Clinical Phase II Study of hematopoietic stem ctell transplantation for ataxia telangiectasia and related diseases
Not Applicable
Recruiting
- Conditions
- ataxia telangiectasia DNA damage response disorder
- Registration Number
- JPRN-UMIN000019532
- Lead Sponsor
- Graduate Schoool, Dept. of Community Pediatrics, Perinatal and Maternal Medicine, Tokyo Medical and Dental University
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Recruiting
- Sex
- All
- Target Recruitment
- 5
Inclusion Criteria
Not provided
Exclusion Criteria
multiple organs failure intra cranial hemorrhage heart failure renal failure uncontrolled infection uncontrolled diabetes lever cirrhosis serious psychological problem
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method overall survival for 1 year
- Secondary Outcome Measures
Name Time Method percentage of adverse effect