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Dysport® Pediatric Lower Limb Spasticity Study

Phase 3
Completed
Conditions
Muscle Spasticity
Children
Cerebral Palsy
Interventions
Biological: Botulinum toxin type A
Drug: Placebo
Registration Number
NCT01249417
Lead Sponsor
Ipsen
Brief Summary

The purpose of this research study is to determine whether Dysport® is effective in the treatment of increased stiffness of the calf muscles and to evaluate the safety of this treatment in children with Cerebral Palsy. In addition this study will also check whether Dysport® can lessen the pain caused by spasticity and improve the child's wellbeing.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
241
Inclusion Criteria
  • Children aged 2 to 17 years with cerebral palsy
  • Equinus foot position
  • Ambulatory
  • Intensity of muscle tone equal to or greater than 2 in affected lower limb, as measured on the Modified Ashworth Scale
Exclusion Criteria
  • Fixed contracture
  • Previous phenol, alcohol injection or surgical intervention
  • Other neurological / neuromuscular disorder
  • Severe athetoid or dystonic movements

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Dysport 10 U/KgBotulinum toxin type A10 U/Kg per lower limb. Either one or both lower limbs can be treated. Total volume injected, 2ml per leg.
Dysport 15 U/KgBotulinum toxin type A15 U/Kg per lower limb. Either one or both lower limbs can be treated. Total volume injected, 2ml per leg.
PlaceboPlaceboTotal volume to be injected per lower limb - 2ml. Either one or both lower limbs can be treated.
Primary Outcome Measures
NameTimeMethod
Change in MAS Score in the Gastrocnemius-soleus Complex (GSC) at the Ankle Joint of the (Most) Affected Lower LimbChange from baseline to Week 4

The MAS is a 6-point scale which measures the intensity of muscle tone by measuring the resistance of the muscle to passive lengthening or stretching. Investigator will grade muscle tone in the GSC from 0 (no increase in tone) to 4 (affected parts rigid in flexion or extension).

Secondary Outcome Measures
NameTimeMethod
Goal Attainment Scale (GAS) ScoreWeek 4

GAS is a functional scale used to measure progress towards individual therapy goals. Individual goals defined for each subject by the physician, and the child's parents (caregiver) where applicable, prior to treatment. Post-baseline, the GAS for each goal rated using a defined scale (-2: Much less than expected outcome, -1: somewhat less than expected outcome, 0: expected outcome, 1: somewhat more than expected outcome, and 2: Much more than expected outcome).

Physician's Global Assessment (PGA) of the Treatment Response.Week 4

PGA Scale of the Treatment Response: Global assessment of treatment response assessed by asking the Investigator the following question: "how would you rate the response to treatment in the subject's lower limb(s) since the last injection?" Answers will be made on a 9 point rating scale (-4: markedly worse, -3: much worse, -2: worse, -1: slightly worse, 0: no change, +1: slightly improved, +2: improved, +3: much improved, +4: markedly improved).

Trial Locations

Locations (29)

Texas Scottish Rite - Hospital for Children

🇺🇸

Dallas, Texas, United States

Children's Hospital of Michigan

🇺🇸

Detroit, Michigan, United States

Centro de Rehabilitacion Integral de Queretaro (CRIQ)

🇲🇽

Queretaro, Mexico

Non-public Healthcare Unit at the Association for Disabled People KROK PO KROKU

🇵🇱

Gdansk, Poland

Hospital San José Celaya

🇲🇽

Celaya, Mexico

Neurorehabilitation Laboratory, Pontifical Catholic University

🇨🇱

Santiago, Chile

Hospital Central Dr Ignacio Morones Prieto

🇲🇽

San Luis Potosi, Mexico

Dr Roberto Del Rio Hospital

🇨🇱

Santiago, Chile

Centro de Rehabilitacion Infantil

🇲🇽

Mexico City, Mexico

The Children's Hospital

🇺🇸

Aurora, Colorado, United States

Rehabilitation Institute of Chicago

🇺🇸

Chicago, Illinois, United States

Gillette Children's Speciality Healthcare

🇺🇸

Saint Paul, Minnesota, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Children's Hospital New Orleans

🇺🇸

New Orleans, Louisiana, United States

Club De Leones Cruz Del Sur Rehabilitation Corporation, Punta Arenas

🇨🇱

Punta Arenas, Chile

Shriner's Hospital for Children

🇺🇸

Portland, Oregon, United States

CHU Jean Minjoz

🇫🇷

Besancon, France

B i L- Specjalistyczne Centrum Medyczne

🇵🇱

Lodz, Poland

Non-public Healthcare Unit - Grunwaldzka Clinic

🇵🇱

Poznan, Poland

Ghulane Military Medical Academy and School of Medicine

🇹🇷

Ankara, Turkey

Non-public Healthcare Unit Mazovian Neurorehabilitatio

🇵🇱

Wiazowna, Poland

Ibn-i-Sina Hospital

🇹🇷

Ankara, Turkey

Yildirim Beyazit Training and Research Hospital

🇹🇷

Ankara, Turkey

GATA Haydarpasa Training Hospital

🇹🇷

Istanbul, Turkey

Istanbul Fizik Tedavi Rehabilitasyon Egitim ve Arastirma Hastanesi

🇹🇷

Istanbul, Turkey

Istanbul University Medical School

🇹🇷

Istanbul, Turkey

Dokuz Eylül University Medical Faculty

🇹🇷

Izmir, Turkey

Istanbul Fizik Tedavi Rehabilitasyon

🇹🇷

Istanbul, Turkey

Kocaeli University Medical Faculty

🇹🇷

Izmit, Turkey

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