MedPath

TREND-HD - A Trial of Ethyl-EPA (Miraxion™) in Treating Mild to Moderate Huntington's Disease

Phase 3
Completed
Conditions
Huntington Disease
Registration Number
NCT00146211
Lead Sponsor
Amarin Neuroscience Ltd
Brief Summary

This study is designed to determine the effect of 2 gram/day of ethyl-EPA on motor (movement) signs and symptoms of Huntington disease.

Detailed Description

Multi-center, double blind, placebo-controlled study with parallel groups of outpatients with early, symptomatic Huntington's disease. Participants will be randomized to receive 1 gram twice daily (2 gram/day total daily dose) of active study drug or placebo. The 6-month placebo-controlled phased will be followed by a subsequent 6-month open-label extension phase with all subjects receiving 1 gram twice daily (2 grams/day total daily dose) of active study drug.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
300
Inclusion Criteria
  • Clinical features of Huntington's disease (HD) and confirmatory family history of HD, and/or CAG repeat expansion greater than or equal to 36
  • Ambulatory, not requiring skilled nursing care (total functional capacity [TFC] greater than or equal to 7)
  • Chorea score of at least 2 in one extremity (UHDRS)
  • Maximal dystonia less than or equal to 2 and maximal bradykinesia less than or equal to 2
  • 35 years of age or older of either gender
  • Must be on stable dosages of non-competitive NMDA receptor antagonists, and/or antiepileptic medications for 60 days prior to baseline
  • Females of child-bearing potential must use adequate birth control
Exclusion Criteria
  • History of established diagnosis of tardive dyskinesia
  • Clinical evidence of unstable medical or psychiatric illness
  • Clinically significant active and unstable psychotic disease (hallucinations or delusions)
  • Major depression (Beck Depression Inventory [BDI]-II Score greater than 20) at Screening Visit
  • Suicidal ideation (BDI-II item 9 greater than or equal to 2) at Screening Visit
  • History of clinically significant substance abuse within 12 months of Baseline Visit
  • Pregnant/lactating women
  • Participation in other drug studies within 60 days prior to Baseline Visit
  • Previous participation in any investigational study of ethyl-EPA (Miraxion™)
  • Use of aspirin at daily dosage greater than 325 mg/day
  • Exclusionary Drugs (within 6 months Baseline Visit): Depot neuroleptics
  • Exclusionary Drugs (within 60 days Baseline Visit): Omega-3 supplementation, tetrabenazine or reserpine, high dose and/or variable dose oral anti-psychotic medications, steroid (other than topical), selenium supplements greater than 55 mcg/day, lithium, benzodiazepines (except for low dose), anticoagulants

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Primary Outcome Measures
NameTimeMethod
To compare with placebo the effect of ethyl-EPA on the Total Motor Score-4 component (TMS) of the Unified Huntington's Disease Rating Scale (UHDRS) over a 6-month period of observation.
Secondary Outcome Measures
NameTimeMethod
To compare with placebo the effect of ethyl-EPA over a 6-month period of observation on, 1) Chorea (UHDRS Total Motor Score Scale); 2) Total Motor Score component (TMS) of the UHDRS; and, 3) Clinical Global Impression (CGI) score.

Trial Locations

Locations (40)

UCLA Medical Center

🇺🇸

Los Angeles, California, United States

Emory University

🇺🇸

Atlanta, Georgia, United States

University of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

The Centre for Addiction and Mental Health

🇨🇦

Markham, Ontario, Canada

University of Rochester

🇺🇸

Rochester, New York, United States

Mayo Clinic Arizona

🇺🇸

Scottsdale, Arizona, United States

Hereditary Neurological Disease Centre

🇺🇸

Wichita, Kansas, United States

Colorado Neurological Institute

🇺🇸

Englewood, Colorado, United States

University of California Davis

🇺🇸

Sacramento, California, United States

Indiana University

🇺🇸

Indianapolis, Indiana, United States

University of Chicago

🇺🇸

Chicago, Illinois, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Medical College of Georgia

🇺🇸

Augusta, Georgia, United States

University of California San Francisco

🇺🇸

San Francisco, California, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Ohio State University Parkinson's Center

🇺🇸

Columbus, Ohio, United States

University of Miami

🇺🇸

Miami, Florida, United States

University of Iowa

🇺🇸

Iowa City, Iowa, United States

University of Kansas

🇺🇸

Kansas City, Kansas, United States

University of California San Diego

🇺🇸

La Jolla, California, United States

Institute of Neurodegenerative Disorders

🇺🇸

New Haven, Connecticut, United States

University of Calgary

🇨🇦

Calgary, Alberta, Canada

Washington University School of Medicine

🇺🇸

St. Louis, Missouri, United States

Albany Medical College

🇺🇸

Albany, New York, United States

University of South Florida

🇺🇸

Tampa, Florida, United States

University of Florida

🇺🇸

Gainesville, Florida, United States

Johns Hopkins University

🇺🇸

Baltimore, Maryland, United States

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

Penn State Milton & Hershey Medical College

🇺🇸

Hershey, Pennsylvania, United States

Boston University

🇺🇸

Boston, Massachusetts, United States

North Shore-LIJ Health System

🇺🇸

Manhasset, New York, United States

Massachusetts General Hospital

🇺🇸

Charlestown, Massachusetts, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

University of Tennessee-Memphis

🇺🇸

Memphis, Tennessee, United States

University of Virginia

🇺🇸

Charlottesville, Virginia, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

University of British Columbia

🇨🇦

London, Ontario, Canada

University of Alberta Glenrose Rehab Hospital

🇨🇦

Edmonton, Alberta, Canada

Hotel-Dieu Hospital-CHUM

🇨🇦

Montreal, Quebec, Canada

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

© Copyright 2025. All Rights Reserved by MedPath