MedPath

Adjuvant IP-001 Treatment for HCC Patients Following Surgical Resection and Ablation or Ablation Alone

Phase 2
Recruiting
Conditions
Hepatocellular Carcinoma
Interventions
Drug: 1.0% IP-001 for injection
Procedure: Surgical Resection and Local Ablation
Procedure: Local Ablation Alone
Registration Number
NCT06526338
Lead Sponsor
Robert C. Martin
Brief Summary

The purpose of this study is to evaluate the safety and efficacy of a single injection of IP-001 as adjuvant therapy after local ablation or surgical resection and ablation in patients with hepatocellular carcinoma (HCC).

Detailed Description

This is a Phase 2, two-armed, randomized study designed to evaluate the safety and efficacy of a single administration of intratumoral IP-001 injection following local ablation or surgical resection and local ablation in patients with hepatocellular carcinoma who have an intermediate or high risk of recurrence compared to curative ablation or ablation and surgical resection.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
126
Inclusion Criteria
  • Age ≥ 18 years at time of signing Informed Consent.

  • Has a diagnosis of hepatocellular carcinoma (HCC) documented radiologically by American Association for the Study of Liver Diseases (AASLD) criteria and/or histopathologically from a tumor biopsy.

  • Has a treatment plan to receive either a curative ablation (RFA or MWA) or a curative surgical resection and ablation.

  • Has HCC with intermediate, high or very high risk of recurrence.

  • Has hepatic only HCC (disease confined to the liver only), defined by no extra-hepatic lesions greater than 1 cm in size.

  • Has an Eastern Cooperative Oncology Group (ECOG) performance status of 0-1.

  • Patient with past or ongoing hepatitis C virus (HCV) infection will be eligible if the patient has completed HCV treatment at least 1 month prior to Day 1.

  • Patient with controlled hepatitis B will be eligible if the patients meets the following criteria:

    1. Antiviral therapy for hepatitis B virus (HBV) must be given for at least 4 weeks and HBV viral load must be less than 500 IU/mL prior to treatment. Patients on active HBV therapy with viral loads under 00 IU/mL should stay on the same therapy throughout study treatment.
    2. Patients who are hepatitis B core antibody (anti-HBc) positive, negative for HBsAg, and negative or positive for anti- HBs, and who have an HBV viral load under 500 IU/mL do not require HBV anti-viral prophylaxis.
  • Has adequate organ function as specified in the Adequate Organ Function Laboratory Values Table. Specimens must be collected within 14 days prior to Day 1.

Exclusion Criteria
  • Known allergic reaction to shellfish, crabs, crustacean, or any trial components.

  • Has an active infection requiring systemic therapy.

  • Has a diagnosis of immunodeficiency or currently receiving chronic systemic steroid therapy (in dosing exceeding 10 mg daily of prednisone equivalent), or any other form of immunosuppressive therapy within 7 days prior to treatment day (Day 1), or has plans to start treatment including >10 mg daily of prednisone equivalent or any immunotherapy.

  • Has an active autoimmune disease that has required systemic treatment in the past 2 years (i.e., with use of disease modifying agents or immunosuppressive drugs). NOTE: replacement therapy (e.g., thyroxine or insulin) is not considered a form of systemic treatment and is allowed.

  • Has had an allogenic tissue/solid organ transplant.

  • History of idiopathic pulmonary fibrosis, organizing pneumonia (e.g., bronchiolitis obliterans), drug-induced pneumonitis, active tuberculosis, or idiopathic pneumonitis.

  • Has received local therapy to liver, ablation other than radiofrequency or microwave ablation (i.e., alcohol ablation, transcatheter chemoembolization, transcatheter embolization, hepatic arterial infusion, local radiation/Stereotactic Body Radiation Therapy or radioembolization) less than 3 months prior to treatment.

  • Is receiving any of the following prohibited concomitant therapies less than 21 days from treatment or 5 drug elimination half-lives, whichever is shorter prior to randomization:

    1. Antineoplastic systemic chemotherapy or biological therapy.
    2. Immunotherapy not specified in this protocol.
    3. Systemic glucocorticoids for any purpose other than to modulate symptoms from an adverse event (AE) that is suspected to have an immunologic etiology. Inhaled or topical steroids are allowed, and systemic steroids at doses ≤10 mg/day prednisone or equivalent are allowed. Exception: steroids may be used for premedication prior to imaging.
  • Has received a live vaccine within 28 days prior to treatment Day 1.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
IP-0011.0% IP-001 for injection1.0% IP-001 for injection immediately following local ablation or surgical resection and local ablation
IP-001Surgical Resection and Local Ablation1.0% IP-001 for injection immediately following local ablation or surgical resection and local ablation
IP-001Local Ablation Alone1.0% IP-001 for injection immediately following local ablation or surgical resection and local ablation
ControlSurgical Resection and Local AblationLocal ablation or surgical resection and local ablation alone
ControlLocal Ablation AloneLocal ablation or surgical resection and local ablation alone
Primary Outcome Measures
NameTimeMethod
Recurrence Free SurvivalFrom Date of Randomization until date of documented progression, assessed up to 60 months

Radiological assessments (Triphasic CT or MRI) of the chest, abdomen and pelvis will occur every 12 weeks for the first 2 years, then every 24 weeks thereafter. Recurrence will be determined by the investigator's radiological review per RECIST v1.1

Secondary Outcome Measures
NameTimeMethod
Recurrence Free Survival RateMonths 12 and 24

Assessed from treatment Day 1 to documentation of disease recurrence or extrahepatic) or death, whichever occurs first.

Cancer Free SurvivalMonths 12 and 24

Participants will be followed every 12 weeks from treatment Day 1 for the first 2 years, and every 24 weeks thereafter until disease related death.

Overall SurvivalMonths 12 and 24

Participants will be followed every 12 weeks from treatment Day 1 for the first 2 years, and every 24 weeks thereafter until death of any cause.

Time to Intrahepatic Tumor RecurrenceFrom Date of Randomization until date of documented progression, assessed up to 60 months

Radiological assessments (Triphasic CT or MRI) of the chest, abdomen and pelvis will occur every 12 weeks for the first 2 years, then every 24 weeks thereafter. Recurrence will be determined by the investigator's radiological review per RECIST v1.1

Overall Survival RateMonths 12 and 24

Proportion of participants who have not experienced death from treatment Day 1 at 12 and 24 months after treatment.

Time to Extrahepatic Tumor RecurrenceFrom Date of Randomization until date of documented progression, assessed up to 60 months

Radiological assessments (Triphasic CT or MRI) of the chest, abdomen and pelvis will occur every 12 weeks for the first 2 years, then every 24 weeks thereafter. Recurrence will be determined by the investigator's radiological review per RECIST v1.1

Trial Locations

Locations (1)

University of Louisville

🇺🇸

Louisville, Kentucky, United States

© Copyright 2025. All Rights Reserved by MedPath