MedPath

A Study of Belimumab in Subjects With Systemic Lupus Erythematosus (SLE)

Phase 3
Completed
Conditions
Systemic Lupus Erythematosus
Interventions
Registration Number
NCT00424476
Lead Sponsor
Human Genome Sciences Inc.
Brief Summary

The purpose of this study is to evaluate the efficacy, safety, tolerability, and impact on quality of life of two different doses of belimumab administered in addition to standard therapy in subjects with active, autoantibody-positive systemic lupus erythematosus (SLE) disease.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
865
Inclusion Criteria
  • Clinical diagnosis of SLE by ACR criteria.
  • Active SLE disease.
  • Autoantibody-positive.
  • On stable SLE treatment regimen.

Key

Exclusion Criteria
  • Pregnant or nursing
  • Have received treatment with any B cell targeted therapy.
  • Have received treatment with a biological investigational agent in the past year.
  • Have received IV cyclophosphamide within 180 days of Day 0.
  • Have severe lupus kidney disease.
  • Have active central nervous system (CNS) lupus.
  • Have required management of acute or chronic infections within the past 60 days.
  • Have current drug or alcohol abuse or dependence.
  • Have a historically positive test or test positive at screening for HIV, hepatitis B, or hepatitis C.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Belimumab 10 mg/kgBelimumab 10 mg/kgBelimumab 10 mg/kg
PlaceboPlaceboPlacebo
Belimumab 1 mg/kgBelimumab 1 mg/kgBelimumab 1 mg/kg
Primary Outcome Measures
NameTimeMethod
SLE Responder Index (SRI) Response Rate at Week 52Baseline, 52 weeks

Percentage of subjects with a ≥ 4 point reduction from baseline in SELENA SLEDAI score, and no worsening (increase of \< 0.30 points from baseline) in PGA, and no new BILAG A organ domain score or 2 new BILAG B organ domain scores compared with baseline.

SELENA SLEDAI is calculated from 24 individual descriptors; 0 indicates inactive disease and the maximum theoretical score is 105; scores \> 20 are rare. PGA is a visual analog scale scored from 0 to 3 (1=mild, 2=moderate, 3=severe). BILAG uses a single score for each of the 8 organ domains; range is from severe to no disease (A to E).

Secondary Outcome Measures
NameTimeMethod
Mean Change in Physician's Global Assessment (PGA) at Wk 24.Baseline, 24 weeks

The PGA is a visual analog scale scored from 0 to 3. A score of 1 corresponds to mild lupus disease activity. A score of 2 correlates with moderate disease activity and a score of 3 with severe disease activity.

Percent of Subjects Whose Average Prednisone Dose Has Been Reduced by ≥ 25% From Baseline to ≤ 7.5 mg/Day During Weeks 40 Through 52Baseline, Weeks 40 through 52
Percent of Subjects With a ≥ 4 Point Reduction From Baseline in SELENA SLEDAI Score at Wk 52.Baseline, 52 weeks
Mean Change From Baseline in Medical Outcomes 36-Item Short Form Health Survey (SF-36) Physical Component Summary Score (PCS) at Wk 24.Baseline, 24 weeks

The SF-36 is a generic health related quality of life (HRQOL) measurement. The survey includes 36 questions grouped to 8 domains and 2 summary measures (physical and mental health component, PCS and MCS, respectively) assessing HRQOL. Responses are scored according to the SF-36v2™ manual. A score is calculated for each SF-36 domain based on the patient's response to each question within it. This is then transformed to a scale ranging from 0 (worst) to 100 (best) points. The PCS is norm-based where the mean=50 and standard deviation (SD)=10. Higher scores represent better physical health.

Trial Locations

Locations (92)

CAICI, Instituto Centralizado de Asistencia e Investigación Clínica Integral

🇦🇷

Rosario, Argentina

Fundación Instituto de Reumatología Fernando Chalem

🇨🇴

Bogota, Colombia

Centrode de Investigaciones en Reumatologia Especialidades Medicas (CIREEH)

🇨🇴

Bogotá, Colombia

Davao Medical Center

🇵🇭

Davao City, Philippines

University of Santo Tomas Hospital

🇵🇭

Manila City, Philippines

University of Perpetual Help -Rizal

🇵🇭

Las Pinas City, Philippines

St. Petersburg City Hospital (Rheumatology Center)

🇷🇺

St. Petersburg, Russian Federation

Buddhist Tzu Chi General Hospital, Dalin

🇨🇳

Chia-Yi, Taiwan

Kaohsiung Veterans General Hospital

🇨🇳

Kaohsiung, Taiwan

Chang Gung Memorial Hospital, Linko

🇨🇳

Tau-Yuan County, Taiwan

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Taichung Veterans General Hospital

🇨🇳

Taichung, Taiwan

St.-Petersburg Region Clinical Hospital

🇷🇺

St.-Petersburg, Russian Federation

City Healthcare Institution Municipal Hospital NPZ,

🇷🇺

Yaroslavl, Russian Federation

Buddhist Tzu Chi General Hospital - Hualien

🇨🇳

Haulien, Taiwan

Hospital Interzonal General San Martín

🇦🇷

La Plata, Argentina

Spitalul Clinic Dr. Ion Cantacuzino

🇷🇴

Bucharest, Romania

Chang Gung Memorial Hospital, Kaosiung

🇨🇳

Kaosiung, Taiwan

Chung Shan Medical University Hospital

🇨🇳

Taichung, Taiwan

Spitalul Clinic Colentina

🇷🇴

Bucharest, Romania

State Institution Scientific Research Institute of Rheumatology

🇷🇺

Moscow, Russian Federation

Spitalul de Urgenta al Ministerului Administratiei si Internelor Prof. Dr. Dimitrie Gerota

🇷🇴

Bucharest, Romania

Spitalul Clinic Judetean de Urgenta Cluj-Napoca

🇷🇴

Cluj Napoca, Romania

Academy of Post-Graduated Education

🇷🇺

St.-Petersburg, Russian Federation

Soloviev's City Clinical Hospital,

🇷🇺

Yaroslavl, Russian Federation

Chung-Ho Memorial Hospital, Kaohsiung Medical University

🇨🇳

Kaohsiung, Taiwan

China Medical University Hospital

🇨🇳

Taichung, Taiwan

Chang Gung Memorial Hospital-Keelung

🇨🇳

Keelung, Taiwan

Hospital Sirio Libanes

🇦🇷

Buenos Aires, Argentina

Hospital Britanico de Buenos Aires

🇦🇷

Buenos Aires, Argentina

Centro Privado de Medicina Familiar

🇦🇷

Buenos Aires, Argentina

Atencion Integral en Reumatologia

🇦🇷

Buenos Aires, Argentina

Instituto de Investigaciones Medicas

🇦🇷

Buenos Aires, Argentina

OMI, Organización Médica de Investigación

🇦🇷

Ciudad Autonoma de Buenos Aires, Argentina

Repatriation Hospital

🇦🇺

Daw Park, Australia

CIER, Centro de Investigaciones en Enfermedades Reumáticas

🇦🇷

Ciudad Autonoma de Buenos Aires, Argentina

Hospital General de Agudos Carlos G. Durand

🇦🇷

Ciudad Autonoma de Buenos Aires, Argentina

Centro Medico Privado de Reumatologia

🇦🇷

San Miguel de Tucuman, Argentina

Emeritus Research, Cabrini Hospital

🇦🇺

Melbourne, Australia

Monash Medical Centre

🇦🇺

Melbourne, Australia

Hospital de Clínicas - UNICAMP

🇧🇷

Campinas, Brazil

Royal Perth Hospital

🇦🇺

Shenton Park, Australia

Hospital das Clínicas - Universidade do Paraná

🇧🇷

Curitiba, Brazil

Hospital de Clínicas - Universidade Federal de Pernambuco

🇧🇷

Fortaleza, Brazil

Hospital Geral de Goiânia

🇧🇷

Goiânia, Brazil

Hospital Universitário Pedro Ernesto - UERJ

🇧🇷

Rio de Janeiro, Brazil

Hospital Unversitario Clementino Fraga Filho UFRJ

🇧🇷

Rio de Janeiro, Brazil

Hospital São Lucas da PUC-RS

🇧🇷

Porto Alegre, Brazil

Hospital Abreu Sodré

🇧🇷

São Paulo, Brazil

Hospital do Servidor Público Estadual de São Paulo - Francisco Morato de Oliveira

🇧🇷

São Paulo, Brazil

Hospital Heliópolis

🇧🇷

São Paulo, Brazil

Clínica Dávila

🇨🇱

Santiago, Chile

Hospital Dr. Sotero del Rio

🇨🇱

Santiago, Chile

Pontificia Universidad Católica de Chile

🇨🇱

Santiago, Chile

Hospital Dr. Gustavo Fricke

🇨🇱

Viña del Mar, Chile

Office of Dr. Guzman

🇨🇴

Bogota, Cundinamarca, Colombia

Fundación Oftalmologica de Santander Clinica Carlos Ardila Lulle

🇨🇴

Bucaramanga, Santander, Colombia

Centro de Reumatologia y Ortopedia

🇨🇴

Barranquilla, Colombia

Riesgo de Fracturas

🇨🇴

Bogotá, Colombia

SERVIMED

🇨🇴

Bucaramanga, Colombia

Office of Dr. Jose Molina

🇨🇴

Medellín, Colombia

Corporación para Investigaciones Biológicas (CIB)

🇨🇴

Medellín, Colombia

St. John's Medical College Hospital

🇮🇳

Bangalore, India

Krishna Institute of Medical Sciences

🇮🇳

Hyderabaad, India

Apollo Hospitals

🇮🇳

Hyderabad, India

Nizam's Institute of Medical Sciences

🇮🇳

Hyderabaad, India

Chhatrapati Shahuji Maharaj Medical University

🇮🇳

Lucknow, India

King Edward Memorial (K.E.M.) Hospital

🇮🇳

Mumbai, India

Kerala Institute of Medical Sciences

🇮🇳

Trivandrum, India

Kyungpook National Univesity Hospital

🇰🇷

Daegu, Korea, Republic of

Eulji University Hospital

🇰🇷

Daejeon, Korea, Republic of

Inha University Hospital

🇰🇷

Inchon, Korea, Republic of

Dong-A University Hospital 3-1 (Dept. Rhuematology)

🇰🇷

Pusan, Korea, Republic of

Pusan National University Hospital

🇰🇷

Pusan, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

The Hospital for Rheumatic Diseases, Hanyang University Hospital

🇰🇷

Seoul, Korea, Republic of

Catholic University, Yoido St. Mary's Hospital

🇰🇷

Seoul, Korea, Republic of

Ajou University Hospital

🇰🇷

Suwon, Korea, Republic of

Hospital Nacional Alberto Sabogal Sologuren ESSALUD

🇵🇪

Lima, Peru

Clinica Ricardo Palma Anexo 9 - Javier Prado Este

🇵🇪

Lima, Peru

Chong Hua Hospital

🇵🇭

Cebu City, Philippines

Hospital Nacional Guillermo Almenara Irigoyen ESSALUD

🇵🇪

Lima, Peru

Instituto de Ginecología y Reproducción

🇵🇪

Lima, Peru

Philippine General Hospital

🇵🇭

Manila City, Philippines

St. Luke's Medical Center

🇵🇭

Quezon City, Philippines

Spitalul Clinic Sf Maria

🇷🇴

Bucharest, Romania

Hospital Universitário - Universidade Federal de Juiz de Fora

🇧🇷

Juiz de Fora, Brazil

Hospital Santa Izabel

🇧🇷

Salvador, Brazil

Catholic Universtigy of Korea, Kangnam St. Mary's Hospital

🇰🇷

Seoul, Korea, Republic of

Tuen Mun Hospital

🇭🇰

Tuen Mun, Hong Kong

Pamela Youde Nethersole Eastern Hospital

🇭🇰

Chai Wan, Hong Kong

Rheumatology Assessment and Treatment Center, Pok Oi Hospital

🇭🇰

Shatin, Hong Kong

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