MedPath

LUX-Breast 1: BIBW 2992 (Afatinib) in HER2-positive Metastatic Breast Cancer Patients After One Prior Herceptin Treatment

Phase 3
Completed
Conditions
Breast Neoplasms
Interventions
Registration Number
NCT01125566
Lead Sponsor
Boehringer Ingelheim
Brief Summary

To investigate the efficacy and safety of BIBW 2992 in combination with vinorelbine i.v. chemotherapy as treatment in patients with HER2-overexpressing, metastatic breast cancer, who failed one prior trastuzumab (Herceptin®) treatment

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
508
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm A: BIBW 2992 with vinorelbineBIBW 2992patients receive BIBW 2992 tablets once daily combined with weekly intravenous infusion of vinorelbine
Arm B: trastuzumab with vinorelbinevinorelbinepatients receive weekly intravenous infusion of trastuzumab and vinorelbine
Arm B: trastuzumab with vinorelbinetrastuzumabpatients receive weekly intravenous infusion of trastuzumab and vinorelbine
Arm A: BIBW 2992 with vinorelbinevinorelbinepatients receive BIBW 2992 tablets once daily combined with weekly intravenous infusion of vinorelbine
Primary Outcome Measures
NameTimeMethod
Progression-free Survival (PFS)From randomization (07Sep2010) until disease progression, death or data cut-off (08Jun2013); Up to 34 months

PFS is defined as time from randomisation to disease progression or death whichever occurs first. Assessed by investigator according to the Response Evaluation Criteria in Solid Tumours (RECIST 1.1). RECIST is a set of published rules that define when tumors in cancer patients improve ("respond"), stay the same ("stabilize") or worsen ("progress") during treatment.

Only data collected until the cut-off date for RECIST 1.1 based endpoints (08Jun2013) were considered.

Progression of disease was determined if at least 1 of the following criteria applied:

* At least a 20% increase in the sum of the diameters (SoD) of target lesions taking as reference the smallest SoD recorded since the treatment started, together with an absolute increase in the SoD of at least 5 mm

* Appearance of 1 or more new lesions

* Unequivocal progression of existing non-target lesions

Secondary Outcome Measures
NameTimeMethod
Overall Survival (OS)From randomisation (07Sep2010) to database lock (30Jul2018), up to 95 months.

OS is defined as time from randomisation to death irrespective of the cause of the death.

For patients who had not died up to the cut-off date (03Sep2013), the date they were last known to be alive was derived from the patient status records, the trial completion record, radiological imaging assessments, the study treatment termination record, and the randomisation date.

Best RECIST AssessmentFrom randomization (07Sep2010) until disease progression, death or data cut-off (08Jun2013); Up to 34 months

Best RECIST assessment is defined as CR, PR, stable disease (SD), progressive disease (PD) or not evaluable by investigator (RECIST version 1.1).

CR for target lesions (TL): Disappearance of all target lesions.

CR for non-target lesions (NTL): Disappearance of all non-target lesions and normalization of tumour marker level. All lymph nodes must be non-pathological in size (\<10mm short axis).

PR: At least a 30% decrease in the sum of diameters (SoD) of target lesions taking as reference the baseline sum diameters.

SD: Neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD, taking as references the smallest SoD while on study.

PD: At least a 20% increase in the SoD of target lesions, taking as references the smallest sum on study (this includes the baseline sum if that is the smallest on study). Also, the sum must also demonstrate an absolute increase of a least 5mm. Appearance of one or more new lesions.

Objective Response (OR)Post baseline tumour-imaging was performed at Week 8, 16, 24, 32, 40, 48, 56 and then every 12 weeks (Until final data-base lock on 30 Jul 2018; Up to 95 months)

OR is defined as complete response (CR) and partial response (PR). Assessed by investigator according to Response Evaluation Criteria in Solid Tumours (RECIST) 1.1. Complete Response (CR) for target lesions (TL): Disappearance of all target lesions.

Complete Response (CR) for non-target lesions (NTL): Disappearance of all non-target lesions and normalization of tumour marker level. All lymph nodes must be non-pathological in size (\<10mm short axis)

Partial Response (PR): At least a 30% decrease in the sum of diameters of target lesions taking as reference the baseline sum diameters.

Other factors which add to the overall response of an imaging timepoint as PR are as below:-

* CR in TL, but non-CR/Non-PD in NTL leads to PR

* CR in TL, but not evaluated NTL leads to PR

* PR in TL, but non-PD NTL or not all evaluated NTL leads to PR

Trial Locations

Locations (206)

Ordensklinikum Linz GmbH - Barmherzige Schwestern

🇦🇹

Linz, Austria

Sanatorio Parque

🇦🇷

Rosario, Argentina

Ironwood Cancer and Research Centers

🇺🇸

Chandler, Arizona, United States

Peninsula Haematology & Oncology

🇦🇺

Frankston, Victoria, Australia

Maroondah Hospital

🇦🇺

Ringwood East, Victoria, Australia

Instituto Medico de Asistencia e Investigaciones S. A.

🇦🇷

Buenos Aires, Argentina

Hospital Britanico

🇦🇷

Capital Federal, Argentina

Sanatorio de la Provodencia

🇦🇷

Ciudad Autonoma de Bs As, Argentina

Kaiser Franz Josef Spital Vienna

🇦🇹

Wien, Austria

Grodno Regional Clinical Hospital

🇧🇾

Grodno, Belarus

N. N. Alexandrov National Cancer Center of Belarus

🇧🇾

Minsk Region, Belarus

Public Health Inst. Minsk City Clinical Oncology Dispensary

🇧🇾

Minsk, Belarus

Liège - HOSP St-Joseph

🇧🇪

Liège, Belgium

Centro de Pesquisas Clínicas em Oncología

🇧🇷

Cachoeiro de Itapemirim, Brazil

Brussels - HOSP Jules Bordet

🇧🇪

Bruxelles, Belgium

Edegem - UNIV UZ Antwerpen

🇧🇪

Edegem, Belgium

Hospital Santa Cruz

🇧🇷

Curitiba, Brazil

Faculdade de Medicina do ABC

🇧🇷

Santo André, Brazil

Associação Hospitalar Moinhos de Vento

🇧🇷

Porto Alegre, Brazil

The Ottawa Hospital

🇨🇦

Ottawa, Ontario, Canada

Centro de Novos Tratamentos CliniOnco

🇧🇷

Porto Alegre, Brazil

Centro de Referência da Saude da Mulher-Hosp Perola Byington

🇧🇷

Sao Paulo, Brazil

BC Cancer Agency - Vancouver

🇨🇦

Vancouver, British Columbia, Canada

Peking Union Medical College Hospital

🇨🇳

Beijing, China

Princess Margaret Cancer Centre

🇨🇦

Toronto, Ontario, Canada

CHU de Quebec-Universite Laval Research Centre

🇨🇦

Quebec, Canada

St. Elisabeth-Krankenhaus

🇩🇪

Köln, Germany

National Cancer Center

🇰🇷

Goyang, Korea, Republic of

Severance Hospital

🇰🇷

Seoul, Korea, Republic of

Fudan University Shanghai Cancer Center

🇨🇳

Shanghai, China

Oncology Centre- Mansoura University

🇪🇬

Mansoura, Egypt

HOP Amiens-Picardie Sud

🇫🇷

Amiens Cedex 1, France

CLI Bordeaux Nord Aquitaine

🇫🇷

Bordeaux, France

Tokai University Hospital

🇯🇵

Kanagawa, Isehara, Japan

Ziemia Lubelska Oncological Center, Lublin

🇵🇱

Lublin, Poland

CTR J Perrin, Onco, Clermont-Ferrand

🇫🇷

Clermont-Ferrand Cedex, France

HOP Saint-Louis

🇫🇷

Paris, France

Gynäk.-onkol. Gem.praxis, Dr. Uleer, Hildesheim

🇩🇪

Hildesheim, Germany

Gujarat Cancer and Research Institute

🇮🇳

Ahmedabad, India

Sourasky Medical Center

🇮🇱

Tel-Aviv, Israel

St Vincent's University Hospital

🇮🇪

Dublin 4, Ireland

Rambam Medical Center

🇮🇱

Haifa, Israel

The Chaim Sheba Medical Center Tel Hashomer

🇮🇱

Tel Hashomer, Israel

Mater Misericordiae University Hospital

🇮🇪

Dublin 7, Ireland

Korea University Anam Hospital

🇰🇷

Seoul, Korea, Republic of

National Cancer Center Hospital

🇯🇵

Tokyo, Chuo-ku, Japan

Máxima Medisch Centrum, locatie Eindhoven

🇳🇱

Eindhoven, Netherlands

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

METC Academisch Ziekenhuis Maastricht/Universiteit van Maastricht

🇳🇱

Maastricht, Netherlands

Wilgers oncology

🇿🇦

Pretoria, South Africa

Wojewodzki Specialist Hospital No. 4, Bytom

🇵🇱

Bytom, Poland

Oncology Centre of Olsztyn "KOPERNIK" Sp. z.o.o.

🇵🇱

Olsztyn, Poland

National Cancer Centre

🇸🇬

Singapore, Singapore

CHUC, EPE - CHC-Maternidade Bissaya Barreto

🇵🇹

Coimbra, Portugal

IPO Porto Francisco Gentil, EPE

🇵🇹

Porto, Portugal

Kaohsiung Veterans General Hospital

🇨🇳

Kaohsiung, Taiwan

Regional Clinical Oncology Dispensary

🇷🇺

Saint Petersburg, Russian Federation

Koo Foundation Sun Yet-Sen Cancer Center

🇨🇳

Taipei, Taiwan

Cancer Care Associates Medical Group, Inc

🇺🇸

Redondo Beach, California, United States

Central Coast Medical Oncology Corporation

🇺🇸

Santa Maria, California, United States

Cedar Valley Cancer Center

🇺🇸

Waterloo, Iowa, United States

Pro Health Care Associated

🇺🇸

Lake Success, New York, United States

Port Macquarie Base Hospital (PMBH)

🇦🇺

Port Macquarie, New South Wales, Australia

Associacao Hospital de Caridade de Ijui

🇧🇷

Ijui, Brazil

Irmandade da Santa Casa de Misericórdia de Porto Alegre

🇧🇷

Porto Alegre, Brazil

Instituto Nacional do Câncer - INCA

🇧🇷

Rio de Janeiro, Brazil

Grand River Regional Cancer Centre

🇨🇦

Kitchener, Ontario, Canada

Hopital Notre-Dame du CHUM

🇨🇦

Montreal, Quebec, Canada

Instituto Clínico Oncológico del Sur - ICOS

🇨🇱

Temuco, Chile

Cancer Hospital of Chinese Academy of Medical Science

🇨🇳

Beijing, China

Peking University People's Hospital

🇨🇳

Beijing, China

First Hospital of Jilin University

🇨🇳

Changchun, China

307 Hospital of PLA

🇨🇳

Beijing, China

West China Hospital

🇨🇳

Chengdu, China

Fujian Provincial Tumor Hospital

🇨🇳

Fuzhou, China

Sun Yat-Sen University Cancer Center

🇨🇳

Guangzhou, China

The First Affiliated Hospital, Zhejiang University

🇨🇳

Hangzhou, China

Guangdong Provincial People's Hospital

🇨🇳

Guangzhou, China

NanFang Hosptial

🇨🇳

Guangzhou, China

The Third Affiliated Hospital of Harbin Medical University

🇨🇳

Haerbin, China

Zhejiang Cancer Hospital

🇨🇳

Hangzhou, China

Qilu Hospital, Shangdong University

🇨🇳

Jinan, China

Ruijin Hospital, Shanghai Jiao Tong University School of Medicine

🇨🇳

Shanghai, China

Hospital Ceske Budejovice

🇨🇿

Ceske Budejovice, Czechia

Wuhan Union Hospital

🇨🇳

Wuhan, China

Tianjin Medical University Cancer Institute and Hospital

🇨🇳

Tianjin, China

University Hospital Olomouc

🇨🇿

Olomouc, Czechia

General Faculty Hospital, Prague

🇨🇿

Prague 2, Czechia

MEDICON a.s., Praha 4

🇨🇿

Praha 4, Czechia

El Manial Specialized Hospital

🇪🇬

Cairo, Egypt

CTR P Papin, Onco, Angers

🇫🇷

Angers Cedex 9, France

HOP Jean Minjoz

🇫🇷

Besançon Cedex, France

HOP Victor Hugo

🇫🇷

Le Mans, France

INS Jean Godinot, Onco, Reims

🇫🇷

Reims, France

CTR Catherine de Sienne

🇫🇷

Nantes, France

CTR Eugène Marquis

🇫🇷

Rennes Cedex, France

CTR Paul Strauss

🇫🇷

Strasbourg Cedex, France

CTR René Huguenin

🇫🇷

St Cloud, France

Universitätsklinikum Aachen, AöR

🇩🇪

Aachen, Germany

OnkoDok GbR

🇩🇪

Bottrop, Germany

Medizinisches Zentrum Bonn

🇩🇪

Bonn, Germany

DONAUISAR Klinikum Deggendorf-Dingolfing-Landau gKU

🇩🇪

Deggendorf, Germany

Universitätsklinikum Erlangen

🇩🇪

Erlangen, Germany

Universitätsklinikum Magdeburg AöR

🇩🇪

Magdeburg, Germany

Kliniken Essen - Mitte gGmbH

🇩🇪

Essen, Germany

Universitätsklinikum Köln (AöR)

🇩🇪

Köln, Germany

Klinikum der Universität München - Campus Innenstadt

🇩🇪

München, Germany

Onkologische Praxis Oldenburg

🇩🇪

Oldenburg, Germany

Klinikum rechts der Isar der Technischen Universität München

🇩🇪

München, Germany

Universitätsfrauenklinik am Klinikum Südstadt

🇩🇪

Rostock, Germany

Facharzt für Innere Medizin

🇩🇪

Wuppertal, Germany

St James's Hospital

🇮🇪

Dublin 8, Ireland

Meir Medical Center

🇮🇱

Kfar Saba, Israel

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

P. Stradins Clinical Univ. Hospital, Oncology Clinic

🇱🇻

Riga, Latvia

Hammoud Hospital University Medical Centre (HHUMC)

🇱🇧

Lebanon, Lebanon

Zuyderland Medisch Centrum

🇳🇱

Heerlen, Netherlands

Isala Zwolle

🇳🇱

Zwolle, Netherlands

Hospital Nacional Adolfo Guevara Velasco

🇵🇪

Cusco, Peru

Provincial Specialist M. Kopernik Hospital

🇵🇱

Lodz, Poland

Military Medical Institute

🇵🇱

Warsaw, Poland

Wielkopolskie Oncology Centre n.a. Maria Sklodowska-Courie

🇵🇱

Poznan, Poland

IPO Lisboa Francisco Gentil, EPE

🇵🇹

Lisboa, Portugal

GUZ "Regional Clinical Oncology Dispensary"

🇷🇺

Ryazan, Russian Federation

National University Hospital

🇸🇬

Singapore, Singapore

Institute of Oncology Ljubljana

🇸🇮

Ljubljana, Slovenia

Medical Oncology Centre of Rosebank

🇿🇦

Johannesburg, South Africa

GVI oncology Medi Clinic

🇿🇦

Kraaifontein, South Africa

Langenhoven Drive Oncology Centre

🇿🇦

Port Elizabeth, South Africa

Rondebosch Oncology Centre

🇿🇦

Rondebosch, Cape Town, South Africa

Hospital Clínico San Carlos

🇪🇸

Madrid, Spain

Mount Medical Centre

🇦🇺

Perth, Western Australia, Australia

Vitebsk Regional Clinical Oncology Dispensary

🇧🇾

Vitebsk, Belarus

Sujan Surgical Cancer Hospital

🇮🇳

Amravati, India

KIDWAI memoraial Institute of oncology

🇮🇳

Bangalore, India

Sri Venkateshwara Hospital

🇮🇳

Bengaluru, India

Curie Manavata Cancer centre

🇮🇳

Nashik, India

Bibi General Hospital and Cancer Centre

🇮🇳

Hyderabad, India

Orchid Nursing Home

🇮🇳

Kolkata, India

Natinal Cancer Institute

🇮🇳

Maharagama, India

Dr. Rai Memorial Cancer Centre

🇮🇳

Chennai, India

Central India Cancer Research Institute

🇮🇳

Nagpur, India

Jehangir Hospital Oncology Department

🇮🇳

Pune, India

K.E.M Hospital

🇮🇳

Pune, India

King George Hospital

🇮🇳

Visakhapatnam, India

Beaumont Hospital

🇮🇪

Dubliin 9, Ireland

Istituto Europeo di Oncologia

🇮🇹

Milan, Italy

Osaka Medical Center for Cancer and Cardiovascular Diseases

🇯🇵

Osaka, Osaka, Japan

Riga East Univ. Hospital, Oncology Centre

🇱🇻

Riga, Latvia

Shaare Zedek Medical Center, Jerusalem 91031

🇮🇱

Jerusalem, Israel

Azienda Ospedaliera Universitaria Arcispedale Sant'Anna

🇮🇹

Ferrara, Italy

P.O. Monserrato

🇮🇹

Monserrato (CA), Italy

Hospital de Jesus

🇲🇽

Colonia Centro, Mexico

Instituto Oncologico Miraflores S.A.

🇵🇪

Miraflores, Peru

University Clinical Center, Gdansk

🇵🇱

Gdansk, Poland

Hospital of Lithuanian Univ.of HealthSciences Kauno Klinikos

🇱🇹

Kaunas, Lithuania

National Cancer Institute, Vilnius

🇱🇹

Vilnius, Lithuania

Albert SchweitzerZiekenhuis

🇳🇱

Dordrecht, Netherlands

Instituto Português de Oncologia de Coimbra Francisco Gentil

🇵🇹

Coimbra, Portugal

St.Auton.Heal.Inst."Rep.Clin.Onc.Disp.of MoH of Rep. Tatarstan"

🇷🇺

Kazan, Russian Federation

Clinica San Judas Tadeo

🇵🇪

Lima, Peru

N.A. Semashko Central Clinical Hospital, Moscow

🇷🇺

Moscow, Russian Federation

Bialystock's Oncology Center

🇵🇱

Bialystok, Poland

Clinica Peruano Americana de Trujillo

🇵🇪

Trujillo, Peru

Centro Hospitalar São João,EPE

🇵🇹

Porto, Portugal

POKO Policlinic Dept. of Clinical Oncology

🇸🇰

Poprad, Slovakia

WCR CMJAH Clinical Trial Site

🇿🇦

Johannesburg, South Africa

Hospital Vall d'Hebron

🇪🇸

Barcelona, Spain

Complejo Hospitalario Universitario Insular - Materno Infantil

🇪🇸

Las Palmas de Gran Canaria, Spain

Johns Hopkins Singapore International Medical Center

🇸🇬

Singapore, Singapore

St. Jacobs Hosp.Outpat.Pneumology&Phthisiology Dept,Bardejov

🇸🇰

Bardejov, Slovakia

National Institute of Oncology, Bratislava

🇸🇰

Bratislava, Slovakia

Hospital Clínico de Santiago

🇪🇸

Santiago de Compostela, Spain

Hospital Virgen de la Salud

🇪🇸

Toledo, Spain

Hospital del Mar

🇪🇸

Barcelona, Spain

Hospital Universitari Dexeus

🇪🇸

Barcelona, Spain

Shatabdi Superspeciality Hospital

🇱🇰

Maharashtra, Sri Lanka

Chang-Hua Christian Hospital

🇨🇳

Changhua, Taiwan

Kaohsiung Medical University Chung-Ho Memorial Hospital

🇨🇳

Kaohsiung, Taiwan

Chang Gung Memorial Hospital(TaoYuan)

🇨🇳

Taoyuan County, Taiwan

Ninewells Hospital & Medical School

🇬🇧

Dundee, United Kingdom

Hospital Arnau de Vilanova

🇪🇸

Valencia, Spain

Taipe Veterans General Hospital

🇨🇳

Taipei, Taiwan

Taichung Veterans General Hospital

🇨🇳

Taichung, Taiwan

NCKUH

🇨🇳

Tainan, Taiwan

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Mackay Memorial Hospital

🇨🇳

Taipei, Taiwan

Hacettepe Universitesi Tip Fakultesi, Ic Hastaliklari ABD

🇹🇷

Ankara, Turkey

Ege Universitesi Tip Fakultesi Tibbi Onkoloji Bilim Dali

🇹🇷

Izmir, Turkey

The Royal Marsden Hospital

🇬🇧

Sutton, United Kingdom

Queen Elizabeth Hospital

🇬🇧

Woolwich, London, United Kingdom

Chinese PLA General Hospital

🇨🇳

Beijing, China

St. Jude Heritage Healthcare

🇺🇸

Fullerton, California, United States

North Shore Cancer Research Associates

🇺🇸

Skokie, Illinois, United States

Hope Women's Cancer Center

🇺🇸

Asheville, North Carolina, United States

Achieve Clinical Research, LLC

🇺🇸

Birmingham, Alabama, United States

Robert A. Moss MD, FACP, Inc

🇺🇸

Fountain Valley, California, United States

Santa Barbara Hematology Oncology Medical Group, Inc

🇺🇸

Santa Barbara, California, United States

University of California

🇺🇸

Los Angeles, California, United States

Utah Cancer Specialists Cancer Center

🇺🇸

Salt Lake City, Utah, United States

St Vincent's Hospital Melbourne

🇦🇺

Fitzroy, Victoria, Australia

Dr. Leon Richard Oncology Centre

🇨🇦

Moncton, New Brunswick, Canada

Guy's Hospital

🇬🇧

London, United Kingdom

Thomas Jefferson University

🇺🇸

Philadelphia, Pennsylvania, United States

the 81th Hospital of PLA

🇨🇳

Nanjing, China

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