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A 24-week Study Evaluating the Effectiveness and Safety of Lucentis® 0.2mg in Retinopathy of Prematurity Participants in China

Completed
Conditions
Retinopathy of Prematurity
Interventions
Other: Ranibizumab
Registration Number
NCT05576792
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

This is a 24-week, multicenter, open-label, single-arm, observational, post approval commitment study, which is designed to collect effectiveness, safety and other clinical information of intravitreal ranibizumab 0.2 mg for the treatment of Retinopathy of Prematurity (ROP) participants in a real world clinical setting in mainland China.

Detailed Description

Eligible participants treated according to local routine clinical practice will be enrolled in the study upon signing an Informed Consent.

Participants will enter the study when they receive their first treatment and are followed up for 24 weeks. During the follow up period, participants could receive post-baseline treatment (i.e., ranibizumab or laser therapy) Patients will be treated according to the approved label and standard of care and as per Investigator judgement.

End of study will be defined as completion of the week 24 visit or premature withdrawal visit

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
62
Inclusion Criteria
  1. Signed informed consent from parent(s) or legal guardian(s), in compliance with local requirements

  2. Male or female preterm infants with a birth weight of less than 1500 g

  3. Bilateral ROP with 1 of the following retinal findings in each eye:

    • Zone I, stage 1+, 2+, 3 or 3+ disease, or
    • Zone II, stage 3+ disease, or
    • A-ROP
Exclusion Criteria
  1. Have a history of hypersensitivity (either the patient or the mother) to ranibizumab or any component of the ranibizumab formulation or to drugs of similar chemical classes
  2. Have been previously exposed to any intravitreal or systemic anti-VEGF agent (either the patient or the mother during this child's pregnancy)
  3. Have used (either the patient or the mother) other investigational drugs as part of another clinical study (other than vitamins and minerals) within 30 days or within 5 half-lives of the other investigational drug, whichever is longer
  4. Have received any previous surgical or nonsurgical treatment for ROP (e.g., ablative laser therapy or cryotherapy, vitrectomy)
  5. Participants who have contraindications according to locally approved ranibizumab label

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
ranibizumab 0.2 mgRanibizumabIntravitreal ranibizumab 0.2 mg for the treatment of ROP
Primary Outcome Measures
NameTimeMethod
Number of participants with absence of active Retinopathy of Prematurity (ROP) and absence of unfavorable structural outcomes in both eyes during the observational period after starting study treatment.Week 24

To achieve this outcome, participants cannot fulfill any of the following criteria:

* Require intervention for ROP in either eye at or before the 24week assessment visit with a treatment modality other than ranibizumab

* Have active ROP in either eye at the 24week assessment visit

* Have unfavorable structural outcomes in either eye at or before 24-week assessment visit

Secondary Outcome Measures
NameTimeMethod
Incidence of AEsUp to 24 weeks

Incidence of AEs will be collected

Assessment of weightBaseline, Week 12, and Week 24

For the assessment of weight the participant should be wearing minimal clothing (e.g., a clean diaper). Body weight to the nearest gram will be measured using an electronic scale.

Assessment of head circumferenceBaseline, Week 12, and Week 24

For the assessment of head circumference the participant should be wearing minimal clothing (e.g., a clean diaper). The maximum occipitofrontal head circumference in centimeters will be measured using a tape measure.

Full retinal vascularization in 12 clock hoursWeek 24

Full retinal vascularization in 12 clock hours at the 24-week assessment to evaluate fundus features of ranibizumab 0.2 mg in the treatment of ROP

Assessment of lengthBaseline, Week 12, and Week 24

For the assessment of length the participant should be wearing minimal clothing (e.g., a clean diaper). Recumbent length in centimeters will be measured using an infantometer or according to local clinical practice.

Assessment of lower leg lengthBaseline, Week 12, and Week 24

For the assessment of lower leg length the participant should be wearing minimal clothing (e.g., a clean diaper).The lower leg length (knee-heel length) will be measured to the nearest 0.1 centimeter using a sliding caliper or according to local clinical practice. Measurements should always be done on the right side, unless a physical deformity affects the right side.

Time to intervention with a second modality for ROP or development of unfavorable structural outcomeUp to 24 weeks

Time to intervention with a second modality for ROP or development of unfavorable structural outcome will be collected

Proportion of participants with re-treatment of ROP receiving any post-baseline intervention24 weeks

Proportion of participants with re-treatment of ROP receiving any post-baseline intervention at or before 24 weeks

number of ranibizumab administrations needed in the treatment of participants with ROP24 weeks

number of ranibizumab administrations needed in the treatment of participants with ROP will be collected

Trial Locations

Locations (1)

Novartis Investigative Site

🇨🇳

Guangzhou, Guangdong, China

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