MedPath

A Multicenter Phase 3, Open-Label Study of Bosutinib Versus Imatinib in Adult Patients With Newly Diagnosed Chronic Phase Chronic Myelogenous Leukemia

Phase 3
Completed
Conditions
Leukemia, Myelogenous, Chronic, Breakpoint Cluster Region-Abelson Proto-oncogene (BCR-ABL) Positive
Interventions
Registration Number
NCT02130557
Lead Sponsor
Pfizer
Brief Summary

Phase 3, 2-arm, randomized, open label trial. Patients will be randomized to receive bosutinib or imatinib for the duration of the study.

Detailed Description

The study will be open for enrollment until the planned number of approximately 500 Philadelphia Chromosome Positive (Ph+) patients have been randomized (approximately 250 Ph+ patients in each treatment arm; a total of approximately 530 Ph+ and Ph- patients). All patients will be treated and/or followed for approximately 5 years (240 weeks) after randomization until the study has closed. Patients who discontinue study therapy early due to disease progression or intolerance to study medication will continue to be followed yearly for survival for up to approximately 5 years (240 weeks) after randomization.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
536
Inclusion Criteria
  1. Molecular diagnosis of CP CML of ≤ 6 months (from initial diagnosis).
  2. Adequate hepatic, renal and pancreatic function.
  3. Age ≥ 18 years.
Exclusion Criteria
  1. Any prior medical treatment for CML, including tyrosine kinase inhibitors (TKIs), with the exception of hydroxyurea and/or anagrelide treatment, which are permitted for up to 6 months prior to study entry (signature of ICF) if suitably approved for use in the subject's region.
  2. Any past or current Central Nervous System (CNS) involvement, including leptomeningeal leukemia.
  3. Extramedullary disease only.
  4. Major surgery or radiotherapy within 14 days of randomization.
  5. History of clinically significant or uncontrolled cardiac disease.
  6. Known seropositivity to human immunodeficiency virus (HIV), current acute or chronic hepatitis B (hepatitis B surface-antigen positive), hepatitis C, cirrhosis or evidence of decompensated liver disease. Patients with resolved Hepatitis B can be included.
  7. Recent or ongoing clinically significant GI disorder, e.g. Crohn's Disease, Ulcerative Colitis, or prior total or partial gastrectomy.
  8. History of another malignancy within 5 years with the exception of basal cell carcinoma or cervical carcinoma in situ or stage 1 or 2 cancer that is considered adequately treated and currently in complete remission for at least l2 months.
  9. Current, or recent (within 30 days, or 5 half-lives of investigational product) participation in other clinical trials of investigational agents and/or containing interventional procedures deemed contrary to the objectives and conduct of this trial.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
ImatinibImatinibImatinib, 400 mg, oral administration once a day
BosutinibBosutinibBosutinib, 400 mg, oral administration once a day
Primary Outcome Measures
NameTimeMethod
Percentage of Participants With Major Molecular Response (MMR) at Month 12Month 12

MMR was defined as a ratio of breakpoint cluster region to abelson (BCR-ABL/ABL) less than or equal to (\<=) 0.1 percent (%) on the international scale (IS) (greater than or equal to \[\>=\] 3 log reduction from standardized baseline in ratio of BCR-ABL to ABL transcripts \[\>=3000 ABL required\]) by quantitative reverse transcriptase polymerase chain reaction (RT-qPCR). The percentage of participants with MMR at Month 12 are reported.

Secondary Outcome Measures
NameTimeMethod
Kaplan-Meier Estimate of Probability of Retaining Complete Cytogenetic Response (CCyR) at Month 48Month 48

The Kaplan-Meier curve was generated based on the first date of CCyR until the date of the confirmed loss of CCyR or censoring, objectively documented, for responders only. Confirmed loss of CCyR was the presence of at least one Ph+ metaphase confirmed by a second assessment at least 28 days later. Treatment discontinuation due to suboptimal response/treatment failure, PD or death due to PD within 28 days of last dose were considered confirmed loss of CCyR. PD was defined as disease progression to AP or BP CML.

Percentage of Participants With Complete Cytogenetic Response (CCyR) Up to Month 12Up to Month 12

Complete Cytogenetic Response (CCyR) was based on the prevalence of Ph+ metaphases among cells in metaphase on a bone marrow (BM) aspirate. CCyR was achieved when there was 0% Ph+ metaphases among cells in a BM sample when at least 20 metaphases from a BM sample were analyzed, or MMR if no BM was available. The percentage of participants with CCyR for up to Month 12 are reported.

Kaplan-Meier Estimate of Probability of Retaining Major Molecular Response (MMR) at Month 48Month 48

The Kaplan-Meier curve was generated based on the first date of MMR until the date of the confirmed loss of MMR or censoring, objectively documented, for responders only. Confirmed loss of MMR was BCR-ABL/ABL IS ratio \>0.1% in association with a \>=5-fold increase in BCR-ABL/ABL IS ratio from the lowest value achieved up to that time-point confirmed by a second assessment at least 28 days later. Treatment discontinuation due to suboptimal response/treatment failure, progressive disease (PD) or death due to PD within 28 days of last dose were considered confirmed loss of MMR. PD was defined as disease progression to accelerated phase (AP) or blast phase (BP) CML.

Cumulative Incidence of Event Free Survival (EFS) EventsUp to Month 60

EFS was defined as time from randomization to death due to any cause, transformation to AP or BP at any time, confirmed loss of complete hematologic response (CHR), confirmed loss of CCyR or censoring. Loss of CHR was defined as a hematologic assessment of non-CHR (chronic phase, AP, or BP) confirmed by 2 assessments at least 4 weeks apart. Loss of CHR was defined as appearance of any of the following: WBC count that rises to \>20.0\*10\^9/L, platelet count rises to \>=600\*10\^9/L, appearance of palpable spleen or other extramedullary involvement proven by biopsy, appearance of 5% myelocytes in peripheral blood, appearance of blasts or promyelocytes in peripheral blood. Loss of CCyR was defined as at least 1 Ph+ metaphase from analysis of \<100 metaphases confirmed by follow up cytogenetic analysis after 1 month. Cumulative incidence of EFS was defined as percentage of participants with EFS event at Month 60 and was adjusted for competing risk of treatment discontinuation without event.

Overall Survival (OS) RateUp to Month 60

OS was defined as the time (in months) from randomization to the occurrence of death due to any cause or censoring. Kaplan-meier analysis was used for determination of OS. Percentage of participants who were alive were estimated in this outcome measure.

Percentage of Participants With Major Molecular Response (MMR) Up to Month 18Up to Month 18

MMR was defined as a ratio of BCR-ABL/ABL \<=0.1% on the international scale (\>=3 log reduction from standardized baseline in ratio of BCR-ABL to ABL transcripts \[\>=3000 ABL required\]) by quantitative RT-qPCR. The percentage of participants with MMR for up to Month 18 are reported.

Trial Locations

Locations (182)

Pacific Cancer Medical Center, Inc.

🇺🇸

Anaheim, California, United States

The Emory Clinic

🇺🇸

Atlanta, Georgia, United States

Winship Cancer Institute, Emory University

🇺🇸

Atlanta, Georgia, United States

Kaiser Permanente Hawaii

🇺🇸

Honolulu, Hawaii, United States

Saint Alphonsus Regional Medical Center, Cancer Care Center

🇺🇸

Boise, Idaho, United States

Saint Alphonsus Regional Medical Center

🇺🇸

Boise, Idaho, United States

University of Illinois Cancer Center

🇺🇸

Chicago, Illinois, United States

John H. Stroger, Jr. Hospital of Cook County

🇺🇸

Chicago, Illinois, United States

Lafayette General Medical Center

🇺🇸

Lafayette, Louisiana, United States

University of Massachusetts Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

St. Joseph Mercy-Canton

🇺🇸

Canton, Michigan, United States

Chelsea Community Hospital

🇺🇸

Chelsea, Michigan, United States

St. John Hospital&Medical Center-Van Elslander Cancer Center

🇺🇸

Grosse Pointe Woods, Michigan, United States

Minnesota Oncology Hematology, PA

🇺🇸

Edina, Minnesota, United States

Van Elslander Cancer Center, Pharmacy

🇺🇸

Grosse Pointe Woods, Michigan, United States

Park Nicollet Frauenshuh Cancer center

🇺🇸

Saint Louis Park, Minnesota, United States

Lakeview Hospital

🇺🇸

Stillwater, Minnesota, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

North Mississippi Medical Center Hematology and Oncology Clinic

🇺🇸

Tupelo, Mississippi, United States

John Theurer Cancer Center at Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

San Juan Oncology Associates

🇺🇸

Farmington, New Mexico, United States

NYU Winthrop Hospital - Oncology / Hematology department

🇺🇸

Mineola, New York, United States

NYU Winthrop Hospital - Pharmacy Department

🇺🇸

Mineola, New York, United States

Beth Israel Medical Center

🇺🇸

New York, New York, United States

University of Rochester Investigational Drug Pharmacy

🇺🇸

Rochester, New York, United States

FirstHealth Moore Regional Hospital

🇺🇸

Pinehurst, North Carolina, United States

FirstHealth Outpatient Cancer Center

🇺🇸

Pinehurst, North Carolina, United States

MUSC University Hospital

🇺🇸

Charleston, South Carolina, United States

UC Health Physicians Office South,

🇺🇸

West Chester, Ohio, United States

MUSC-Hollings Cancer Center

🇺🇸

Charleston, South Carolina, United States

GHS Cancer Institute

🇺🇸

Spartanburg, South Carolina, United States

HSHS St. Vincent Hospital Regional Cancer Center at HSHS St. Vincent Hospital

🇺🇸

Green Bay, Wisconsin, United States

HSHS St. Vincent Hospital Regional Cancer Center at HSHS St. Mary's Hospital Medical Center

🇺🇸

Green Bay, Wisconsin, United States

St George Hospital - Hematology Department

🇦🇺

Kogarah, New South Wales, Australia

UZ Ghent (University Hospital Ghent)

🇧🇪

Ghent, Belgium

Juravinski Cancer Centre

🇨🇦

Hamilton, Ontario, Canada

Lakeridge Health

🇨🇦

Oshawa, Ontario, Canada

Princess Margaret Cancer Centre

🇨🇦

Toronto, Ontario, Canada

Hopital Maisonneuve-Rosemont

🇨🇦

Montreal, Quebec, Canada

Saskatoon Cancer Centre

🇨🇦

Saskatoon, Saskatchewan, Canada

CHU de Québec - Université Laval

🇨🇦

Quebec, Canada

Fakultní Nemocnice Brno

🇨🇿

Brno, Czechia

Fakultní Nemocnice Hradec Králové

🇨🇿

Hradec Králové, Czechia

Fakultní nemocnice Olomouc

🇨🇿

Olomouc, Czechia

Aalborg University Hospital

🇩🇰

Aalborg, Denmark

Aarhus University Hospital

🇩🇰

Aarhus, Denmark

Institut Bergonié

🇫🇷

Bordeaux, France

Všeobecná fakultní Nemocnice v Praze

🇨🇿

Prague, Czechia

Oncologie Centre de Radiotherapie

🇫🇷

Strasbourg, NC, France

private Practice of Pr Philippe Rousselot

🇫🇷

Le Chesnay, France

Akademiska Hospital

🇸🇪

Uppsala, Sweden

private Practice of Dr. Viviane Dubruille

🇫🇷

Nantes cedex 1, France

INSERM CIC 1402 - CHU Poitiers

🇫🇷

Poitiers, France

Hôpital L'Archet 1-CHU Nice

🇫🇷

Nice, France

Institut de Cancérologie du Gard - Hématologie Clinique

🇫🇷

Nimes, France

Pr Mauricette Michallet Centre Hospitalier Lyon Sud

🇫🇷

Pierre Bénite, France

Universitätsklinikum Bonn

🇩🇪

Bonn, RP, Germany

Institut Universitaire du Cancer de Toulouse - Oncopole

🇫🇷

Toulouse cedex 9, France

Uniklinikum Aachen

🇩🇪

Aachen, Germany

Charité, CVK, Med. Klinik m.S Hämatologie und Onkologie

🇩🇪

Berlin, Germany

Universitätsklinikum Hamburg-Eppendorf, Onkologisches Zentrum

🇩🇪

Hamburg, Germany

Universitätsklinikum Freiburg, Klinik für Innere Medizin I

🇩🇪

Freiburg, Germany

Universitätsklinikum Jena, Klinik für Innere Medizin II

🇩🇪

Jena Lobeda-Ost, Germany

Schwerpunktpraxis für Hämatologie und Onkologie

🇩🇪

Magdeburg, Germany

Semmelweis Egyetem I. Belgyógyászat

🇭🇺

Budapest, Hungary

Debreceni Egyetem Klinikai Központ, Belgyógyászati Inézet Hematológiai Tanszék

🇭🇺

Debrecen, Hungary

Szegedi Tudományegyetem, AOK, Szent-Györgyi Albert Klinikai Központ, II. sz.

🇭🇺

Szeged, Hungary

Jász-Nagykun-Szolnok Megyei Hetényi, Géza Kórház-Rendelőintézet

🇭🇺

Szolnok, Hungary

Hematology Department, Rambam Medical Centre

🇮🇱

Haifa, Israel

Hematology Div. Davidoff Cancer Center, Rabin Medical Center

🇮🇱

Petah-Tikva, Israel

Azienda Ospedaliero-Universitaria "Policlinico - Vittorio Emanuele" - P.O. G. Rodolico

🇮🇹

Catania, CT, Italy

USC Ematologia, A. O. Papa Giovanni XXIII

🇮🇹

Bergamo, Italy

Dipartimento di ematologia

🇮🇹

Reggio Calabria, Italy

Policlinico S. Orsola - Malpighi,

🇮🇹

Bologna, Italy

Azienda Ospedaliero Universitaria Careggi

🇮🇹

Firenze, Italy

Istituto Scientifico San Raffaele

🇮🇹

Milano, Italy

IRCCS - AOU San Martino_IST, Ematologia 1

🇮🇹

Genova, Italy

A.O.U. Policlinico Università degli Studi di Napoli "Federico II"

🇮🇹

Napoli, Italy

Unità di Ricerca Clinica, U.O. Ematologia Adulti

🇮🇹

Monza, Italy

ASL Roma 2 - Ospedale Sant'Eugenio

🇮🇹

Roma, Italy

Hallym University Sacred Heart Hospital

🇰🇷

Anyang-si, Korea, Republic of

Dong A University Hospital

🇰🇷

Busan, Korea, Republic of

Keimyung University Dongsan Hospital

🇰🇷

Daegu, Korea, Republic of

Chonbuk National University Hospital

🇰🇷

Jeonju, Korea, Republic of

Kangbuk Samsung Hospital

🇰🇷

Seoul, Korea, Republic of

Seoul St. Mary's Hospital of the Catholic University of Korea

🇰🇷

Seoul, Korea, Republic of

Hospital Angeles del Pedregal (S.A. de C.V.)

🇲🇽

Mexico City, DF, Mexico

Monterrey International Research Center

🇲🇽

Monterrey, Nuevo LEON, Mexico

Klinische Farrnacologie en Apotheek

🇳🇱

Amsterdam, Noord-holland, Netherlands

Haukeland University Hospital Department of Hematology

🇳🇴

Bergen, Norway

Klinika Hematologii i Transplantologii Uniwersyteckie Centrum Kliniczne

🇵🇱

Gdansk, Pomorskie, Poland

Universytet Medyczny im. Piastów Śląskich we Wrocławiu Katedra i

🇵🇱

Wrocław, Poland

SPSK, Klinika Hematoonkologii i Transplantacji Szpiku w Lublinie

🇵🇱

Lublin, Poland

Univerzitná Nemocnica Bratislava-Nemocnica sv. Cyrila a Metoda

🇸🇰

Bratislava, Slovakia

Department of Medical Oncology, University of Pretoria and Steve Biko

🇿🇦

Pretoria, Gauteng, South Africa

The Medical Oncology Centre of Rosebank

🇿🇦

Johannesburg, Gauteng, South Africa

Department of Haematology

🇬🇧

Cardiff, United Kingdom

Groenkloof Life hospital.

🇿🇦

Pretoria, Gauteng, South Africa

Hospital Universitario La Princesa

🇪🇸

Madrid, Málaga, Spain

Hospital Vall d'Hebron

🇪🇸

Barcelona, Spain

Hospital Clínic

🇪🇸

Barcelona, Spain

Hospital Universitario Gregorio Marañón

🇪🇸

Madrid, Spain

Hospital Ramón y Cajal

🇪🇸

Madrid, Spain

Hospital Clinico San Carlos

🇪🇸

Madrid, Spain

Hospital Virgen de la Salud

🇪🇸

Toledo, Spain

Hospital Universitario de Salamanca

🇪🇸

Salamanca, Spain

Hospital Clínico Universitario de Valencia

🇪🇸

Valencia, Spain

Linköping University Hospital

🇸🇪

Linköping, Sweden

Skåne University Hospital

🇸🇪

Lund, Sweden

Karolinska University Hospital Solna

🇸🇪

Stockholm, Sweden

Norrlands University Hospital

🇸🇪

Umeå, Sweden

China Medical University Hospital

🇨🇳

Taichung city, R.o.c., Taiwan

Chi-Mei Medical Center

🇨🇳

Tainan City, R.o.c., Taiwan

Division of Hematology, Department of Internal Medicine, Maharaj Nakorn Chiang Mai Hospital

🇹🇭

Muang, Chiang MAI, Thailand

King Chulalongkorn Memorial Hospital

🇹🇭

Bangkok, Thailand

Division of Hematology, Department of Medicine, Faculty of Medicine Siriraj Hospital

🇹🇭

Bangkok, Thailand

MI "Cherkasy Regional Oncological Dispensary " of Cherkasy Regional Council

🇺🇦

Cherkasy, Ukraine

State Institution "National research center for radiation medicine of NAMS of Ukraine",

🇺🇦

Kyiv, Ukraine

State Institution "National research center for radiation medicine of NAMS of Ukraine"

🇺🇦

Kyiv, Ukraine

Kyiv City Clinical Hospital #9, Hematology department #1,

🇺🇦

Kyiv, Ukraine

transplantation department of hemotology and transplantology division within Clinical Radiology

🇺🇦

Kyiv, Ukraine

State Institution "Institute of Blood Pathology and Transfusion Medicine NAMS of Ukraine"

🇺🇦

Lviv, Ukraine

Catherine Lewis Centre, Hammersmith Hospital

🇬🇧

London, Greater London, United Kingdom

Chair of internal medicine #2.

🇺🇦

Kyiv, Ukraine

Linda McCartney Centre

🇬🇧

Liverpool, Merseyside, United Kingdom

Department of Clinical Haematology

🇬🇧

Nottingham, Nottinghamshire, United Kingdom

Heartlands Hospital

🇬🇧

Birmingham, WEST Midlands, United Kingdom

Cancer & Haematology Centre, Churchill Hospital

🇬🇧

Oxford, Oxfordshire, United Kingdom

Department of Haematology The Royal Hallamshire Hospital

🇬🇧

Sheffield, South Yorkshire, United Kingdom

St James's Institute of Oncology

🇬🇧

Leeds, WEST Yorkshire, United Kingdom

The Hope Clinical Trials Facility

🇬🇧

Leicester, United Kingdom

Indiana Blood and Marrow Transplantation

🇺🇸

Indianapolis, Indiana, United States

PHARMACY Department Franciscan St. Francis Health ATTN:Jill Leslie, Pharm D

🇺🇸

Indianapolis, Indiana, United States

The University of Texas, MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Virginia Mason Medical Center

🇺🇸

Seattle, Washington, United States

Seattle Cancer Care Alliance

🇺🇸

Seattle, Washington, United States

University of Cincinnati Medical Center

🇺🇸

Cincinnati, Ohio, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Roskilde Hospital

🇩🇰

Roskilde, Denmark

A.O. Brozu - P.O. Armando Businco

🇮🇹

Cagliari, Italy

University Health Shreveport

🇺🇸

Shreveport, Louisiana, United States

Saint Alphonsus Caldwell Cancer Care Center

🇺🇸

Caldwell, Idaho, United States

Saint Alphonsus Medical Center Nampa

🇺🇸

Nampa, Idaho, United States

LSU Health Sciences Center-Shreveport

🇺🇸

Shreveport, Louisiana, United States

Emory University Hospital

🇺🇸

Atlanta, Georgia, United States

Department of Haematology at UZ Leuven (7 th Floor)

🇧🇪

Leuven, Belgium

Singapore General Hospital

🇸🇬

Singapore, Singapore

Cancer Center of Acadiana at Lafayette General Medical Center

🇺🇸

Lafayette, Louisiana, United States

Helsinki University Central Hospital

🇫🇮

Helsinki, Finland

National University Hospital, Main Building

🇸🇬

Singapore, Singapore

University of Massachusetts Memorial Medical Center, ONC/Research Pharmacy

🇺🇸

Worcester, Massachusetts, United States

MUSC University of South Carolina, Investigational Drug Services

🇺🇸

Charleston, South Carolina, United States

Eastern Clinical Research Unit, Level 2

🇦🇺

Box Hill, Victoria, Australia

Horizon Health Network - The Moncton Hospital

🇨🇦

Moncton, New Brunswick, Canada

Nebraska Methodist Hospital

🇺🇸

Omaha, Nebraska, United States

Hematology Department CHR Verviers

🇧🇪

Verviers, Belgium

St. Joseph Mercy-Brighton

🇺🇸

Brighton, Michigan, United States

Hematology Department of CHU de Liège

🇧🇪

Liège, Belgium

HSHS St. Vincent Hospital

🇺🇸

Green Bay, Wisconsin, United States

Samodzielny Publiczny Szpital Kliniczny im. A Mielęckiego, ŚUM w Katowicach

🇵🇱

Katowice, Poland

Petz Aladár Megyei OktatóKórház, II. Belgyógyászati Osztály és Haematológiai Részleg

🇭🇺

Györ, Hungary

VU University Medical Center

🇳🇱

Amsterdam, Noord Holland, Netherlands

SPZOZ ZSM w Chorzowie Oddzial Hematologiczny

🇵🇱

Chorzow, Poland

Somogy Megyei Kaposi Mór Oktató Kórház

🇭🇺

Kaposvár, Hungary

St. Olavs Hospital

🇳🇴

Trondheim, Norway

Szpital Uniwersytecki w Krakowie, Oddział Kliniczny Hematologii

🇵🇱

Kraków, Poland

Wojewódzki Szpital Specjalistyczny im M. Kopernika, Klinika Hematologii Uniwersytetu Medycznego

🇵🇱

Łódź, Poland

Tan Tock Seng Hospital

🇸🇬

Singapore, Singapore

Khmelnytskyi Regional Hospital, Hematology Department

🇺🇦

Khmelnytskyi, Ukraine

Hospital (Universitari(o)) Germans Trias i Pujol

🇪🇸

Badalona, Barcelona, Spain

Mackay Memorial Hospital

🇨🇳

Taipei City, R.o.c., Taiwan

Phramongkutklao Hospital

🇹🇭

Bangkok, Thailand

Regional Clinical Hospital in Ivano-Frankivsk, Hematology Department

🇺🇦

Ivano-Frankivsk, Ukraine

Kaohsiung Medical University Chung-Ho Memorial Hospital

🇨🇳

Kaohsiung City, Taiwan

Rcca Md Llc

🇺🇸

Bethesda, Maryland, United States

St. John Hospital&Medical Center

🇺🇸

Detroit, Michigan, United States

Huntsman Cancer Hospital

🇺🇸

Salt Lake City, Utah, United States

St. Joseph Mercy Hospital - Inpatient Pharmacy

🇺🇸

Ann Arbor, Michigan, United States

Utah Cancer Specialists

🇺🇸

Salt Lake City, Utah, United States

Froedtert Hospital and the Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

St. Joseph Mercy Hospital

🇺🇸

Ann Arbor, Michigan, United States

Huntsman Cancer Institute

🇺🇸

Salt Lake City, Utah, United States

© Copyright 2025. All Rights Reserved by MedPath