16 years of age, parental)
informed consent.

Exclusion Criteria

- Any medical or social reason, which obstructs or inhibits study participation
according to treating physician
- Intrekking van (ouderlijke) toestemming

Study & Design

Study Type
Observational invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>1. To describe the natural course of disease e.g. symptoms and complications,<br /><br>growth, psychosocial and neurocognitive development, socioeconomic and<br /><br>demographic characteristics of children and adults with SCD;<br /><br>2. To identify (molecular) genetic and epigenetic, biological, demographic and<br /><br>psychological and therapeutic determinants for morbidity and mortality in<br /><br>children and adults with SCD;<br /><br>3. To investigate the long-term effects of current and future therapies on SCD<br /><br>symptoms and complications, preservation of organ function, growth,<br /><br>psychosocial and neurocognitive development in children and adults with SCD.<br /><br>4. To evaluate and improve aspects of care of children and adults with SCD by<br /><br>measurement of patient-reported outcomes (PROs) and patient reported<br /><br>experiences (PREs) and analyses of associations with health care outcome. </p><br>
Secondary Outcome Measures
NameTimeMethod
<p>Not applicable.</p><br>
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