Expanded Access to Velmanase Alfa
- Conditions
- Alpha-Mannosidosis
- Registration Number
- NCT04959240
- Lead Sponsor
- Chiesi Farmaceutici S.p.A.
- Brief Summary
Individual patient expanded access requests may be considered for patients who have no other treatment options.
- Detailed Description
Expanded access may provide access for treatment prior to approval by the local regulatory agency.
Recruitment & Eligibility
- Status
- AVAILABLE
- Sex
- Not specified
- Target Recruitment
- Not specified
Inclusion Criteria
Exclusion Criteria
Study & Design
- Study Type
- EXPANDED_ACCESS
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method